{"id":"W4309408407","doi":"10.51731/cjht.2022.496","title":"Nusinersen (Spinraza)","year":2022,"lang":"en","type":"article","venue":"Canadian Journal of Health Technologies","topic":"Neurogenetic and Muscular Disorders Research","field":"Medicine","cited_by":4,"is_retracted":false,"has_abstract":true,"ca_institutions":"","funders":"","keywords":"Reimbursement; SMA*; Medicine; Intrathecal; Spinal muscular atrophy; Food and drug administration; Family medicine; Intensive care medicine; Surgery; Political science; Medical emergency; Pathology; Computer science; Disease; Health care","routes":{"ca_aff":false,"ca_fund":false,"ca_venue":false,"about_ca":true,"invisible_to_affiliation_only":true},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.0005284403,0.0007058935,0.0006261292,0.001097122,0.0005161156,0.001321292,0.0008025619,0.001768758,0.1336455],"category_scores_gemma":[0.00106988,0.0002141436,0.0004664173,0.0005448958,0.000504141,0.000766322,0.0009034321,0.001438291,0.04872315],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.001057203,"about_ca_system_score_gemma":0.002867657,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.01200251,"about_ca_topic_score_gemma":0.03486595,"domain_scores_codex":[0.9995574,0.0000543567,0.00003815498,0.0001024642,0.0001934813,0.00005413084],"domain_scores_gemma":[0.999613,0.00007159174,0.00005669566,0.00002567869,0.0001165571,0.0001164974],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"design_other","study_design_gemma":"not_applicable","study_design_scores_codex":[0.0007825198,0.0001202522,0.0004455171,0.005786854,0.00008000627,0.0005954735,0.000121625,0.0002107525,0.007718591,0.008028388,0.2125012,0.7636089],"study_design_scores_gemma":[0.0001727883,0.0002494458,0.0008048798,0.0009670333,0.00004592967,0.0006570071,0.00004880635,0.00005680299,0.002344529,0.0005817569,0.9940586,0.00001233872],"study_design_candidate":"not_applicable","study_design_consensus":null,"genre_codex":"other","genre_gemma":"other","genre_scores_codex":[0.008470033,0.4347058,0.00209361,0.008846159,0.005650323,0.0003804479,0.004874607,0.001926351,0.5330526],"genre_scores_gemma":[0.07891998,0.2385351,0.005389811,0.01086645,0.001129144,0.0002187554,0.006626175,0.0003403774,0.6579741],"genre_candidate":"other","genre_consensus":"other","teacher_disagreement_score":0.1336455,"threshold_uncertainty_score":0.4470887,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.03693449601395939,"score_gpt":0.3159404689860767,"score_spread":0.2790059729721173,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}