{"id":"W4310105223","doi":"10.1182/blood-2022-163625","title":"Long-Term Safety and Efficacy of Pegcetacoplan Treatment in Adults with Paroxysmal Nocturnal Hemoglobinuria","year":2022,"lang":"en","type":"article","venue":"Blood","topic":"Complement system in diseases","field":"Immunology and Microbiology","cited_by":7,"is_retracted":false,"has_abstract":true,"ca_institutions":"Toronto General Hospital; University Health Network","funders":"","keywords":"Paroxysmal nocturnal hemoglobinuria; Medicine; Term (time); Internal medicine","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.001343286,0.0002635577,0.0007236135,0.0001490411,0.0003172283,0.0004659492,0.0001937011,0.0005274173,0.0008071667],"category_scores_gemma":[0.002375919,0.0001107143,0.0007224315,0.0002152037,0.0001958057,0.0005435955,0.000213237,0.001031007,0.0001966462],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.0004492418,"about_ca_system_score_gemma":0.0005226012,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.0006206057,"about_ca_topic_score_gemma":0.001120057,"domain_scores_codex":[0.9995134,0.000167668,0.00007347379,0.00008149842,0.00008781124,0.00007611455],"domain_scores_gemma":[0.9983677,0.000353226,0.0006339085,0.00009651423,0.0001706847,0.0003779737],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"design_other","study_design_gemma":"observational","study_design_scores_codex":[0.242673,0.009286209,0.3557868,0.0008827431,0.002799871,0.001074974,0.0005491583,0.001702299,0.0112327,0.0002383535,0.005875387,0.3678984],"study_design_scores_gemma":[0.02862759,0.2132141,0.7363482,0.0003110656,0.002141236,0.002646854,0.000310663,0.002828278,0.003187312,0.0003747999,0.009949183,0.00006068297],"study_design_candidate":"observational","study_design_consensus":null,"genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9938657,0.003791962,0.0001717781,0.0003063932,0.0000405453,0.00009337055,0.0004912951,0.00001663297,0.001222368],"genre_scores_gemma":[0.9975616,0.0007429337,0.000180977,0.0003645895,0.00006554407,0.00009475541,0.0006894703,0.000002172846,0.0002980103],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.001343286,"threshold_uncertainty_score":0.007104039,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.008062017544466098,"score_gpt":0.2262863002728752,"score_spread":0.2182242827284091,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}