{"id":"W4312129700","doi":"10.3233/jnd-221600","title":"Improvements in Walking Distance during Nusinersen Treatment – A Prospective 3-year SMArtCARE Registry Study","year":2022,"lang":"en","type":"article","venue":"Journal of Neuromuscular Diseases","topic":"Neurogenetic and Muscular Disorders Research","field":"Medicine","cited_by":30,"is_retracted":false,"has_abstract":true,"ca_institutions":"University of Ottawa; Ottawa Hospital; Children's Hospital of Eastern Ontario","funders":"Desitin Arzneimittel; Italfarmaco; Merz Pharmaceuticals; Swedish Orphan Biovitrum; Argenx; Harmony Biosciences; Spark Therapeutics; Sarepta Therapeutics; Sanofi; PTC Therapeutics; Ultragenyx Pharmaceutical; Sanofi Genzyme; F. Hoffmann-La Roche; AveXis; Biogen; Ipsen; Alnylam Pharmaceuticals; Pfizer","keywords":"Medicine; SMA*; Spinal muscular atrophy; Clinical trial; Pediatrics; Physical therapy; Disease; Internal medicine","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.001903654,0.0005038701,0.001040411,0.001415174,0.0005318674,0.001127237,0.0006101304,0.0007738722,0.001287457],"category_scores_gemma":[0.002616568,0.0004293931,0.001178961,0.002213959,0.0003510783,0.001220812,0.001246698,0.0006301104,0.0004803354],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.0005371136,"about_ca_system_score_gemma":0.0006168645,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.00528772,"about_ca_topic_score_gemma":0.007963633,"domain_scores_codex":[0.998153,0.0004608256,0.0003405412,0.0005067375,0.0002829738,0.0002558812],"domain_scores_gemma":[0.9970008,0.0003170949,0.001560538,0.0003910767,0.000347846,0.0003826671],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"observational","study_design_gemma":"observational","study_design_scores_codex":[0.0006795234,0.000106169,0.9971431,0.00003314107,0.0002171403,0.0001136978,0.0001024808,0.00004898138,0.00007986924,0.00001345446,0.0002111197,0.001251333],"study_design_scores_gemma":[0.00005616117,0.0002943208,0.9988449,0.00001313989,0.0001064479,0.0001518769,0.0001463405,0.0001051411,0.0000288078,0.000008084121,0.000237361,0.00000739923],"study_design_candidate":"observational","study_design_consensus":"observational","genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9972102,0.0002748636,0.00006066911,0.00001938229,0.000005870337,0.00003391649,0.002098948,0.00000455383,0.0002915705],"genre_scores_gemma":[0.9924911,0.0002413197,0.0001364583,0.00004223427,0.00001668503,0.0000789918,0.006803745,0.000006661524,0.0001827614],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.00528772,"threshold_uncertainty_score":0.01051384,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.01239348945411948,"score_gpt":0.2863020476790517,"score_spread":0.2739085582249322,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}