{"id":"W4312129700","doi":"10.3233/jnd-221600","title":"Improvements in Walking Distance during Nusinersen Treatment – A Prospective 3-year SMArtCARE Registry Study","year":2022,"lang":"en","type":"article","venue":"Journal of Neuromuscular Diseases","topic":"Neurogenetic and Muscular Disorders Research","field":"Medicine","cited_by":30,"is_retracted":false,"has_abstract":true,"ca_institutions":"University of Ottawa; Ottawa Hospital; Children's Hospital of Eastern Ontario","funders":"Desitin Arzneimittel; Italfarmaco; Merz Pharmaceuticals; Swedish Orphan Biovitrum; Argenx; Harmony Biosciences; Spark Therapeutics; Sarepta Therapeutics; Sanofi; PTC Therapeutics; Ultragenyx Pharmaceutical; Sanofi Genzyme; F. Hoffmann-La Roche; AveXis; Biogen; Ipsen; Alnylam Pharmaceuticals; Pfizer","keywords":"Medicine; SMA*; Spinal muscular atrophy; Clinical trial; Pediatrics; Physical therapy; Disease; Internal medicine","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"codex-gemma-dda1882f352a","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.0001436049,0.0001925379,0.0004231278,0.000293451,0.0001799457,0.000032739,0.0001889623,0.00001757906,0.0001050049],"category_scores_gemma":[0.0001326352,0.0001629606,0.0003321191,0.000432449,0.00004361245,0.00008453255,0.0001535039,0.0003317961,0.00000144572],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.0004301616,"about_ca_system_score_gemma":0.0002900991,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.00002958456,"about_ca_topic_score_gemma":0.00001332799,"domain_scores_codex":[0.9976559,0.0002634378,0.0004381559,0.0003279615,0.001003645,0.0003109041],"domain_scores_gemma":[0.9990014,0.00002965842,0.0002234136,0.0003882149,0.0001322045,0.0002250601],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"observational","study_design_gemma":"observational","study_design_scores_codex":[0.001827998,0.005308757,0.9725047,0.0001106825,0.0003233993,0.009801737,0.0007561038,0.0002242539,0.006733358,0.000004705372,0.00006216655,0.002342188],"study_design_scores_gemma":[0.009898034,0.003585592,0.9782694,0.00005507533,0.0002990787,0.0002949285,0.006002442,0.00002751055,0.0002905994,0.00002679017,0.001110938,0.0001395955],"study_design_candidate":"observational","study_design_consensus":"observational","genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.996713,0.001637373,0.000006905606,0.0002205203,0.0001361045,0.001135816,0.00002389782,0.00001412363,0.000112265],"genre_scores_gemma":[0.9992203,0.0001709153,0.00002450511,0.00007110092,0.00009588034,0.0001029747,0.000005421976,0.00004089936,0.0002680719],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.009506809,"threshold_uncertainty_score":0.6645342,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.01239348945411948,"score_gpt":0.2863020476790517,"score_spread":0.2739085582249322,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}