{"id":"W4322623267","doi":"10.1016/j.ymgme.2023.107490","title":"PHASE 3 APHENITY LONG-TERM STUDY DESIGN: SEPIAPTERIN FOR TREATMENT OF PHENYLKETONURIA","year":2023,"lang":"en","type":"article","venue":"Molecular Genetics and Metabolism","topic":"Methemoglobinemia and Tumor Lysis Syndrome","field":"Medicine","cited_by":0,"is_retracted":false,"has_abstract":true,"ca_institutions":"SickKids Foundation; University of Toronto","funders":"","keywords":"Constipation; Medicine; Ileus; Hyperkalemia; Vincristine; Adverse effect; Hyponatremia; Pediatrics; Chemotherapy; Internal medicine; Gastroenterology; Surgery; Cyclophosphamide","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.001471565,0.001553314,0.001679655,0.0004993077,0.0007010982,0.001282476,0.0009783463,0.002229477,0.009689341],"category_scores_gemma":[0.0008239041,0.0004197093,0.001514647,0.0003291486,0.0007621762,0.0008179297,0.0004216225,0.002859271,0.001651161],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.0008474547,"about_ca_system_score_gemma":0.002159358,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.001210214,"about_ca_topic_score_gemma":0.002392283,"domain_scores_codex":[0.9995272,0.0001727336,0.00002436195,0.00007235161,0.00005023838,0.0001531116],"domain_scores_gemma":[0.9993228,0.00009600425,0.0001377456,0.0000673892,0.00007149318,0.000304627],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"randomized_trial","study_design_gemma":"not_applicable","study_design_scores_codex":[0.7823507,0.07470113,0.003743927,0.002056785,0.002857353,0.0005013042,0.0001953985,0.001591761,0.03031159,0.0008247825,0.008666069,0.09219919],"study_design_scores_gemma":[0.5970222,0.3854534,0.006187546,0.00009037635,0.0004834039,0.0002003841,0.00004238012,0.0005697865,0.002868694,0.0003631062,0.006691504,0.00002735035],"study_design_candidate":"not_applicable","study_design_consensus":null,"genre_codex":"empirical","genre_gemma":"protocol","genre_scores_codex":[0.9587516,0.005699287,0.002384125,0.001557033,0.0008087634,0.01901649,0.004566932,0.0003190597,0.00689669],"genre_scores_gemma":[0.9287093,0.004762633,0.005943143,0.00578756,0.0007920008,0.02965447,0.004584775,0.0001043918,0.01966178],"genre_candidate":"protocol","genre_consensus":null,"teacher_disagreement_score":0.009689341,"threshold_uncertainty_score":0.03241402,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.05573078695184803,"score_gpt":0.3528474221905341,"score_spread":0.2971166352386861,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}