{"id":"W4366495712","doi":"10.1093/pch/pxac122","title":"Ensuring access to innovative therapies for children, adolescents, and young adults across Canada: The single patient study experience","year":2023,"lang":"en","type":"review","venue":"Paediatrics & Child Health","topic":"Pharmaceutical studies and practices","field":"Medicine","cited_by":4,"is_retracted":false,"has_abstract":true,"ca_institutions":"University of Calgary; Women's College Hospital; Government of Alberta; University of Alberta; BC Children's Hospital; C17 Council; University of Toronto; SickKids Foundation; Hospital for Sick Children","funders":"Health Canada; Hospital for Sick Children; Bayer Canada; BC Children's Hospital","keywords":"Medicine; Expanded access; Limiting; Clinical trial; Family medicine","routes":{"ca_aff":true,"ca_fund":true,"ca_venue":false,"about_ca":true,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.01699911,0.0003010586,0.00121419,0.001762327,0.001654135,0.003841387,0.001266501,0.001331409,0.003721093],"category_scores_gemma":[0.02050623,0.0002253244,0.0007000343,0.005372894,0.001675954,0.001091463,0.001562122,0.001883248,0.0003059982],"about_ca_system_candidate":true,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.01713779,"about_ca_system_score_gemma":0.1083104,"about_ca_topic_candidate":true,"about_ca_topic_consensus":true,"about_ca_topic_score_codex":0.6458082,"about_ca_topic_score_gemma":0.8534235,"domain_scores_codex":[0.9942828,0.001785145,0.0006194061,0.0003040437,0.002512173,0.0004963383],"domain_scores_gemma":[0.9774284,0.009410994,0.00206458,0.000590708,0.008432344,0.002073048],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"design_other","study_design_gemma":"not_applicable","study_design_scores_codex":[0.0005614274,0.0002188635,0.007626894,0.03374226,0.0004209983,0.001083976,0.003712912,0.0002739483,0.001101712,0.01345409,0.05315813,0.8846447],"study_design_scores_gemma":[0.0004283548,0.0004287263,0.02896515,0.04194923,0.00103201,0.001912899,0.004714962,0.0001856154,0.0008461705,0.002078661,0.9173483,0.0001098913],"study_design_candidate":"not_applicable","study_design_consensus":null,"genre_codex":"review","genre_gemma":"review","genre_scores_codex":[0.007686216,0.9629021,0.0004322118,0.01500658,0.0003750243,0.0003479721,0.0005139374,0.00001637615,0.01271958],"genre_scores_gemma":[0.04858391,0.9413729,0.001926649,0.00571571,0.0002333613,0.0001905023,0.0003157027,0.00001565627,0.001645552],"genre_candidate":"review","genre_consensus":"review","teacher_disagreement_score":0.9828622,"threshold_uncertainty_score":0.7125553,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.1231060686956678,"score_gpt":0.4405985375011718,"score_spread":0.317492468805504,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}