{"id":"W4367607934","doi":"10.1164/ajrccm-conference.2023.207.1_meetingabstracts.a6429","title":"Understanding the Experiences of Caregivers of Children With Spinal Muscular Atrophy in the Era of Disease-modifying Therapies","year":2023,"lang":"en","type":"article","venue":"","topic":"Neurogenetic and Muscular Disorders Research","field":"Medicine","cited_by":0,"is_retracted":false,"has_abstract":false,"ca_institutions":"Hospital for Sick Children","funders":"","keywords":"Spinal muscular atrophy; Disease; Medicine; Physical medicine and rehabilitation; Progressive muscular atrophy; Neuroscience; Psychology; Pathology; Amyotrophic lateral sclerosis","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"codex-gemma-dda1882f352a","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.0002147873,0.00007324917,0.0001607378,0.00009000533,0.00005027547,0.000004641151,0.0001810281,0.00001634389,0.00003136804],"category_scores_gemma":[0.00002401088,0.00003321972,0.00009344341,0.0005472317,0.0005473228,0.00002275184,0.00003399307,0.0001039251,4.092516e-7],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.00001108076,"about_ca_system_score_gemma":0.00008929508,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.0001599845,"about_ca_topic_score_gemma":0.0000175972,"domain_scores_codex":[0.9989735,0.00008579132,0.0001414928,0.0001234326,0.0005290383,0.0001467215],"domain_scores_gemma":[0.9995611,0.00005571938,0.00004979135,0.00026479,0.00003826012,0.00003031224],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"observational","study_design_gemma":"qualitative","study_design_scores_codex":[0.003013432,0.0005291884,0.5639517,0.001023973,0.001103153,0.00009645634,0.4051602,0.00117261,0.01069438,0.007943036,0.000306641,0.005005213],"study_design_scores_gemma":[0.001742681,0.0009667175,0.3315203,0.0002407768,0.00009373864,0.000008692829,0.6625595,0.0002374182,0.002283546,0.000248237,0.00001388999,0.00008446284],"study_design_candidate":"qualitative","study_design_consensus":null,"genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9972867,0.0007913427,0.0004918817,0.0006174878,0.00001235426,0.0004434513,0.000001409628,0.000007085405,0.0003482353],"genre_scores_gemma":[0.9995275,0.0003464442,0.00003621247,0.00003147468,0.000008917428,0.00002287464,0.000002541761,0.000007598415,0.00001644164],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.2573993,"threshold_uncertainty_score":0.2016634,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.06400834356596613,"score_gpt":0.3133280982338904,"score_spread":0.2493197546679243,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}