{"id":"W4379279840","doi":"10.1017/cjn.2023.88","title":"C.2 SUNFISH parts 1 and 2: 4-year efficacy and safety data of risdiplam in types 2 and 3 spinal muscular atrophy (SMA)","year":2023,"lang":"en","type":"article","venue":"Canadian Journal of Neurological Sciences / Journal Canadien des Sciences Neurologiques","topic":"Neurogenetic and Muscular Disorders Research","field":"Medicine","cited_by":1,"is_retracted":false,"has_abstract":true,"ca_institutions":"Calgary Laboratory Services","funders":"","keywords":"SMA*; Medicine; Placebo; Tolerability; Spinal muscular atrophy; Population; Internal medicine; Adverse effect; Disease; Pathology","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":true,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.001758024,0.000776546,0.001536653,0.0004810629,0.0004309055,0.0005359136,0.0006181502,0.001382475,0.004350936],"category_scores_gemma":[0.000982929,0.0002020599,0.001460804,0.0002441327,0.0004930776,0.0006430304,0.000289416,0.001290858,0.0006414058],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.0006778483,"about_ca_system_score_gemma":0.0007862748,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.001193234,"about_ca_topic_score_gemma":0.001860052,"domain_scores_codex":[0.9995816,0.0001315366,0.00003886823,0.00007021682,0.00009588397,0.00008179661],"domain_scores_gemma":[0.99906,0.0001256086,0.0002499307,0.000125058,0.0001493993,0.0002900256],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"randomized_trial","study_design_gemma":"observational","study_design_scores_codex":[0.6202508,0.03468352,0.01343379,0.001960978,0.003161056,0.0008060581,0.0003024428,0.001280031,0.1022821,0.0002081241,0.007749017,0.2138821],"study_design_scores_gemma":[0.1468112,0.7419305,0.07309442,0.0001563322,0.001860997,0.001367315,0.00009946245,0.0008391461,0.02441124,0.0001602944,0.009180168,0.00008894967],"study_design_candidate":"observational","study_design_consensus":null,"genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.990807,0.004100469,0.0004436884,0.0003944889,0.00009765478,0.0007934332,0.001840761,0.00008719324,0.001435305],"genre_scores_gemma":[0.9812795,0.003403984,0.001266741,0.001242339,0.0001703167,0.001080698,0.006120711,0.00003287138,0.005402887],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.004350936,"threshold_uncertainty_score":0.01455534,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.0627583819039077,"score_gpt":0.3268370546142428,"score_spread":0.2640786727103351,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}