{"id":"W4379279840","doi":"10.1017/cjn.2023.88","title":"C.2 SUNFISH parts 1 and 2: 4-year efficacy and safety data of risdiplam in types 2 and 3 spinal muscular atrophy (SMA)","year":2023,"lang":"en","type":"article","venue":"Canadian Journal of Neurological Sciences / Journal Canadien des Sciences Neurologiques","topic":"Neurogenetic and Muscular Disorders Research","field":"Medicine","cited_by":1,"is_retracted":false,"has_abstract":true,"ca_institutions":"Calgary Laboratory Services","funders":"","keywords":"SMA*; Medicine; Placebo; Tolerability; Spinal muscular atrophy; Population; Internal medicine; Adverse effect; Disease; Pathology","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":true,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"codex-gemma-dda1882f352a","candidate_categories":["sts"],"consensus_categories":[],"category_scores_codex":[0.003572522,0.0001865069,0.0004582994,0.0009028905,0.0006950179,0.0001862172,0.0007224018,0.0001127867,0.00002967175],"category_scores_gemma":[0.002215097,0.0001283254,0.00005879677,0.001141601,0.005779372,0.0003563507,0.0001977913,0.0007112945,6.673865e-7],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.00003007743,"about_ca_system_score_gemma":0.001239695,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.0008055877,"about_ca_topic_score_gemma":0.01671036,"domain_scores_codex":[0.9971138,0.0004834718,0.0005529645,0.0005043288,0.0005709492,0.000774446],"domain_scores_gemma":[0.997844,0.0003456751,0.0002376043,0.0001754114,0.0001615065,0.001235821],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"observational","study_design_gemma":"observational","study_design_scores_codex":[0.0002654876,0.00002356512,0.9832979,0.00003493364,0.00001601361,0.004141148,0.0001942055,0.0001806583,0.0001182823,0.0002503603,0.0001488253,0.01132859],"study_design_scores_gemma":[0.0008437533,0.02856839,0.9557227,0.00007706576,0.00004179927,0.009511678,0.0002565089,0.001227743,0.00002549534,0.001881856,0.001704219,0.0001387976],"study_design_candidate":"observational","study_design_consensus":"observational","genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9920456,0.003306549,0.000003880347,0.003978076,0.0001288345,0.0001843033,0.00001272893,0.000007008841,0.0003329951],"genre_scores_gemma":[0.9933702,0.005546442,0.0004931612,0.0005042909,0.00006811122,8.267098e-7,6.40536e-7,0.000007704616,0.000008614519],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.02854482,"threshold_uncertainty_score":0.9969263,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.0627583819039077,"score_gpt":0.3268370546142428,"score_spread":0.2640786727103351,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}