{"id":"W4379780662","doi":"10.1097/01.ogx.0000943144.42223.f9","title":"In Utero Enzyme-Replacement Therapy for Infantile-Onset Pompe's Disease","year":2023,"lang":"en","type":"article","venue":"Obstetrical & Gynecological Survey","topic":"Lysosomal Storage Disorders Research","field":"Medicine","cited_by":3,"is_retracted":false,"has_abstract":true,"ca_institutions":"Ottawa Hospital; Children's Hospital of Eastern Ontario; University of Ottawa","funders":"","keywords":"Medicine; In utero; Enzyme replacement therapy; Disease; Pediatrics; Internal medicine; Pregnancy; Fetus; Genetics","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.0001813525,0.000153361,0.0003062936,0.0002510991,0.0001785683,0.0001844923,0.000121818,0.0004089144,0.003919329],"category_scores_gemma":[0.0005585531,0.00004786474,0.000293209,0.0001854016,0.00008897464,0.00009180346,0.0001105268,0.0003908745,0.000569935],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.0002412648,"about_ca_system_score_gemma":0.0002543739,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.001138195,"about_ca_topic_score_gemma":0.002129611,"domain_scores_codex":[0.9999386,0.00002121209,0.000006371504,0.000007031847,0.00001341266,0.00001340476],"domain_scores_gemma":[0.9999026,0.00004511459,0.00001471902,0.000003719374,0.000004154416,0.0000296681],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"design_other","study_design_gemma":"not_applicable","study_design_scores_codex":[0.0311766,0.002755935,0.08042688,0.00166628,0.0009013834,0.04677742,0.0003009292,0.0008261999,0.02246002,0.001791908,0.06562894,0.7452875],"study_design_scores_gemma":[0.007242916,0.02211715,0.5191503,0.00184225,0.001795621,0.0929051,0.0004111195,0.001564382,0.01602289,0.00159342,0.3352878,0.00006706837],"study_design_candidate":"not_applicable","study_design_consensus":null,"genre_codex":"empirical","genre_gemma":"review","genre_scores_codex":[0.5635219,0.3650005,0.001612045,0.009607505,0.002807897,0.0002243095,0.003385451,0.0001719091,0.05366855],"genre_scores_gemma":[0.9014859,0.08085375,0.001082944,0.002917519,0.001037508,0.00007759991,0.001674687,0.00001236204,0.01085781],"genre_candidate":"review","genre_consensus":null,"teacher_disagreement_score":0.003919329,"threshold_uncertainty_score":0.01311147,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.07550301283897357,"score_gpt":0.3659560058034184,"score_spread":0.2904529929644448,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}