{"id":"W4382995246","doi":"10.1177/17562864231182934","title":"Cardiac therapies for Duchenne muscular dystrophy","year":2023,"lang":"en","type":"review","venue":"Therapeutic Advances in Neurological Disorders","topic":"Muscle Physiology and Disorders","field":"Biochemistry, Genetics and Molecular Biology","cited_by":18,"is_retracted":false,"has_abstract":true,"ca_institutions":"University of Alberta","funders":"Muscular Dystrophy Canada; Alberta Innovates; Women and Children's Health Research Institute; Children's Health Research Institute","keywords":"Medicine; Duchenne muscular dystrophy; Dystrophin; Intensive care medicine; Disease; Bioinformatics; Cardiomyopathy; Exon skipping; Clinical trial; Muscular dystrophy; Genetic enhancement; Genome editing; CRISPR; Internal medicine; Heart failure; Exon; Gene","routes":{"ca_aff":true,"ca_fund":true,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"codex-gemma-dda1882f352a","candidate_categories":["metaepi_narrow"],"consensus_categories":[],"category_scores_codex":[0.0002500321,0.0006215986,0.00130452,0.0001243772,0.0001179718,0.00001774005,0.0006178036,0.0006624392,0.00001728624],"category_scores_gemma":[0.0001350644,0.0004760122,0.0009190082,0.0003040657,0.0003829817,0.000009611538,0.0001552833,0.0003910609,0.00002545111],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.000007803275,"about_ca_system_score_gemma":0.00006978463,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.000002870239,"about_ca_topic_score_gemma":0.00002067878,"domain_scores_codex":[0.9971762,0.0004561994,0.0005346712,0.001042597,0.0001297537,0.0006605321],"domain_scores_gemma":[0.9987749,0.0003059352,0.0002219903,0.000596613,0.00002891029,0.00007162537],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"design_other","study_design_gemma":"not_applicable","study_design_scores_codex":[0.0002454187,0.0001346955,0.00003846002,0.002138166,0.0002531545,0.000002132781,0.00001435054,0.000136518,0.00003074718,0.0008647399,0.00007265771,0.996069],"study_design_scores_gemma":[0.0004346925,0.0008136891,0.00007328424,0.0001472182,0.0001758248,0.000001082272,0.0000240308,0.0000112067,0.000001033889,0.01120314,0.9866063,0.0005085203],"study_design_candidate":"design_other","study_design_consensus":null,"genre_codex":"review","genre_gemma":"review","genre_scores_codex":[0.0004661829,0.9964038,0.0005852372,0.00008075014,0.0005536257,0.001566646,0.00009738767,0.00007199043,0.000174352],"genre_scores_gemma":[0.000857741,0.996416,0.0001023316,0.0003716111,0.0002110928,0.001385578,0.0004459374,0.0001151866,0.00009450026],"genre_candidate":"review","genre_consensus":"review","teacher_disagreement_score":0.9955605,"threshold_uncertainty_score":0.9997692,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.03475826749725864,"score_gpt":0.3471559604144085,"score_spread":0.3123976929171499,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}