{"id":"W4382995246","doi":"10.1177/17562864231182934","title":"Cardiac therapies for Duchenne muscular dystrophy","year":2023,"lang":"en","type":"review","venue":"Therapeutic Advances in Neurological Disorders","topic":"Muscle Physiology and Disorders","field":"Biochemistry, Genetics and Molecular Biology","cited_by":18,"is_retracted":false,"has_abstract":true,"ca_institutions":"University of Alberta","funders":"Muscular Dystrophy Canada; Alberta Innovates; Women and Children's Health Research Institute; Children's Health Research Institute","keywords":"Medicine; Duchenne muscular dystrophy; Dystrophin; Intensive care medicine; Disease; Bioinformatics; Cardiomyopathy; Exon skipping; Clinical trial; Muscular dystrophy; Genetic enhancement; Genome editing; CRISPR; Internal medicine; Heart failure; Exon; Gene","routes":{"ca_aff":true,"ca_fund":true,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.0003079506,0.0006109789,0.0008288677,0.001783389,0.0002541486,0.0005921843,0.0005641755,0.000828325,0.005102507],"category_scores_gemma":[0.0003434992,0.0001729823,0.0005688035,0.0008973423,0.0002222542,0.0006190776,0.000535415,0.001816277,0.002075402],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.0003365817,"about_ca_system_score_gemma":0.0004797043,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.0005330172,"about_ca_topic_score_gemma":0.001428449,"domain_scores_codex":[0.9998816,0.00001848364,0.00001774177,0.00001903639,0.00005041485,0.00001265101],"domain_scores_gemma":[0.9998858,0.00005959576,0.00001661817,0.000003478019,0.00002380167,0.00001075929],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"design_other","study_design_gemma":"not_applicable","study_design_scores_codex":[0.00007553158,0.0001036627,0.00009060453,0.0138198,0.00006947003,0.0003038325,0.00005870771,0.0002936996,0.004103178,0.002811485,0.0250252,0.9532449],"study_design_scores_gemma":[0.00002394851,0.0001365337,0.000674438,0.003465137,0.0001033782,0.001594782,0.00003159383,0.00007562569,0.0009122365,0.001264564,0.9917035,0.00001428343],"study_design_candidate":"not_applicable","study_design_consensus":null,"genre_codex":"review","genre_gemma":"review","genre_scores_codex":[0.0002368227,0.9974476,0.0001912306,0.0002026249,0.0002028594,0.000007384413,0.00002865398,0.00001200066,0.001670886],"genre_scores_gemma":[0.001108882,0.996904,0.0003101823,0.000253505,0.0001194075,0.00001151905,0.00006375707,0.00000301429,0.001225653],"genre_candidate":"review","genre_consensus":"review","teacher_disagreement_score":0.005102507,"threshold_uncertainty_score":0.01706964,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.03475826749725864,"score_gpt":0.3471559604144085,"score_spread":0.3123976929171499,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}