{"id":"W4383531882","doi":"10.1136/archdischild-2023-325762","title":"Understanding caregiver experiences with disease-modifying therapies for spinal muscular atrophy: a qualitative study","year":2023,"lang":"en","type":"article","venue":"Archives of Disease in Childhood","topic":"Neurogenetic and Muscular Disorders Research","field":"Medicine","cited_by":10,"is_retracted":false,"has_abstract":true,"ca_institutions":"SickKids Foundation; Hospital for Sick Children; Public Health Ontario; University of Toronto","funders":"","keywords":"Medicine; SMA*; Spinal muscular atrophy; Disease; Qualitative research; Neuromuscular disease; Health care; Population; Family medicine; Physical therapy; Pathology","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":true,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.01151622,0.0008089704,0.0009629448,0.001349804,0.01021341,0.003843703,0.001668831,0.001534692,0.003793549],"category_scores_gemma":[0.01915082,0.0006998396,0.0005449771,0.001550918,0.006828762,0.00434937,0.005312948,0.002838841,0.0003695093],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.00702413,"about_ca_system_score_gemma":0.006862952,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.02523476,"about_ca_topic_score_gemma":0.03891593,"domain_scores_codex":[0.9929827,0.004933601,0.0002182564,0.0003272837,0.0004453895,0.001092636],"domain_scores_gemma":[0.9848504,0.01043226,0.001245828,0.0002775362,0.001463993,0.001729854],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"qualitative","study_design_gemma":"qualitative","study_design_scores_codex":[0.00002835282,0.00002385171,0.002944002,0.0001062572,0.000003328438,0.0006984759,0.9935202,0.00001626398,0.0001971877,0.0003817111,0.0003904578,0.001689891],"study_design_scores_gemma":[0.000002063565,0.00002043972,0.0007743115,0.0001114968,0.000002327339,0.00017776,0.9965026,0.0000211256,0.00005469201,0.00007345443,0.002253962,0.00000574045],"study_design_candidate":"qualitative","study_design_consensus":"qualitative","genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9906387,0.001850068,0.001210705,0.002391035,0.00009609476,0.0001261455,0.0001768544,0.00001153447,0.003498761],"genre_scores_gemma":[0.9951983,0.001706957,0.0005469473,0.0007917049,0.00002185266,0.0001663889,0.00007263396,0.00001600379,0.001479148],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.02523476,"threshold_uncertainty_score":0.06090438,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.09929078672461235,"score_gpt":0.381044630825993,"score_spread":0.2817538441013807,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}