{"id":"W4385655000","doi":"10.1097/01.hs9.0000975056.36410.cc","title":"PB2064: THE COMPLETE STUDY: A SINGLE ARM, MULTICENTER OBSERVATIONAL STUDY TO EVALUATE EFFECTIVENESS OF PEGCETACOPLAN UNDER REAL WORLD CONDITIONS IN PATIENTS WITH PAROXYSMAL NOCTURNAL HEMOGLOBINURIA (PNH)","year":2023,"lang":"en","type":"article","venue":"HemaSphere","topic":"Complement system in diseases","field":"Immunology and Microbiology","cited_by":2,"is_retracted":false,"has_abstract":true,"ca_institutions":"","funders":"","keywords":"Paroxysmal nocturnal hemoglobinuria; Eculizumab; Medicine; Anemia; Observational study; Internal medicine; Hemolysis; Hemoglobinuria; Pediatrics; Intensive care medicine; Complement system; Immunology; Antibody","routes":{"ca_aff":false,"ca_fund":false,"ca_venue":false,"about_ca":true,"invisible_to_affiliation_only":true},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.003269239,0.001931648,0.002991829,0.000344633,0.000701022,0.0009994012,0.0008676825,0.001719099,0.004677247],"category_scores_gemma":[0.002906573,0.0007830701,0.002580734,0.0006423475,0.0007832394,0.001572275,0.0008798497,0.002168924,0.001217271],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.00077737,"about_ca_system_score_gemma":0.001584794,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.001070679,"about_ca_topic_score_gemma":0.001569939,"domain_scores_codex":[0.9983127,0.001039439,0.0001001383,0.0002879908,0.000126213,0.0001335238],"domain_scores_gemma":[0.9974536,0.0004015481,0.0008426707,0.0003536912,0.000245567,0.0007028611],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"randomized_trial","study_design_gemma":"observational","study_design_scores_codex":[0.8950941,0.0130994,0.05651379,0.001153311,0.006731213,0.0002315161,0.0001847468,0.0005927816,0.003081878,0.0002371174,0.005128996,0.01795114],"study_design_scores_gemma":[0.6681891,0.176807,0.1438568,0.0001532579,0.004012557,0.0004800466,0.0001671405,0.001126014,0.0005514026,0.0004153571,0.004142127,0.00009925952],"study_design_candidate":"observational","study_design_consensus":null,"genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9837624,0.002334939,0.0006757235,0.000799523,0.0002269552,0.004494029,0.006014438,0.00005729375,0.001634753],"genre_scores_gemma":[0.9725904,0.001482759,0.00237213,0.001808124,0.0007481927,0.008448331,0.01044955,0.00004113841,0.002059379],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.004677247,"threshold_uncertainty_score":0.01728958,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.07548879676121699,"score_gpt":0.3284828945546748,"score_spread":0.2529940977934578,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}