{"id":"W4385655000","doi":"10.1097/01.hs9.0000975056.36410.cc","title":"PB2064: THE COMPLETE STUDY: A SINGLE ARM, MULTICENTER OBSERVATIONAL STUDY TO EVALUATE EFFECTIVENESS OF PEGCETACOPLAN UNDER REAL WORLD CONDITIONS IN PATIENTS WITH PAROXYSMAL NOCTURNAL HEMOGLOBINURIA (PNH)","year":2023,"lang":"en","type":"article","venue":"HemaSphere","topic":"Complement system in diseases","field":"Immunology and Microbiology","cited_by":2,"is_retracted":false,"has_abstract":true,"ca_institutions":"","funders":"","keywords":"Paroxysmal nocturnal hemoglobinuria; Eculizumab; Medicine; Anemia; Observational study; Internal medicine; Hemolysis; Hemoglobinuria; Pediatrics; Intensive care medicine; Complement system; Immunology; Antibody","routes":{"ca_aff":false,"ca_fund":false,"ca_venue":false,"about_ca":true,"invisible_to_affiliation_only":true},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"codex-gemma-dda1882f352a","candidate_categories":["insufficient_payload"],"consensus_categories":[],"category_scores_codex":[0.0006374415,0.0002425743,0.0004297264,0.0001252914,0.0002146696,0.00002308228,0.000307016,0.00003516977,0.001037596],"category_scores_gemma":[0.00005714738,0.0001703769,0.00006825922,0.0006519529,0.0001020545,0.00008136991,0.0001949715,0.0001738772,0.000229742],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.0001476281,"about_ca_system_score_gemma":0.0000816977,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.0004363607,"about_ca_topic_score_gemma":0.004867287,"domain_scores_codex":[0.9971832,0.001340415,0.0004972897,0.000401283,0.000208513,0.0003692961],"domain_scores_gemma":[0.9983372,0.0007953585,0.0001815905,0.0004310644,0.000217073,0.00003770529],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"observational","study_design_gemma":"observational","study_design_scores_codex":[0.001608931,0.005570133,0.9865759,0.00006713701,0.0004660613,0.000008540156,0.001269579,0.001570661,0.001860303,0.0001048667,0.0008714456,0.00002643078],"study_design_scores_gemma":[0.008961699,0.001741726,0.9834053,0.0001986704,0.0001375256,0.000001238813,0.005026862,0.00001806126,0.0001645674,0.00006358349,0.00009510092,0.0001856665],"study_design_candidate":"observational","study_design_consensus":"observational","genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9952416,0.00002532275,0.00001086548,0.00007356723,0.00032876,0.003758557,0.0003082204,0.00006267946,0.0001904198],"genre_scores_gemma":[0.9987636,1.927882e-7,0.00001417602,0.0000523908,0.00001872829,0.000381615,0.0004649356,0.00002616886,0.0002781602],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.007352768,"threshold_uncertainty_score":0.9998756,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.07548879676121699,"score_gpt":0.3284828945546748,"score_spread":0.2529940977934578,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}