{"id":"W4386021623","doi":"10.1097/01.hs9.0000967992.84731.80","title":"S270: TRANSFUSION INDEPENDENCE AFTER EXAGAMGLOGENE AUTOTEMCEL IN PATIENTS WITH TRANSFUSION-DEPENDENT ΒETA-THALASSEMIA","year":2023,"lang":"en","type":"article","venue":"HemaSphere","topic":"Prenatal Screening and Diagnostics","field":"Medicine","cited_by":2,"is_retracted":false,"has_abstract":true,"ca_institutions":"SickKids Foundation; Hospital for Sick Children; University of Toronto; BC Children's Hospital; University of British Columbia","funders":"","keywords":"Medicine; Thalassemia; Clinical endpoint; Internal medicine; Blood transfusion; Pediatrics; Clinical trial","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.0003891324,0.0002096807,0.0005086031,0.000115226,0.000165375,0.0004279357,0.0001809465,0.0003643828,0.007094325],"category_scores_gemma":[0.0005049035,0.00006521453,0.0006895383,0.0001623123,0.0001470669,0.0002546131,0.0001679489,0.0007987022,0.0006723717],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.0003448515,"about_ca_system_score_gemma":0.0005163525,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.0002741244,"about_ca_topic_score_gemma":0.0006515131,"domain_scores_codex":[0.9998958,0.00003998814,0.000009698638,0.00001594434,0.00001305254,0.00002546576],"domain_scores_gemma":[0.9997252,0.00007377207,0.00007107653,0.000009356069,0.00001946973,0.0001012574],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"design_other","study_design_gemma":"observational","study_design_scores_codex":[0.3554657,0.00456691,0.03756411,0.00292458,0.001190309,0.001020137,0.0002801867,0.001831995,0.0235821,0.00105756,0.02910731,0.5414091],"study_design_scores_gemma":[0.2370257,0.4229849,0.1987774,0.002087949,0.004311954,0.005035359,0.0004424052,0.00556212,0.02798546,0.002498757,0.09317851,0.0001094616],"study_design_candidate":"observational","study_design_consensus":null,"genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9697296,0.01611759,0.000617119,0.002402389,0.0003657496,0.0004175006,0.001644162,0.0001151375,0.008590766],"genre_scores_gemma":[0.9888758,0.0044187,0.0004743761,0.001345369,0.0003266847,0.000291351,0.001574117,0.00001995602,0.002673713],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.007094325,"threshold_uncertainty_score":0.0237329,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.008949082000055683,"score_gpt":0.2283407603991669,"score_spread":0.2193916783991112,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}