{"id":"W4386021623","doi":"10.1097/01.hs9.0000967992.84731.80","title":"S270: TRANSFUSION INDEPENDENCE AFTER EXAGAMGLOGENE AUTOTEMCEL IN PATIENTS WITH TRANSFUSION-DEPENDENT ΒETA-THALASSEMIA","year":2023,"lang":"en","type":"article","venue":"HemaSphere","topic":"Prenatal Screening and Diagnostics","field":"Medicine","cited_by":2,"is_retracted":false,"has_abstract":true,"ca_institutions":"SickKids Foundation; Hospital for Sick Children; University of Toronto; BC Children's Hospital; University of British Columbia","funders":"","keywords":"Medicine; Thalassemia; Clinical endpoint; Internal medicine; Blood transfusion; Pediatrics; Clinical trial","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"codex-gemma-dda1882f352a","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.0002182053,0.0002795061,0.0003874922,0.0001217136,0.00006738996,0.00002192169,0.0001338291,0.0002720359,0.0008392116],"category_scores_gemma":[0.00009602398,0.0002174308,0.00009088959,0.0006404004,0.00005671755,0.0001310644,0.00005339347,0.0004625851,0.0002812664],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.000102836,"about_ca_system_score_gemma":0.0001381008,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.0003561619,"about_ca_topic_score_gemma":0.0006648732,"domain_scores_codex":[0.9976988,0.00005315469,0.0003527096,0.0005252741,0.0008630173,0.0005070243],"domain_scores_gemma":[0.999036,0.0001322817,0.00005129998,0.0004212369,0.0001015764,0.0002575806],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"observational","study_design_gemma":"observational","study_design_scores_codex":[0.001405307,0.0004243194,0.9808366,0.0001701474,0.00004108378,0.0008378787,0.0005241172,0.0001881282,0.0007045454,0.0000245787,0.0004026772,0.01444061],"study_design_scores_gemma":[0.004838426,0.0005592523,0.9903209,0.0006889051,0.00007957823,0.0000230062,0.0001736621,0.0002060494,0.0024748,0.00005558566,0.0002928509,0.0002869923],"study_design_candidate":"observational","study_design_consensus":"observational","genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9946184,0.0002272882,0.0004023368,0.0002858774,0.0001359409,0.0007056473,0.00004466173,0.0002459876,0.003333866],"genre_scores_gemma":[0.9979139,0.0001758907,0.0005557546,0.000197992,0.00006148119,0.0001015612,0.00009369128,0.00005399812,0.0008457619],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.01415362,"threshold_uncertainty_score":0.9188778,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.008949082000055683,"score_gpt":0.2283407603991669,"score_spread":0.2193916783991112,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}