{"id":"W4386548380","doi":"10.2196/46363","title":"Twice-Weekly Outpatient Rehabilitation Intervention for Young Children With Spinal Muscular Atrophy Treated With Genetic-Based Therapies: Protocol for a Feasibility Study","year":2023,"lang":"en","type":"article","venue":"JMIR Research Protocols","topic":"Neurogenetic and Muscular Disorders Research","field":"Medicine","cited_by":3,"is_retracted":false,"has_abstract":true,"ca_institutions":"University of Toronto; Holland Bloorview Kids Rehabilitation Hospital","funders":"","keywords":"Medicine; Rehabilitation; Physical therapy; Psychological intervention; Tolerability; Clinical trial; Spinal muscular atrophy; SMA*; Randomized controlled trial; Intervention (counseling); Physical medicine and rehabilitation; Adverse effect; Surgery; Nursing; Internal medicine; Disease","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":true,"about_ca":true,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"codex-gemma-dda1882f352a","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.002483962,0.0003564247,0.0004896239,0.000625744,0.0004334503,0.0001571795,0.0003404719,0.0001332868,0.00004760224],"category_scores_gemma":[0.0004306685,0.0002414022,0.0003182657,0.001388619,0.0003901107,0.0001075673,0.00009497747,0.0004653218,0.0000158882],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.0002704133,"about_ca_system_score_gemma":0.0005677458,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.0001060351,"about_ca_topic_score_gemma":0.0001063591,"domain_scores_codex":[0.9944914,0.0009697627,0.0005803554,0.001132241,0.001834732,0.0009915348],"domain_scores_gemma":[0.9963406,0.0002463806,0.000153465,0.001091019,0.001869567,0.0002989593],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"observational","study_design_gemma":"observational","study_design_scores_codex":[0.1088163,0.01699961,0.8433706,0.00594445,0.0004998548,0.00003030067,0.001072999,0.00007473454,0.002175388,0.00001831878,0.001672278,0.01932525],"study_design_scores_gemma":[0.05229815,0.2541519,0.683025,0.001916781,0.00003676573,0.000007031504,0.001444287,0.0008511355,0.0009810763,0.00009121268,0.004912283,0.0002843833],"study_design_candidate":"observational","study_design_consensus":"observational","genre_codex":"protocol","genre_gemma":"protocol","genre_scores_codex":[0.3483641,0.000001192822,0.001517347,0.0003125916,0.000001464088,0.6496472,0.00002302048,0.0001177979,0.00001537595],"genre_scores_gemma":[0.1027764,8.079599e-8,0.002822097,0.00001497645,0.00007040408,0.8938662,0.00008360294,0.0001159871,0.000250178],"genre_candidate":"protocol","genre_consensus":"protocol","teacher_disagreement_score":0.2455877,"threshold_uncertainty_score":0.9844097,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.1859211017293542,"score_gpt":0.5321306806031957,"score_spread":0.3462095788738414,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}