{"id":"W4387310502","doi":"10.1016/j.nmd.2023.07.304","title":"P195 The Canadian neuromuscular disease registry: a national Duchenne muscular dystrophy registry for post-marketing surveillance","year":2023,"lang":"en","type":"article","venue":"Neuromuscular Disorders","topic":"Biomedical Ethics and Regulation","field":"Medicine","cited_by":0,"is_retracted":false,"has_abstract":false,"ca_institutions":"Muscular Dystrophy Canada; University of Calgary; Dalhousie University","funders":"","keywords":"Medicine; Disease registry; Duchenne muscular dystrophy; Neuromuscular disease; Stakeholder; Muscular dystrophy; Clinical trial; Family medicine; Inclusion (mineral); Disease; Physical therapy; Pathology; Psychology; Public relations; Internal medicine; Political science","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":true,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.00519988,0.0003732074,0.0004242245,0.003034896,0.003363169,0.00375528,0.001644277,0.002128247,0.02753494],"category_scores_gemma":[0.01799781,0.0004399151,0.0005333079,0.004527411,0.0009505208,0.0007415296,0.001061099,0.00113031,0.005248403],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.02207474,"about_ca_system_score_gemma":0.1613487,"about_ca_topic_candidate":true,"about_ca_topic_consensus":true,"about_ca_topic_score_codex":0.9452238,"about_ca_topic_score_gemma":0.9684491,"domain_scores_codex":[0.9949813,0.0004736683,0.000316667,0.0002274604,0.002943453,0.00105734],"domain_scores_gemma":[0.9694602,0.003929267,0.00181477,0.001069395,0.01882233,0.004904109],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"not_applicable","study_design_gemma":"observational","study_design_scores_codex":[0.000132007,0.0001008146,0.05058918,0.0001217851,0.00002412371,0.0002710067,0.0002032761,0.0001640053,0.0002367686,0.004258738,0.9094859,0.03441233],"study_design_scores_gemma":[0.0002602622,0.00006523504,0.2799989,0.0003347726,0.00004696728,0.0002670597,0.0005786225,0.0009223646,0.0004099743,0.0006583299,0.7164068,0.00005066624],"study_design_candidate":"observational","study_design_consensus":null,"genre_codex":"other","genre_gemma":"empirical","genre_scores_codex":[0.08456245,0.004268243,0.004365236,0.1221433,0.004513028,0.009735792,0.190806,0.001223347,0.5783826],"genre_scores_gemma":[0.3733805,0.004739029,0.01981925,0.05688391,0.002952636,0.005137803,0.1087827,0.0006497391,0.4276545],"genre_candidate":"empirical","genre_consensus":null,"teacher_disagreement_score":0.05477619,"threshold_uncertainty_score":0.1601642,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.01541779073237711,"score_gpt":0.267361937432199,"score_spread":0.2519441466998219,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}