{"id":"W4389230681","doi":"10.1182/blood-2023-173366","title":"Durable Symptom Improvement for Patients with Non-Transfusion Dependent Thalassemia Treated with Luspatercept: Patient-Reported Outcomes from the BEYOND Study","year":2023,"lang":"en","type":"article","venue":"Blood","topic":"Hemoglobinopathies and Related Disorders","field":"Medicine","cited_by":6,"is_retracted":false,"has_abstract":true,"ca_institutions":"University of Toronto","funders":"","keywords":"Medicine; Dosing; Placebo; Anemia; Thalassemia; Internal medicine; Physical therapy; Alternative medicine","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"codex-gemma-dda1882f352a","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.0001230726,0.0003228085,0.0004201061,0.00008144045,0.0002798908,0.00004192755,0.0001197354,0.0001201406,0.00005178833],"category_scores_gemma":[0.00002742609,0.0001542002,0.00009610353,0.0003705876,0.00004437913,0.00006898463,0.00004812872,0.0001979825,0.00001796528],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.00004293724,"about_ca_system_score_gemma":0.00008413901,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.001140471,"about_ca_topic_score_gemma":0.0003148268,"domain_scores_codex":[0.9979787,0.00003223224,0.0004185425,0.0005083355,0.0006203972,0.0004417273],"domain_scores_gemma":[0.9988479,0.0001089685,0.000164576,0.000539983,0.0001992007,0.0001393843],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"observational","study_design_gemma":"observational","study_design_scores_codex":[0.0007801303,0.003562314,0.988227,0.00003008322,0.001367372,0.0001012147,0.002379167,0.00002301445,0.001405098,3.93771e-7,0.0002301908,0.001894083],"study_design_scores_gemma":[0.03353842,0.007181852,0.9482039,0.000142237,0.002036602,0.000005425751,0.005732351,0.00005999417,0.002774221,0.000006928645,0.00005805169,0.0002600735],"study_design_candidate":"observational","study_design_consensus":"observational","genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9941766,0.00002341296,0.00002175119,0.0003479393,0.0001183993,0.004777017,0.00008847474,0.0001705226,0.0002758396],"genre_scores_gemma":[0.998392,0.00004146347,0.00005962133,0.0001992962,0.00002382279,0.000415513,0.0004593295,0.00006758679,0.0003413141],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.04002309,"threshold_uncertainty_score":0.6288103,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.005952660741951309,"score_gpt":0.2170941259203972,"score_spread":0.2111414651784459,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}