{"id":"W4394600820","doi":"10.1212/wnl.0000000000205716","title":"Delphi Consensus Panel on Assessing Clinically Meaningful Treatment Outcomes in Adults Living with Spinal Muscular Atrophy (SMA) (P2-11.007)","year":2024,"lang":"en","type":"article","venue":"Neurology","topic":"Neurogenetic and Muscular Disorders Research","field":"Medicine","cited_by":0,"is_retracted":false,"has_abstract":true,"ca_institutions":"Stan Cassidy Foundation","funders":"","keywords":"SMA*; Spinal muscular atrophy; Medicine; Physical medicine and rehabilitation; Physical therapy; Atrophy; Delphi method; Pathology; Disease; Computer science","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":["metaresearch"],"consensus_categories":[],"category_scores_codex":[0.2868001,0.001096961,0.00193702,0.004527458,0.004505051,0.003857628,0.003978223,0.007919106,0.007631011],"category_scores_gemma":[0.2705616,0.001199819,0.004962713,0.002743952,0.003517734,0.003272855,0.01275027,0.01038475,0.003127486],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.008172837,"about_ca_system_score_gemma":0.0596506,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.006635365,"about_ca_topic_score_gemma":0.007681874,"domain_scores_codex":[0.8128625,0.1269511,0.03160225,0.003565507,0.01705802,0.00796058],"domain_scores_gemma":[0.6491627,0.1689273,0.009035682,0.01093422,0.1442179,0.01772229],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"not_applicable","study_design_gemma":"qualitative","study_design_scores_codex":[0.001895175,0.0009539637,0.02023975,0.02090141,0.001026784,0.001172455,0.05111643,0.003244742,0.006587301,0.03324799,0.4637941,0.39582],"study_design_scores_gemma":[0.002164407,0.00159472,0.04535491,0.07424596,0.000845972,0.001991506,0.04951743,0.006696071,0.004144939,0.04844701,0.7640116,0.0009854984],"study_design_candidate":"qualitative","study_design_consensus":null,"genre_codex":"commentary","genre_gemma":"methods","genre_scores_codex":[0.08966931,0.02232662,0.103438,0.4655976,0.02159331,0.1271799,0.01016267,0.000761244,0.1592715],"genre_scores_gemma":[0.3741599,0.01530211,0.2824455,0.119205,0.00323952,0.1832103,0.01029328,0.0003847293,0.01175963],"genre_candidate":"methods","genre_consensus":null,"teacher_disagreement_score":0.2868001,"threshold_uncertainty_score":0.8795024,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.0499206488106331,"score_gpt":0.3583272347439351,"score_spread":0.3084065859333019,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}