{"id":"W4399707657","doi":"10.1007/s40265-024-02051-2","title":"Treatment Options in Spinal Muscular Atrophy: A Pragmatic Approach for Clinicians","year":2024,"lang":"en","type":"review","venue":"Drugs","topic":"Neurogenetic and Muscular Disorders Research","field":"Medicine","cited_by":12,"is_retracted":false,"has_abstract":false,"ca_institutions":"McGill University; McGill University Health Centre","funders":"Biogen","keywords":"Spinal muscular atrophy; SMA*; Medicine; Clinical trial; Physical medicine and rehabilitation; Physical therapy; Disease; Intensive care medicine; Pathology","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.002495331,0.00117742,0.003457719,0.002341688,0.0005639567,0.002668521,0.001524312,0.003789468,0.006460719],"category_scores_gemma":[0.003643431,0.0004527133,0.001291191,0.001518225,0.0009650013,0.003092131,0.001403689,0.006215952,0.002130898],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.001562181,"about_ca_system_score_gemma":0.002732453,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.00165292,"about_ca_topic_score_gemma":0.005723727,"domain_scores_codex":[0.9992304,0.0002975848,0.000148006,0.00008678913,0.000185957,0.00005120534],"domain_scores_gemma":[0.9973311,0.00199948,0.0002258779,0.00003383527,0.0003066896,0.0001029496],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"design_other","study_design_gemma":"not_applicable","study_design_scores_codex":[0.000223226,0.0001254621,0.000192944,0.03998069,0.0003054701,0.000438041,0.0001287272,0.0005457306,0.0006344075,0.01054355,0.09160176,0.8552799],"study_design_scores_gemma":[0.0001780106,0.0001460311,0.000565042,0.044323,0.0004977857,0.001146285,0.0001715221,0.0002250894,0.0001333431,0.009009498,0.9435564,0.00004796325],"study_design_candidate":"not_applicable","study_design_consensus":null,"genre_codex":"review","genre_gemma":"review","genre_scores_codex":[0.00003828434,0.9947456,0.0001862776,0.003501512,0.0004919869,0.000007422636,0.00002011062,0.0000100142,0.0009987921],"genre_scores_gemma":[0.0008799097,0.99192,0.0009326581,0.004470903,0.001091086,0.00002933883,0.00003512034,0.000003955958,0.0006369675],"genre_candidate":"review","genre_consensus":"review","teacher_disagreement_score":0.006460719,"threshold_uncertainty_score":0.0216133,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.09045282201644811,"score_gpt":0.4430056190012872,"score_spread":0.352552796984839,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}