{"id":"W4404052172","doi":"10.3325/cmj.2024.65.454","title":"Could choosing risdiplam instead of nusinersen in the treatment of type 1 spinal muscular atrophy be a huge cost-minimization opportunity?","year":2024,"lang":"en","type":"article","venue":"Croatian Medical Journal","topic":"Neurogenetic and Muscular Disorders Research","field":"Medicine","cited_by":5,"is_retracted":false,"has_abstract":false,"ca_institutions":"Vancouver Coastal Health","funders":"","keywords":"Spinal muscular atrophy; Cost-minimization analysis; Medicine; Minification; Physical medicine and rehabilitation; Computer science; Physical therapy; Surgery; Internal medicine; Disease","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.0009477964,0.0004155298,0.001769415,0.000458661,0.0002952168,0.001054866,0.0009545207,0.00161097,0.01924534],"category_scores_gemma":[0.001423335,0.0001538723,0.00124744,0.0003407235,0.0004443723,0.0009453092,0.0003875003,0.003124072,0.001973784],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.000572357,"about_ca_system_score_gemma":0.001430927,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.001458464,"about_ca_topic_score_gemma":0.004871211,"domain_scores_codex":[0.9996346,0.0001127966,0.00004422748,0.00008305799,0.0000663833,0.0000588761],"domain_scores_gemma":[0.9994076,0.0002448608,0.00008248301,0.00003055611,0.0000695281,0.0001649299],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"design_other","study_design_gemma":"theoretical_or_conceptual","study_design_scores_codex":[0.02745416,0.002881,0.00735028,0.004200254,0.001351318,0.002940646,0.0001362556,0.003405934,0.0155831,0.01166044,0.02566718,0.8973694],"study_design_scores_gemma":[0.03281696,0.0390538,0.06545949,0.009873981,0.006220248,0.02190639,0.001807163,0.006561279,0.01441647,0.04006754,0.7611519,0.0006647696],"study_design_candidate":"theoretical_or_conceptual","study_design_consensus":null,"genre_codex":"review","genre_gemma":"empirical","genre_scores_codex":[0.3354273,0.4166585,0.01614868,0.1538987,0.01231932,0.0008318899,0.002302246,0.0006300877,0.06178346],"genre_scores_gemma":[0.7776729,0.1233483,0.03183252,0.03998458,0.005361244,0.0004751459,0.00138645,0.0001774035,0.01976132],"genre_candidate":"empirical","genre_consensus":null,"teacher_disagreement_score":0.01924534,"threshold_uncertainty_score":0.06438214,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.06710551458483013,"score_gpt":0.3796128894036102,"score_spread":0.31250737481878,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}