{"id":"W4405038931","doi":"10.1182/blood-2024-204001","title":"Durable Clinical Benefits with Exagamglogene Autotemcel for Severe Sickle Cell Disease","year":2024,"lang":"en","type":"article","venue":"Blood","topic":"Hemoglobinopathies and Related Disorders","field":"Medicine","cited_by":3,"is_retracted":false,"has_abstract":true,"ca_institutions":"SickKids Foundation; Hospital for Sick Children; University of Toronto","funders":"","keywords":"Medicine; Disease; Intensive care medicine; Internal medicine","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.0007320407,0.0002264169,0.0005787947,0.0001510359,0.0001705918,0.0004000297,0.0001880442,0.0003778751,0.004602655],"category_scores_gemma":[0.0007773064,0.00005284579,0.0005630959,0.0001108319,0.0001605409,0.0003335995,0.0002082583,0.0009107222,0.0004563431],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.0001998974,"about_ca_system_score_gemma":0.000269817,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.0001778341,"about_ca_topic_score_gemma":0.0005713143,"domain_scores_codex":[0.9997885,0.00006991118,0.00001871442,0.00003415502,0.00004535025,0.00004339961],"domain_scores_gemma":[0.9994584,0.0001734468,0.0001210861,0.00004618485,0.0000532678,0.0001476839],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"design_other","study_design_gemma":"observational","study_design_scores_codex":[0.04784118,0.008039108,0.01453598,0.00161004,0.0009627513,0.0007414036,0.0002396875,0.001159805,0.08004823,0.001053048,0.01570006,0.8280687],"study_design_scores_gemma":[0.06385306,0.4239284,0.2968566,0.001304495,0.002243008,0.01103428,0.0004716439,0.004566323,0.05802872,0.002632331,0.1349439,0.0001372136],"study_design_candidate":"observational","study_design_consensus":null,"genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9623189,0.02375498,0.002751445,0.001598159,0.0002837939,0.0003027777,0.001367434,0.0003507833,0.007271664],"genre_scores_gemma":[0.9924288,0.002624245,0.0009556398,0.001125368,0.0001658375,0.0001224757,0.001023161,0.00001946184,0.00153494],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.004602655,"threshold_uncertainty_score":0.01539737,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.01591468730630843,"score_gpt":0.266319517157481,"score_spread":0.2504048298511726,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}