{"id":"W4405043258","doi":"10.1182/blood-2024-205779","title":"Durable Clinical Benefits with Exagamglogene Autotemcel for Transfusion-Dependent β-Thalassemia","year":2024,"lang":"en","type":"article","venue":"Blood","topic":"Hemoglobinopathies and Related Disorders","field":"Medicine","cited_by":3,"is_retracted":false,"has_abstract":true,"ca_institutions":"University of British Columbia; SickKids Foundation; Hospital for Sick Children; BC Children's Hospital; University of Toronto","funders":"","keywords":"Thalassemia; Medicine; Blood transfusion; Intensive care medicine; Pediatrics; Immunology; Internal medicine","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.0006303455,0.0002659147,0.0005238281,0.0001511324,0.0001487217,0.0004411949,0.0002087895,0.0003354699,0.003862296],"category_scores_gemma":[0.0005709583,0.00007407773,0.0005178015,0.0001076715,0.000172808,0.0003080354,0.0001759673,0.001031433,0.0004731987],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.0002446474,"about_ca_system_score_gemma":0.0002832532,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.0001910544,"about_ca_topic_score_gemma":0.0004831453,"domain_scores_codex":[0.9998591,0.00004149106,0.0000123283,0.0000285525,0.00002652467,0.00003199986],"domain_scores_gemma":[0.999632,0.0001017289,0.00009435295,0.00003779645,0.00003396246,0.0001000679],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"design_other","study_design_gemma":"observational","study_design_scores_codex":[0.0621513,0.01085296,0.01565364,0.001479773,0.0009215836,0.001079158,0.000301026,0.00106685,0.1250616,0.000831704,0.01194858,0.7686518],"study_design_scores_gemma":[0.07409702,0.5319209,0.2000352,0.0009958295,0.002372065,0.01357513,0.0004257254,0.003892202,0.07224013,0.001552978,0.09877754,0.0001152761],"study_design_candidate":"observational","study_design_consensus":null,"genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.976823,0.0134701,0.002200913,0.0009232012,0.0001816837,0.0003229816,0.000876327,0.0003240176,0.004877781],"genre_scores_gemma":[0.9933169,0.002059827,0.001047707,0.0008393968,0.00009698809,0.0001598755,0.0008399317,0.00002530781,0.001614133],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.003862296,"threshold_uncertainty_score":0.01292068,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.01872442205762847,"score_gpt":0.2836189345401104,"score_spread":0.264894512482482,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}