{"id":"W4405048868","doi":"10.1182/blood-2024-211188","title":"Non-Factor Therapy Reduces Burden of Care for Caregivers of Children with Severe Hemophilia a: A Longitudinal Cohort Study Using the Hemophilia Family Impact Tool (H-FIT v1.1)","year":2024,"lang":"en","type":"article","venue":"Blood","topic":"Hemophilia Treatment and Research","field":"Medicine","cited_by":0,"is_retracted":false,"has_abstract":true,"ca_institutions":"SickKids Foundation; University of Toronto; Hospital for Sick Children","funders":"Novo Nordisk","keywords":"Medicine; Haemophilia; Clotting factor; Pediatrics; Cohort; Factor IX; Internal medicine; Physical therapy","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.001496196,0.0003682272,0.0004266416,0.0005554725,0.001082494,0.0009585022,0.000457174,0.000591877,0.001680822],"category_scores_gemma":[0.00363699,0.000455268,0.001117913,0.0008263375,0.0002011529,0.0008604538,0.0006591339,0.001568738,0.0002756229],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.0006727227,"about_ca_system_score_gemma":0.0008346993,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.01950483,"about_ca_topic_score_gemma":0.02452415,"domain_scores_codex":[0.9994144,0.0001596817,0.00004949857,0.0001119883,0.0001128687,0.0001515805],"domain_scores_gemma":[0.9983031,0.0001566054,0.0008377609,0.0001091461,0.0002655295,0.0003278076],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"observational","study_design_gemma":"observational","study_design_scores_codex":[0.0002955868,0.0002821752,0.9968253,0.00002220936,0.0001198871,0.00006603917,0.0004311806,0.00001649398,0.0000555147,0.00001419025,0.0002548441,0.001616387],"study_design_scores_gemma":[0.00004079995,0.000574534,0.9977415,0.00003477525,0.00009102542,0.0001795439,0.0009022313,0.00008270635,0.00002844286,0.00001602179,0.0002999743,0.000008458418],"study_design_candidate":"observational","study_design_consensus":"observational","genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9990319,0.0002567019,0.00003401492,0.00006914747,0.000009171876,0.00002465766,0.0004111883,0.000001235211,0.0001620933],"genre_scores_gemma":[0.9984716,0.0003231002,0.0001196512,0.0000641141,0.00001182939,0.00005765586,0.0006557343,0.000001947937,0.000294437],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.01950483,"threshold_uncertainty_score":0.0387826,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.03389536429052385,"score_gpt":0.3307208482085037,"score_spread":0.2968254839179798,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}