{"id":"W4409488299","doi":"10.1056/nejmoa2307159","title":"Fidanacogene Elaparvovec for Hemophilia B — A Multiyear Follow-up Study","year":2025,"lang":"en","type":"article","venue":"New England Journal of Medicine","topic":"Hemophilia Treatment and Research","field":"Medicine","cited_by":19,"is_retracted":false,"has_abstract":true,"ca_institutions":"University of Toronto; St. Michael's Hospital","funders":"Pfizer","keywords":"Political science","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.002328367,0.0004563897,0.0007370263,0.0005674404,0.001070436,0.0009418071,0.0004675571,0.001121027,0.001969215],"category_scores_gemma":[0.0018509,0.000317078,0.0007098527,0.0006033674,0.0002848255,0.0009188162,0.0004284428,0.001344195,0.0006052728],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.0005157059,"about_ca_system_score_gemma":0.0005197563,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.001721933,"about_ca_topic_score_gemma":0.001662416,"domain_scores_codex":[0.9992223,0.0002436942,0.00005514104,0.0001518866,0.0001931503,0.0001337548],"domain_scores_gemma":[0.9983158,0.000167277,0.0005480163,0.0001710974,0.000328221,0.0004695589],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"observational","study_design_gemma":"observational","study_design_scores_codex":[0.05660899,0.01154405,0.8581637,0.0004349179,0.003364115,0.0006918467,0.0005750538,0.0002271071,0.004426801,0.0001557025,0.003566223,0.06024163],"study_design_scores_gemma":[0.005431877,0.03123069,0.9550688,0.000116884,0.001406082,0.000701404,0.0002233687,0.0003047941,0.0005245704,0.0001067005,0.004842294,0.00004249439],"study_design_candidate":"observational","study_design_consensus":"observational","genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.994551,0.002982408,0.0002165987,0.0001964606,0.00003644324,0.0002697294,0.0006578314,0.00001559419,0.001074],"genre_scores_gemma":[0.9962875,0.0007793426,0.0002511133,0.0003919042,0.00005111231,0.0002150243,0.001130938,0.000004900228,0.0008882691],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.002328367,"threshold_uncertainty_score":0.01231372,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.03778149658422426,"score_gpt":0.3604893753141291,"score_spread":0.3227078787299049,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}