{"id":"W4411403814","doi":"10.1016/j.jacl.2025.06.014","title":"Patient experience with familial chylomicronemia syndrome before and after olezarsen treatment: Qualitative interviews with clinical trial participants","year":2025,"lang":"en","type":"article","venue":"Journal of clinical lipidology","topic":"Lipid metabolism and disorders","field":"Medicine","cited_by":2,"is_retracted":false,"has_abstract":true,"ca_institutions":"Centre hospitalier de l'Université Laval; Université de Montréal; Centre hospitalier universitaire de Québec; Montreal Clinical Research Institute","funders":"Ionis Pharmaceuticals","keywords":"Medicine; Clinical trial; Pediatrics; Physical therapy; Family medicine; Internal medicine","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.02659101,0.0005935127,0.001077805,0.0008352598,0.004932517,0.00327047,0.002052825,0.00219064,0.002674578],"category_scores_gemma":[0.0522835,0.0006241784,0.0006231792,0.0011541,0.004554925,0.003242064,0.005025235,0.003877895,0.0003480678],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.004338125,"about_ca_system_score_gemma":0.004730172,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.005287946,"about_ca_topic_score_gemma":0.008343638,"domain_scores_codex":[0.9672633,0.02858404,0.0008584408,0.0006892558,0.0009533843,0.001651592],"domain_scores_gemma":[0.9513965,0.03869897,0.003640085,0.000638585,0.00226382,0.003362152],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"qualitative","study_design_gemma":"qualitative","study_design_scores_codex":[0.0003464502,0.000110018,0.003835382,0.0003453054,0.00001647524,0.0005324431,0.9867589,0.00006766718,0.0006525514,0.0003295302,0.0007001542,0.006305121],"study_design_scores_gemma":[0.00004755002,0.0003019745,0.002559679,0.0002868654,0.00001471679,0.0002037803,0.9899291,0.0001472369,0.0002875046,0.0002327335,0.005955424,0.00003335345],"study_design_candidate":"qualitative","study_design_consensus":"qualitative","genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9892967,0.001465281,0.00166857,0.003519255,0.0001007506,0.0007269409,0.0002569711,0.00001991426,0.002945636],"genre_scores_gemma":[0.9928347,0.001035437,0.001519319,0.001796035,0.00004132526,0.001353177,0.0001641624,0.00002160061,0.001234281],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.02659101,"threshold_uncertainty_score":0.1406283,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.1153734872179014,"score_gpt":0.479847142103922,"score_spread":0.3644736548860207,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}