{"id":"W4413361938","doi":"10.1177/22143602251366721","title":"Association between exon-skipping therapy with eteplirsen and cardiac outcomes in Duchenne muscular dystrophy","year":2025,"lang":"en","type":"article","venue":"Journal of Neuromuscular Diseases","topic":"Muscle Physiology and Disorders","field":"Biochemistry, Genetics and Molecular Biology","cited_by":4,"is_retracted":false,"has_abstract":true,"ca_institutions":"Health Care Foundation","funders":"Sarepta Therapeutics","keywords":"Medicine; Hazard ratio; Internal medicine; Confidence interval","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.001314726,0.0001465441,0.0003107236,0.0002603904,0.0001709073,0.0003839449,0.0002299972,0.0004100259,0.001179996],"category_scores_gemma":[0.002753877,0.0001000541,0.0005889499,0.0002858603,0.0001848915,0.0002431269,0.0002404071,0.0005158252,0.00006410388],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.0002324398,"about_ca_system_score_gemma":0.0001739398,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.0005168464,"about_ca_topic_score_gemma":0.0004905568,"domain_scores_codex":[0.9994105,0.0002512697,0.00007009569,0.0001272636,0.00007128248,0.00006962849],"domain_scores_gemma":[0.9965729,0.001238628,0.00159886,0.0001684327,0.00009758219,0.0003237656],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"observational","study_design_gemma":"observational","study_design_scores_codex":[0.004131593,0.000143099,0.9908267,0.00002758641,0.000369988,0.00009958843,0.00002216055,0.0002523041,0.00033353,0.00003757541,0.00008241531,0.003673462],"study_design_scores_gemma":[0.0001127912,0.0008384486,0.9978741,0.000008497076,0.0001732406,0.0001998983,0.00002594351,0.000484177,0.0001162123,0.00005108033,0.0001112083,0.000004408465],"study_design_candidate":"observational","study_design_consensus":"observational","genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9991249,0.0004909058,0.00006964672,0.00002807942,0.000004097977,0.000005208014,0.0000913679,0.000001592354,0.0001842385],"genre_scores_gemma":[0.9997217,0.00006653061,0.00002248607,0.00001297166,0.000006631331,0.0000052801,0.00009866544,5.081366e-7,0.00006505448],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.001314726,"threshold_uncertainty_score":0.006953061,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.004809709694601823,"score_gpt":0.2334361149937114,"score_spread":0.2286264052991096,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}