{"id":"W4416641339","doi":"10.1016/j.revmed.2025.10.421","title":"Comparaisons indirectes des traitements de pégunigalsidase alfa par rapport à d’autres thérapies pour l’indice de masse ventriculaire gauche dans la maladie de Fabry","year":2025,"lang":"fr","type":"article","venue":"La Revue de Médecine Interne","topic":"Lysosomal Storage Disorders Research","field":"Medicine","cited_by":0,"is_retracted":false,"has_abstract":false,"ca_institutions":"Chinook Regional Hospital","funders":"","keywords":"Drug compliance; Behavioral analysis; Limiting; Fabry disease","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"codex-gemma-dda1882f352a","candidate_categories":["metaepi_narrow","insufficient_payload"],"consensus_categories":[],"category_scores_codex":[0.002045697,0.0007246786,0.001114595,0.0006855462,0.0003163244,0.0002434016,0.001008727,0.0006504097,0.002277201],"category_scores_gemma":[0.001929533,0.0007598444,0.000499092,0.001083541,0.0009330769,0.0002289002,0.0004155871,0.001407651,0.0001848953],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.00177866,"about_ca_system_score_gemma":0.001765544,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.002583469,"about_ca_topic_score_gemma":0.0008152622,"domain_scores_codex":[0.9943014,0.001274394,0.0009521259,0.0008330246,0.0005139169,0.002125125],"domain_scores_gemma":[0.996365,0.001453985,0.0002824337,0.0007581289,0.000258051,0.0008824111],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"observational","study_design_gemma":"observational","study_design_scores_codex":[0.0005787828,0.003248893,0.8986588,0.003031055,0.001804532,0.01206963,0.008902721,0.0001994435,0.009887421,0.002309512,0.03091015,0.0283991],"study_design_scores_gemma":[0.006517591,0.0003317323,0.9203416,0.009369673,0.001215051,0.00257173,0.006471607,0.006325123,0.01823876,0.002306739,0.02566035,0.0006500306],"study_design_candidate":"observational","study_design_consensus":"observational","genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9323908,0.02538736,0.01197731,0.009342914,0.0002955994,0.0008701299,0.0001533657,0.0001982299,0.01938429],"genre_scores_gemma":[0.9465412,0.002485429,0.002960129,0.0005578462,0.0004973339,0.0002766421,0.0001095037,0.0001304304,0.04644146],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.02774907,"threshold_uncertainty_score":0.9994853,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.01932197965911205,"score_gpt":0.3059982650655945,"score_spread":0.2866762854064825,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}