{"id":"W6908615245","doi":"10.3389/fneur.2023.1284444/full","title":"Long-term safety, tolerability, and efficacy of efgartigimod (ADAPT+): interim results from a phase 3 open-label extension study in participants with generalized myasthenia gravis","year":2024,"lang":"en","type":"article","venue":"Leiden Repository (Leiden University)","topic":"Myasthenia Gravis and Thymoma","field":"Medicine","cited_by":0,"is_retracted":false,"has_abstract":true,"ca_institutions":"University Health Network","funders":"Argenx","keywords":"Myasthenia gravis; Adverse effect; Incidence (geometry); Interim; Clinical endpoint; Interim analysis; Neuromuscular disease","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.003718111,0.001196393,0.001129417,0.0002298209,0.000405219,0.0005948262,0.0005314917,0.0007811249,0.002745232],"category_scores_gemma":[0.0009652186,0.0002928899,0.001155718,0.0001910832,0.0005792544,0.0006918524,0.0004546257,0.001438261,0.0005879233],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.0002999253,"about_ca_system_score_gemma":0.0007452604,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.0004194036,"about_ca_topic_score_gemma":0.001151535,"domain_scores_codex":[0.9994381,0.0002729929,0.00004412299,0.00006824056,0.00008744513,0.00008907421],"domain_scores_gemma":[0.9988287,0.0001673865,0.000371551,0.0001377402,0.0001382116,0.0003563928],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"randomized_trial","study_design_gemma":"nonrandomized_trial","study_design_scores_codex":[0.6137744,0.06026722,0.0416775,0.001290224,0.003375937,0.0005753431,0.0004899781,0.001505457,0.1067393,0.0001654585,0.007424424,0.1627148],"study_design_scores_gemma":[0.1970107,0.6758512,0.11311,0.00005496024,0.001210933,0.0006167241,0.0001325189,0.0005563045,0.007854464,0.0001636542,0.003384296,0.00005421099],"study_design_candidate":"nonrandomized_trial","study_design_consensus":null,"genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.9960238,0.0005652618,0.0003561962,0.0001338595,0.00004014739,0.001017746,0.001033791,0.00006895359,0.0007602226],"genre_scores_gemma":[0.9897717,0.0005745157,0.002086289,0.0007866392,0.0001858034,0.002005697,0.002962636,0.00002511217,0.001601539],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.003718111,"threshold_uncertainty_score":0.01966345,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.06080074947281706,"score_gpt":0.3296286303355453,"score_spread":0.2688278808627283,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}