{"id":"W6999855564","doi":"","title":"Développement d'une approche de thérapie génique pour l'ataxie de Friedreich par la délétion de l'expansion GAA dans le gène de la frataxine","year":2023,"lang":"fr","type":"other","venue":"","topic":"Food composition and properties","field":"Nursing","cited_by":0,"is_retracted":false,"has_abstract":true,"ca_institutions":"Dow Chemical (Canada)","funders":"Fonds de Recherche du Québec - Santé; Canadian Institutes of Health Research; Ataxia Canada","keywords":"Transplantation; Transcription (linguistics); Genetic inheritance","routes":{"ca_aff":true,"ca_fund":true,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.0007532222,0.0007044328,0.0009257477,0.0006302468,0.0003746774,0.00132173,0.001035784,0.001549988,0.003690846],"category_scores_gemma":[0.0004267887,0.0004067312,0.001206509,0.0002980346,0.0005142816,0.0006145997,0.0004411766,0.002017278,0.001395335],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.0006774499,"about_ca_system_score_gemma":0.000785722,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.001644093,"about_ca_topic_score_gemma":0.0022935,"domain_scores_codex":[0.9993817,0.00009077075,0.0000328543,0.0001700329,0.0002516704,0.00007296112],"domain_scores_gemma":[0.9998229,0.00003844402,0.00003541849,0.00002733397,0.00005166514,0.00002432054],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"bench_or_experimental","study_design_gemma":"bench_or_experimental","study_design_scores_codex":[0.0006250491,0.0007431991,0.0006156001,0.001276119,0.0002090004,0.0003958684,0.0001591507,0.001671263,0.835168,0.001939713,0.0024798,0.1547173],"study_design_scores_gemma":[0.0008965185,0.008482847,0.003520473,0.0003369844,0.000888581,0.002882397,0.0001191952,0.006012237,0.7834148,0.001350295,0.1919887,0.0001068741],"study_design_candidate":"bench_or_experimental","study_design_consensus":"bench_or_experimental","genre_codex":"empirical","genre_gemma":"empirical","genre_scores_codex":[0.4826556,0.1455992,0.3147226,0.006996393,0.002666199,0.002460054,0.002288475,0.004815673,0.0377958],"genre_scores_gemma":[0.7373827,0.06637693,0.1494619,0.003705224,0.000391406,0.001596458,0.002736511,0.000425346,0.03792348],"genre_candidate":"empirical","genre_consensus":"empirical","teacher_disagreement_score":0.003690846,"threshold_uncertainty_score":0.0123471,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.01600749926802009,"score_gpt":0.2688190219639249,"score_spread":0.2528115226959048,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}