{"id":"W7117325868","doi":"10.1177/22143602251399244","title":"A toolkit for new facioscapulohumeral muscular dystrophy trial sites","year":2025,"lang":"en","type":"article","venue":"Journal of Neuromuscular Diseases","topic":"Muscle Physiology and Disorders","field":"Biochemistry, Genetics and Molecular Biology","cited_by":1,"is_retracted":false,"has_abstract":true,"ca_institutions":"Children's Hospital of Eastern Ontario; Hotchkiss Brain Institute; University of Calgary","funders":"","keywords":"Facioscapulohumeral muscular dystrophy; Clinical trial; Reimbursement; Muscular dystrophy; Disease; Drug development; Drug trial; MEDLINE","routes":{"ca_aff":true,"ca_fund":false,"ca_venue":false,"about_ca":false,"invisible_to_affiliation_only":false},"retraction":null,"screen":null,"direct_labels":[],"prediction":{"model_version":"metacan-v3-hybrid-931329e0061c","candidate_categories":[],"consensus_categories":[],"category_scores_codex":[0.1144312,0.001151021,0.001562501,0.004595325,0.002920109,0.0111417,0.006102448,0.00492746,0.141097],"category_scores_gemma":[0.09158029,0.001749229,0.002629463,0.003796408,0.002471301,0.01001718,0.01944669,0.008673484,0.074067],"about_ca_system_candidate":false,"about_ca_system_consensus":false,"about_ca_system_score_codex":0.003096659,"about_ca_system_score_gemma":0.04193398,"about_ca_topic_candidate":false,"about_ca_topic_consensus":false,"about_ca_topic_score_codex":0.00200392,"about_ca_topic_score_gemma":0.005196048,"domain_scores_codex":[0.9382862,0.04289196,0.005742962,0.002620618,0.007825742,0.002632486],"domain_scores_gemma":[0.8165023,0.04480385,0.0137484,0.02338558,0.02528732,0.07627244],"domain_codex":null,"domain_gemma":null,"domain_candidate":null,"domain_consensus":null,"study_design_codex":"not_applicable","study_design_gemma":"not_applicable","study_design_scores_codex":[0.001803681,0.000941864,0.003177699,0.002275162,0.0001621665,0.001235841,0.001602804,0.001262192,0.002094852,0.02003905,0.6353332,0.3300714],"study_design_scores_gemma":[0.001544381,0.0005173257,0.002074215,0.001522302,0.00007924774,0.0006376455,0.0006723225,0.0008467527,0.0005223138,0.01870698,0.9727452,0.0001313652],"study_design_candidate":"not_applicable","study_design_consensus":"not_applicable","genre_codex":"commentary","genre_gemma":"methods","genre_scores_codex":[0.01383463,0.02590281,0.2591368,0.2990183,0.01796347,0.04252338,0.01709656,0.05225022,0.2722738],"genre_scores_gemma":[0.04160826,0.0135023,0.6882168,0.04921351,0.005527583,0.05214952,0.01364016,0.009145213,0.1269967],"genre_candidate":"methods","genre_consensus":null,"teacher_disagreement_score":0.141097,"threshold_uncertainty_score":0.6051772,"prediction_status":"machine_predicted_unvalidated"},"machine_scores":{"provisional":true,"baseline":true,"maturity_gate_passed":false,"score_opus":0.01056508436837165,"score_gpt":0.2780919602734229,"score_spread":0.2675268759050513,"validation_status":"score_only:v0-immature-baseline","note":"Baseline scores from an immature model (maturity gate not passed). Scores rank; they never assert a category."}}