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Enregistrement W3008735477 · doi:10.1001/jamaoncol.2019.6716

Global Retinoblastoma Presentation and Analysis by National Income Level

2020· article· en· W3008735477 sur OpenAlex

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affAu moins un auteur déclare une institution canadienne dans l'instantané OpenAlex épinglé.
fundUn bailleur canadien est enregistré sur le travail.

Notice bibliographique

RevueJAMA Oncology · 2020
Typearticle
Langueen
DomaineMedicine
ThématiqueOcular Oncology and Treatments
Établissements canadiensBC Children's HospitalUniversity of British ColumbiaUniversité de MontréalCentre Hospitalier Universitaire Sainte-JustineHospital for Sick Children
Organismes subventionnairesCliniques Universitaires Saint-LucEmory Eye CenterNIH Clinical CenterNational Cancer InstituteFaculty of Medicine and Health, University of SydneySchool of Medicine, Shanghai Jiao Tong UniversityCollege of Medicine, University of CincinnatiUniversité de ParisServicio Andaluz de SaludUniversitas AndalasCentre hospitalier universitaire Sainte-JustineMasarykova UniverzitaDali UniversityUniversitas AirlanggaUniversity of Cape TownHospital for Sick ChildrenAddis Ababa UniversityAnna UniversityUniversité Mohammed V de RabatAarhus UniversitetUniversity of GhanaPrince of Songkla UniversityJimma UniversityHospital Infantil de México Federico GómezUniversità degli Studi di PadovaUniversitas UdayanaShanghai Jiao Tong UniversityHacettepe ÜniversitesiTel Aviv UniversitySeoul National University HospitalFaculdade de Medicina da Universidade de São PauloMahidol UniversityHebrew University of JerusalemUniversitätsklinikum Hamburg-EppendorfUniversiteit StellenboschUniversidade de São PauloChulalongkorn UniversityCentre Hospitalier Universitaire VaudoisNorthwestern UniversitySeoul National UniversityHelsingin YliopistoSemmelweis EgyetemUniversity of CincinnatiAmsterdam University Medical CentersUniversitätsklinikum EssenBirmingham Women's and Children's NHS Foundation TrustLeonard M. Miller School of MedicineIndus HospitalUniversity of Southern CaliforniaChildren's Hospital ColoradoCleveland ClinicHadassah Medical OrganizationGuangxi Medical UniversityIran University of Medical SciencesTehran University of Medical Sciences and Health ServicesUniversidade de CoimbraUniversity of MiamiUniversity of South CarolinaUniversity of LouisvilleJohns Hopkins UniversityFeinberg School of MedicineAnkara UniversitesiEge ÜniversitesiUniversità degli Studi di SienaChang Gung Medical FoundationChildren's Hospital Los AngelesSt. Jude Children's Research HospitalAarhus UniversitetshospitalUniversidad de ChileEmory UniversityInyuvesi Yakwazulu-NataliUniversity of OtagoConsejo Nacional de Investigaciones Científicas y TécnicasUniwersytet Jagielloński Collegium Medicum
Mots-clésMedicineRetinoblastomaInterquartile rangePediatricsCohortStrabismusReferralSurgeryInternal medicineFamily medicine

Résumé

récupéré en direct d'OpenAlex

Importance: Early diagnosis of retinoblastoma, the most common intraocular cancer, can save both a child's life and vision. However, anecdotal evidence suggests that many children across the world are diagnosed late. To our knowledge, the clinical presentation of retinoblastoma has never been assessed on a global scale. Objectives: To report the retinoblastoma stage at diagnosis in patients across the world during a single year, to investigate associations between clinical variables and national income level, and to investigate risk factors for advanced disease at diagnosis. Design, Setting, and Participants: A total of 278 retinoblastoma treatment centers were recruited from June 2017 through December 2018 to participate in a cross-sectional analysis of treatment-naive patients with retinoblastoma who were diagnosed in 2017. Main Outcomes and Measures: Age at presentation, proportion of familial history of retinoblastoma, and tumor stage and metastasis. Results: The cohort included 4351 new patients from 153 countries; the median age at diagnosis was 30.5 (interquartile range, 18.3-45.9) months, and 1976 patients (45.4%) were female. Most patients (n = 3685 [84.7%]) were from low- and middle-income countries (LMICs). Globally, the most common indication for referral was leukocoria (n = 2638 [62.8%]), followed by strabismus (n = 429 [10.2%]) and proptosis (n = 309 [7.4%]). Patients from high-income countries (HICs) were diagnosed at a median age of 14.1 months, with 656 of 666 (98.5%) patients having intraocular retinoblastoma and 2 (0.3%) having metastasis. Patients from low-income countries were diagnosed at a median age of 30.5 months, with 256 of 521 (49.1%) having extraocular retinoblastoma and 94 of 498 (18.9%) having metastasis. Lower national income level was associated with older presentation age, higher proportion of locally advanced disease and distant metastasis, and smaller proportion of familial history of retinoblastoma. Advanced disease at diagnosis was more common in LMICs even after adjusting for age (odds ratio for low-income countries vs upper-middle-income countries and HICs, 17.92 [95% CI, 12.94-24.80], and for lower-middle-income countries vs upper-middle-income countries and HICs, 5.74 [95% CI, 4.30-7.68]). Conclusions and Relevance: This study is estimated to have included more than half of all new retinoblastoma cases worldwide in 2017. Children from LMICs, where the main global retinoblastoma burden lies, presented at an older age with more advanced disease and demonstrated a smaller proportion of familial history of retinoblastoma, likely because many do not reach a childbearing age. Given that retinoblastoma is curable, these data are concerning and mandate intervention at national and international levels. Further studies are needed to investigate factors, other than age at presentation, that may be associated with advanced disease in LMICs.

Récupéré en direct depuis OpenAlex et désinversé. Les résumés ne sont pas conservés dans cette base de données : les index inversés représentent 8,6 Go des 9,3 Go de texte de la base, et le serveur dispose de 13 Go libres.

Prédiction distillée sur la base complète

Imitation des enseignants

Ni prévalence calibrée, ni vérité terrain. Validation humaine à venir. Apprise à partir de 10 348 étiquettes directes de Codex et de 10 348 étiquettes directes de Gemma. Le mode candidate est l'union des têtes enseignantes seuillées; le consensus est leur intersection. Ces sorties portent le statut machine_predicted_unvalidated et ne sont ni des étiquettes humaines ni des étiquettes directes de modèles de pointe.

score de la tête « metaresearch » (Codex)0,000
score de la tête « metaresearch » (Gemma)0,000
Version: codex-gemma-dda1882f352aStatut de validation: machine_predicted_unvalidated
Catégories candidatesaucune
Catégories consensuellesaucune
DomaineSignal candidat: aucune · Signal consensuel: aucune
Devis d'étudeSignal candidat: Observationnel · Signal consensuel: Observationnel
GenreSignal candidat: Empirique · Signal consensuel: Empirique
Score de désaccord entre enseignants0,043
Score d'incertitude au seuil0,320

Scores Codex et Gemma par catégorie

CatégorieCodexGemma
Métarecherche0,0000,000
Méta-épidémiologie (sens strict)0,0000,000
Méta-épidémiologie (sens large)0,0000,000
Bibliométrie0,0000,000
Études des sciences et des technologies0,0000,000
Communication savante0,0000,000
Science ouverte0,0000,000
Intégrité de la recherche0,0000,000
Charge utile insuffisante (le modèle a refusé de juger)0,0000,000

Scores machine (provisoires)

Les deux têtes enseignantes du modèle étudiant, lues sur ce travail. Un score ordonne la base pour la relecture; il n'affirme jamais une catégorie, et le statut de validation accompagne chaque rangée tel quel.

Scores de référence d'un modèle non mature (critères de maturité non atteints, 7 itérations). Un score ordonne; il n'affirme jamais une catégorie.

Tête enseignante Opus0,034
Tête enseignante GPT0,355
Écart entre enseignants0,321 · la distance entre les deux têtes enseignantes sur ce seul travail
Statut de validationscore_only:v0-immature-baseline · tel quel depuis la passe de notation : score_only signifie que le nombre peut ordonner les travaux, et qu'aucune étiquette de catégorie n'en découle