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Enregistrement W4281716488 · doi:10.1001/jamaneurol.2022.1166

Association of Rare <i>APOE</i> Missense Variants V236E and R251G With Risk of Alzheimer Disease

2022· article· en· W4281716488 sur OpenAlex

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Notice bibliographique

RevueJAMA Neurology · 2022
Typearticle
Langueen
DomaineMedicine
ThématiqueAlzheimer's disease research and treatments
Établissements canadiensOntario Brain InstituteUniversity of TorontoUniversity Health Network
Organismes subventionnairesInstituto de Salud Carlos IIIEconomic and Social Research CouncilNational Institutes of HealthUniversité de ParisAmsterdam NeuroscienceRégion NormandieBerlin Institute of HealthNormandie UniversitéNational Institute on AgingUniversità degli Studi di CamerinoUniversität Duisburg-EssenRheinische Friedrich-Wilhelms-Universität BonnUniversität zu KölnFreie Universität BerlinMedical Research CouncilCentre Hospitalier Universitaire de BordeauxUniversità degli Studi di BresciaUppsala UniversitetDeutsches Zentrum für Neurodegenerative ErkrankungenUniversität ZürichCentre Hospitalier Universitaire VaudoisUniversitat de BarcelonaUniversità Cattolica del Sacro CuoreTechnische Universität MünchenUniversita degli Studi di Bari Aldo MoroUniversidade de LisboaInstituto de Investigación Sanitaria del Principado de AsturiasUniversidad Autónoma de MadridUniversitätsspital ZürichMedizinische Universität WienNational and Kapodistrian University of AthensKarolinska InstitutetUniversity of TorontoUniversidad de CantabriaUniversität WienUniversität HeidelbergUniversità degli Studi di Milano-BicoccaAssistance publique-Hôpitaux de ParisAgence Nationale de la RechercheUniversità degli Studi di PerugiaUniversiteit MaastrichtUniversity of OxfordVrije Universiteit AmsterdamUniversité Paris-SaclayUniversity of BristolUniversité de BordeauxLundbeckfondenItä-Suomen YliopistoCardiff UniversityUniversitat Autònoma de BarcelonaEidgenössische Technische Hochschule ZürichUniversité de LilleCentro de Investigación Biomédica en Red sobre Enfermedades NeurodegenerativasUniversitetet i OsloDevelopment of Innovative Strategies for a Transdisciplinary approach to ALZheimer's diseaseMedical University SofiaInstituto de Investigación Marqués de ValdecillaFondazione I.R.C.C.S. Istituto Neurologico Carlo BestaUniversità degli Studi di MilanoEU Joint Programme – Neurodegenerative Disease ResearchUniversità degli Studi di FirenzeHumboldt-Universität zu BerlinInstitut National de la Santé et de la Recherche MédicaleNeuroscience Center Zurich, University of ZurichAristotle University of ThessalonikiUniverzita Karlova v PrazeUniversità degli Studi di CagliariCentro de Biología Molecular Severo OchoaUniversidad de MálagaAmsterdam University Medical CentersUniversità degli Studi di ParmaUniversity of Texas Health Science Center at San AntonioUniversidad de SevillaUniversidade de AveiroStockholms UniversitetAlzheimer's Association
Mots-clésMissense mutationDiseaseApolipoprotein EAlzheimer's diseaseAssociation (psychology)MedicineGeneticsInternal medicineBiologyPsychologyMutationGene

Résumé

récupéré en direct d'OpenAlex

Importance: The APOE ε2 and APOE ε4 alleles are the strongest protective and risk-increasing, respectively, genetic variants for late-onset Alzheimer disease (AD). However, the mechanisms linking APOE to AD-particularly the apoE protein's role in AD pathogenesis and how this is affected by APOE variants-remain poorly understood. Identifying missense variants in addition to APOE ε2 and APOE ε4 could provide critical new insights, but given the low frequency of additional missense variants, AD genetic cohorts have previously been too small to interrogate this question robustly. Objective: To determine whether rare missense variants on APOE are associated with AD risk. Design, Setting, and Participants: Association with case-control status was tested in a sequenced discovery sample (stage 1) and followed up in several microarray imputed cohorts as well as the UK Biobank whole-exome sequencing resource using a proxy-AD phenotype (stages 2 and 3). This study combined case-control, family-based, population-based, and longitudinal AD-related cohorts that recruited referred and volunteer participants. Stage 1 included 37 409 nonunique participants of European or admixed European ancestry, with 11 868 individuals with AD and 11 934 controls passing analysis inclusion criteria. In stages 2 and 3, 475 473 participants were considered across 8 cohorts, of which 84 513 individuals with AD and proxy-AD and 328 372 controls passed inclusion criteria. Selection criteria were cohort specific, and this study was performed a posteriori on individuals who were genotyped. Among the available genotypes, 76 195 were excluded. All data were retrieved between September 2015 and November 2021 and analyzed between April and November 2021. Main Outcomes and Measures: In primary analyses, the AD risk associated with each missense variant was estimated, as appropriate, with either linear mixed-model regression or logistic regression. In secondary analyses, associations were estimated with age at onset using linear mixed-model regression and risk of conversion to AD using competing-risk regression. Results: A total of 544 384 participants were analyzed in the primary case-control analysis; 312 476 (57.4%) were female, and the mean (SD; range) age was 64.9 (15.2; 40-110) years. Two missense variants were associated with a 2-fold to 3-fold decreased AD risk: APOE ε4 (R251G) (odds ratio, 0.44; 95% CI, 0.33-0.59; P = 4.7 × 10-8) and APOE ε3 (V236E) (odds ratio, 0.37; 95% CI, 0.25-0.56; P = 1.9 × 10-6). Additionally, the cumulative incidence of AD in carriers of these variants was found to grow more slowly with age compared with noncarriers. Conclusions and Relevance: In this genetic association study, a novel variant associated with AD was identified: R251G always coinherited with ε4 on the APOE gene, which mitigates the ε4-associated AD risk. The protective effect of the V236E variant, which is always coinherited with ε3 on the APOE gene, was also confirmed. The location of these variants confirms that the carboxyl-terminal portion of apoE plays an important role in AD pathogenesis. The large risk reductions reported here suggest that protein chemistry and functional assays of these variants should be pursued, as they have the potential to guide drug development targeting APOE.

Récupéré en direct depuis OpenAlex et désinversé. Les résumés ne sont pas conservés dans cette base de données : les index inversés représentent 8,6 Go des 9,3 Go de texte de la base, et le serveur dispose de 13 Go libres.

Prédiction distillée sur la base complète

Imitation des enseignants

Ni prévalence calibrée, ni vérité terrain. Validation humaine à venir. Apprise à partir de 10 348 étiquettes directes de Codex et de 10 348 étiquettes directes de Gemma. Le mode candidate est l'union des têtes enseignantes seuillées; le consensus est leur intersection. Ces sorties portent le statut machine_predicted_unvalidated et ne sont ni des étiquettes humaines ni des étiquettes directes de modèles de pointe.

score de la tête « metaresearch » (Codex)0,000
score de la tête « metaresearch » (Gemma)0,000
Version: codex-gemma-dda1882f352aStatut de validation: machine_predicted_unvalidated
Catégories candidatesaucune
Catégories consensuellesaucune
DomaineSignal candidat: aucune · Signal consensuel: aucune
Devis d'étudeSignal candidat: Observationnel · Signal consensuel: Observationnel
GenreSignal candidat: Empirique · Signal consensuel: Empirique
Score de désaccord entre enseignants0,008
Score d'incertitude au seuil0,382

Scores Codex et Gemma par catégorie

CatégorieCodexGemma
Métarecherche0,0000,000
Méta-épidémiologie (sens strict)0,0000,000
Méta-épidémiologie (sens large)0,0000,000
Bibliométrie0,0000,000
Études des sciences et des technologies0,0000,000
Communication savante0,0000,000
Science ouverte0,0000,000
Intégrité de la recherche0,0000,000
Charge utile insuffisante (le modèle a refusé de juger)0,0000,000

Scores machine (provisoires)

Les deux têtes enseignantes du modèle étudiant, lues sur ce travail. Un score ordonne la base pour la relecture; il n'affirme jamais une catégorie, et le statut de validation accompagne chaque rangée tel quel.

Scores de référence d'un modèle non mature (critères de maturité non atteints, 7 itérations). Un score ordonne; il n'affirme jamais une catégorie.

Tête enseignante Opus0,013
Tête enseignante GPT0,261
Écart entre enseignants0,248 · la distance entre les deux têtes enseignantes sur ce seul travail
Statut de validationscore_only:v0-immature-baseline · tel quel depuis la passe de notation : score_only signifie que le nombre peut ordonner les travaux, et qu'aucune étiquette de catégorie n'en découle