MétaCan
Menu
← Retour à la cohorte
Enregistrement W4316081537 · doi:10.14309/01.ajg.0000859944.44760.c4

S826 Baseline and Early Predictors of Response to Risankizumab Induction and Maintenance Treatment in Patients With Moderate to Severe Crohn's Disease

2022· article· en· W4316081537 sur OpenAlexaff
Jean‐Frédéric Colombel, Walter Reinisch, Stefan Schreiber, Silvio Danese, Ken Sugimoto, María T. Abreu, Naomi Martin, Kristina Kligys, Valerie Pivorunas, Alexandra Song, Javier Zambrano, Yafei Zhang, Remo Panaccione

Notice bibliographique

RevueThe American Journal of Gastroenterology · 2022
Typearticle
Langueen
DomaineBiochemistry, Genetics and Molecular Biology
ThématiqueInflammatory Bowel Disease
Établissements canadiensUniversity of Calgary
Organismes subventionnairesnon disponible
Mots-clésMedicineCrohn's diseaseInternal medicineCrohn diseaseDiseaseBaseline (sea)Gastroenterology

Résumé

récupéré en direct d'OpenAlex

Introduction: Pivotal phase 3 induction (ADVANCE and MOTIVATE) and maintenance (FORTIFY) studies established that treatment with risankizumab (RZB), a humanized monoclonal antibody with high specificity for the p19 subunit of interleukin-23, was superior to placebo for achieving clinical remission and endoscopic response in patients with moderate to severe Crohn's disease (CD). This exploratory analysis aimed to determine predictors of response to risankizumab induction and maintenance therapy. Methods: Pooled data from patients in the RZB 600 mg intravenous (IV) dosing groups in ADVANCE + MOTIVATE induction studies (n=527) and data from the RZB 360 mg subcutaneous (SC) dosing group in FORTIFY (n=141) were evaluated. Multivariate logistic regression models were used to determine predictors of clinical and endoscopic outcomes at Weeks 12 and 52. For FORTIFY, separate logistic regression models were used to access end-of-induction characteristics for the achievement of outcomes at Week 52. Results: Baseline characteristics found to be predictive of clinical and/or endoscopic outcomes at Week 12 and Week 52 are highlighted in the Table. Age and duration of disease were evaluated but were not predictive. Compared to patients with ileal disease, patients with colonic disease were more likely to achieve endoscopic endpoints at Week 12, while patients with ileal-colonic disease were more likely to achieve endoscopic response at Week 12; patients with either colonic or ileal-colonic disease were more likely to achieve endoscopic response at Week 52. Conversely, patients with prior bio-failure at BL were less likely to achieve endoscopic response at Week 12, and clinical and endoscopic responses at Week 52. Patients using corticosteroids at BL were less likely to achieve clinical endpoints at Weeks 12 and 52. Patients achieving clinical or endoscopic endpoints at Week 12 were more likely to achieve these endpoints at Week 52. Conclusion: For patients treated with risankizumab, baseline disease location predicted achievement of endoscopic responses, corticosteroid use predicted achievement of clinical endpoints, and prior bio-failure status predicted achievement of both clinical and endoscopic endpoints at Week 52. Notably, achievement of clinical or endoscopic outcomes after induction with risankizumab were associated with a higher likelihood of achieving long-term clinical and endoscopic outcomes. Table 1. - Induction Baseline Characteristics and FORTIFY Week 0 Clinical Outcomes as Predictors of Week 12 Response to Risankizumab Induction and Week 52 Response to Risankizumab Maintenance Dosing Week 12 SF/APS Clinical Remission RZB 600 mg IV Week 12 CDAI Clinical Remission RZB 600 mg IV Week 12 CDAI Clinical Response RZB 600 mg IV Week 12Endoscopic Response RZB 600 mg IV Week 12Endoscopic Remission RZB 600 mg IV Week 12Ulcer-free Endoscopy RZB 600 mg IV Week 52 SF/APS Clinical Remission RZB 360 mg SC Week 52 CDAI Clinical Remission RZB 360 mg SC Week 52 CDAI Clinical Response RZB 360 mg SC Week 52Endoscopic Response RZB 360 mg SC Week 52Endoscopic Remission RZB 360 mg SC Week 52Ulcer-free Endoscopy RZB 360 mg SC Induction Baseline Characteristics as Predictors of ResponseOdds Ratio [95% CI]P-value Colonic Disease Only 1.436 [0.766, 2.693]P=0.260 1.653 [0.883, 3.094]P=0.116 1.448 [0.774, 2.709]P=0.247 5.178 [2.411, 11.123] P< 0.001 3.077 [1.425, 6.644] P=0.004 3.393 [1.510, 7.624] P=0.003 0.654 [0.265, 1.614]P=0.357 0.886 [0.357, 2.203]P=0.795 0.938 [0.378, 2.328]P=0.890 4.909 [1.468, 16.410] P=0.010 2.135 [0.722, 6.317]P=0.170 2.428 [0.731, 8.060]P=0.147 Ileal-colonic Disease Only 0.751 [0.411, 1.370] P=0.350 0.821 [0.451, 1.492] P=0.517 0.906 [0.506, 1.622] P=0.739 2.880 [1.379, 6.017] P=0.005 1.262 [0.590, 2.702] P=0.548 0.767 [0.331, 1.775] P=0.535 0.634 [0.263, 1.529] P=0.311 1.032 [0.426, 2.503] P=0.944 0.806 [0.333, 1.952] P=0.632 4.351 [1.318, 14.366] P=0.016 1.826 [0.627, 5.321] P=0.270 2.018 [0.617, 6.602] P=0.246 Bio-Failure Status 0.675 [0.423, 1.076] P=0.098 0.789 [0.495, 1.258] P=0.320 0.867 [0.540, 1.393] P=0.556 0.438 [0.271, 0.709] P< 0.001 0.597 [0.352, 1.013] P=0.056 0.570 [0.317, 1.026] P=0.061 0.425 [0.229, 0.787] P=0.006 0.373 [0.200, 0.698] P=0.002 0.426 [0.225, 0.805] P=0.009 0.443 [0.233, 0.844] P=0.013 0.444 [0.228, 0.863] P=0.017 0.295 [0.144, 0.606] P< 0.001 Corticosteroid Use 0.506 [0.321, 0.799] P=0.003 0.491 [0.313, 0.769] P=0.002 0.440 [0.283, 0.683] P< 0.001 0.742 [0.466, 1.181] P=0.208 0.786 [0.463, 1.334] P=0.372 0.891 [0.493, 1.609] P=0.701 0.443 [0.243, 0.805] P=0.008 0.331 [0.178, 0.613] P< 0.001 0.374 [0.210, 0.668] P< 0.001 0.796 [0.430, 1.474] P=0.468 0.787 [0.403, 1.539] P=0.485 0.939 [0.450, 1.959] P=0.866 Induction Week 12 Clinical Outcomes as Predictors of Response at Maintenance Week 52Odds Ratio [95% CI]P-value SF/APS Clinical Response 1.538 [0.969, 2.442] P=0.068 1.418 [0.894, 2.249] P=0.137 1.596 [1.005, 2.535] P=0.048 2.880 [1.737, 4.774] P< 0.001 4.417 [2.466, 7.909] P< 0.001 3.517 [1.884, 6.565] P< 0.001 SF/APS Clinical Remission 2.084 [1.095, 3.967] P=0.025 1.429 [0.760, 2.684] P=0.268 1.704 [0.889, 3.267] P=0.109 3.696 [1.904, 7.172] P< 0.001 5.368 [2.542, 11.337] P< 0.001 5.091 [2.264, 11.448] P< 0.001 Endoscopic Response 1.066 [0.527, 2.156] P=0.860 0.886 [0.438, 1.793] P=0.736 1.279 [0.613, 2.666] P=0.512 3.592 [1.712, 7.540] P< 0.001 5.765 [2.663, 12.479] P< 0.001 6.314 [2.824, 14.120] P< 0.001 Endoscopic Remission 1.186 [0.503, 2.796] P=0.696 0.810 [0.344, 1.907] P=0.629 1.067 [0.433, 2.625] P=0.888 4.342 [1.732, 10.887] P=0.002 9.227 [3.436, 24.776] P< 0.001 8.036 [2.934, 22.006] P< 0.001

Récupéré en direct depuis OpenAlex et désinversé. Les résumés ne sont pas conservés dans cette base de données : les index inversés représentent 8,6 Go des 9,3 Go de texte de la base, et le serveur dispose de 13 Go libres.

Comment cette classification a été obtenuedéplier

Prédiction machine sur la base complète

Imitation des enseignants

Ni prévalence calibrée, ni vérité terrain. Validation humaine à venir. Le volet Gemma est une étiquette directe du modèle pour chaque travail de la base, lue sur la notice réduite au titre. Le volet Codex est un classifieur appris des 10 348 étiquettes directes de Codex et calibré sur les taux pondérés de l'échantillon; les champs sans appui suffisant ne portent aucun appel Codex. Le mode candidate est l'union des deux volets; le consensus est leur intersection. Ces sorties portent le statut machine_predicted_unvalidated et ne sont pas des étiquettes humaines.

score de la tête « metaresearch » (Codex)0,002
score de la tête « metaresearch » (Gemma)0,003
Version: metacan-v3-hybrid-931329e0061cStatut de validation: machine_predicted_unvalidated
Catégories candidatesaucune
Catégories consensuellesaucune
DomaineSignal candidat: aucune · Signal consensuel: aucune
Devis d'étudeSignal candidat: Observationnel · Signal consensuel: Observationnel
GenreSignal candidat: Empirique · Signal consensuel: Empirique
Score de désaccord entre enseignants0,002
Score d'incertitude au seuil0,009

Scores du classifieur distillé par catégorie (deux têtes)

CatégorieCodexGemma
Métarecherche0,0020,003
Méta-épidémiologie (sens strict)0,0000,000
Méta-épidémiologie (sens large)0,0010,001
Bibliométrie0,0000,001
Études des sciences et des technologies0,0000,000
Communication savante0,0000,000
Science ouverte0,0000,000
Intégrité de la recherche0,0000,000
Charge utile insuffisante (le modèle a refusé de juger)0,0020,000

Scores machine (provisoires)

Les deux têtes enseignantes du modèle étudiant, lues sur ce travail. Un score ordonne la base pour la relecture; il n'affirme jamais une catégorie, et le statut de validation accompagne chaque rangée tel quel.

Scores de référence d'un modèle non mature (critères de maturité non atteints, 7 itérations). Un score ordonne; il n'affirme jamais une catégorie.

Tête enseignante Opus0,003
Tête enseignante GPT0,198
Écart entre enseignants0,195 · la distance entre les deux têtes enseignantes sur ce seul travail
Statut de validationscore_only:v0-immature-baseline · tel quel depuis la passe de notation : score_only signifie que le nombre peut ordonner les travaux, et qu'aucune étiquette de catégorie n'en découle

Classification

machine, non validée

Prédiction automatique; un appel candidat d’une seule source (Gemma direct ou Codex distillé), pas un consensus.

Les modèles n’ont appliqué aucune catégorie : rien dans la taxonomie ne correspondait à ce travail.
Devis d'étudeObservationnel
Domainenon disponible
GenreEmpirique

Le détail, modèle par modèle et score par score, se trouve en fin de page sous « Comment cette classification a été obtenue ».

En bref

Citations0
Publié2022
Routes d'admission1
Résumé présentoui

Explorer davantage

Même revueThe American Journal of Gastroenterology→Même sujetInflammatory Bowel Disease→Travaux en français237 207→