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Enregistrement W4386143084 · doi:10.1097/01.hs9.0000977400.14880.93

PB2681: GAPS IN THE ASSESSMENT AND MONITORING OF CARDIOVASCULAR RISK AND PSYCHOLOGICAL BURDEN IN POLYCYTHEMIA VERA: LANDMARK 2.0: A WORLDWIDE HEALTH SURVEY

2023· article· en· W4386143084 sur OpenAlexaff
Claire Harrison, David M. Ross, Laura Fogliatto, Lynda Foltz, Lambert Busque, Zhijian Xiao, Florian H. Heidel, Michael Koehler, Giuseppe A. Palumbo, Massimo Breccia, Norio Komatsu, Keita Kirito, Blanca Xicoy Cirici, Joaquín Martínez‐López, Alicia Rovó, Cheryl Petruk, Catalin Bobirca, Laura Mirams, Abigail McMillan, Gavin Harper, Jean‐Jacques Kiladjian

Notice bibliographique

RevueHemaSphere · 2023
Typearticle
Langueen
DomaineMedicine
ThématiqueMyeloproliferative Neoplasms: Diagnosis and Treatment
Établissements canadiensHôpital Maisonneuve-RosemontUniversity of British Columbia
Organismes subventionnairesnon disponible
Mots-clésMedicinePolycythemia veraPhlebotomyQuality of life (healthcare)Internal medicine

Résumé

récupéré en direct d'OpenAlex

Topic: 35. Quality of life and palliative care Background: Polycythemia vera (PV) patients (pts) have a high risk of thrombosis and cardiovascular (CV) events are the main cause of death. PV Pts also report reduced quality of life (QoL) due to high symptom and psychological burden. Aims: This study examined patterns in CV risk assessment and PV-related psychological burden, comparing results from physician (phys) and pt perspectives. Methods: The LANDMARK 2.0 survey of PV pts and phys was conducted in 11 countries between April 2021–May 2022. Pts aged 18–89 years (yrs), and phys who were managing PV pts within the preceding 12 months (mo) were included. Pts were stratified by current therapy (tx) stage: first-line cytoreductive tx for ≤1yr (PV-C), second-line tx for ≤1yr (PV-I), or any line of tx for >1yr (PV-M). Results: Overall, 133 phys and 274 PV pts (PV-C =86; PV-I =26; PV-M =162) completed the survey. In the PV-C, PV-I, and PV-M groups, median age was 63, 59, and 64 yrs and time since PV diagnosis was 43, 117, and 312 weeks, respectively. Most common PV treatments were hydroxyurea and ruxolitinib. Phlebotomies were received by 53%, 31%, and 29% pts in PV-C, PV-I, and PV-M stages respectively. Basic CV assessment (e.g., BP and chol) was routinely performed by 77%, 62% and 53% of PV-C, PV-I and PV-M treating phys, respectively. Comprehensive CV assessment (e.g., ECG and/or ECO) was performed less frequently (PV-C=60%; PV-I=47%; PV-M=32%). Among phys who never performed basic (n=21) or comprehensive (n=40) CV assessment, reasons cited include lack of necessity (38% & 43%), insufficient time (38% & 15%) and insufficient resources (19% & 35%). 68% and 63% of all phys believe that basic or comprehensive CV assessment could not be used more effectively in pt management. In contrast, 55% of all pts reported receiving routine basic CV assessment. In particular, PV-C pts reported a lower rate than phys (63% vs 77%). Fewer PV-M pts received advice on reducing CV risk (45% in the last 12mo) vs PV-C and PV-I pts (73% & 69%, respectively, in the last 6mo). Fewer PV-M pts had comprehensive CV assessment compared to PV-C and PV-I pts (42% vs 76% or 59%, respectively). On a scale from 1 (no impact) to 5 (significant impact), when asked how PV affects QoL, most pts (58%) reported an impact of 3–5 on emotional well-being and mental health, especially PV-C (66%) and PV-I (80%) pts. 38% of all pts rated the impact of phlebotomy on QoL as 3–5, 41% of whom experienced stress about managing hematocrit. However, a minority of phys reported ever having assessed the emotional burden of phlebotomy (PV-C, 33%; PV-I, 28%; PV-M, 36%). Among respondents who had ever carried out/received a psychosocial burden assessment during routine visits, fewer pts than phys reporting the assessment being performed always/often (Figure 1). Regarding PV-related psychological burden support received, 52% of pts reported being somewhat/very satisfied. More pts vs phys reported a lack of communication on self-help strategies in PV-I (36% vs 12%) or on the rationale for having performed specific tests in PV-I (20% vs 8%) and PV-C (24% vs 9%).Summary/Conclusion: Control CV risk factors in PV pts is recommended, however, there is no standard method for monitoring CV risk, highlighting an unmet need. These findings indicate that CV-risk education and testing are not typically provided throughout the tx process, particularly for pts who are stabilized on long-term maintenance therapy. Additionally, our findings show pts and phys disagree about the perceived importance of PV-related QoL assessments. Pt care may be enhanced with regular assessments throughout tx and increased communication Keywords: Polycythemia vera, Thrombosis, Myeloproliferative disorder, Quality of life

Récupéré en direct depuis OpenAlex et désinversé. Les résumés ne sont pas conservés dans cette base de données : les index inversés représentent 8,6 Go des 9,3 Go de texte de la base, et le serveur dispose de 13 Go libres.

Comment cette classification a été obtenuedéplier

Prédiction distillée sur la base complète

Imitation des enseignants

Ni prévalence calibrée, ni vérité terrain. Validation humaine à venir. Apprise à partir de 10 348 étiquettes directes de Codex et de 10 348 étiquettes directes de Gemma. Le mode candidate est l'union des têtes enseignantes seuillées; le consensus est leur intersection. Ces sorties portent le statut machine_predicted_unvalidated et ne sont ni des étiquettes humaines ni des étiquettes directes de modèles de pointe.

score de la tête « metaresearch » (Codex)0,001
score de la tête « metaresearch » (Gemma)0,000
Version: codex-gemma-dda1882f352aStatut de validation: machine_predicted_unvalidated
Catégories candidatesaucune
Catégories consensuellesaucune
DomaineSignal candidat: aucune · Signal consensuel: aucune
Devis d'étudeSignal candidat: Observationnel · Signal consensuel: Observationnel
GenreSignal candidat: Empirique · Signal consensuel: Empirique
Score de désaccord entre enseignants0,015
Score d'incertitude au seuil0,422

Scores Codex et Gemma par catégorie

CatégorieCodexGemma
Métarecherche0,0010,000
Méta-épidémiologie (sens strict)0,0000,000
Méta-épidémiologie (sens large)0,0010,000
Bibliométrie0,0000,000
Études des sciences et des technologies0,0000,000
Communication savante0,0000,000
Science ouverte0,0000,000
Intégrité de la recherche0,0000,000
Charge utile insuffisante (le modèle a refusé de juger)0,0000,000

Scores machine (provisoires)

Les deux têtes enseignantes du modèle étudiant, lues sur ce travail. Un score ordonne la base pour la relecture; il n'affirme jamais une catégorie, et le statut de validation accompagne chaque rangée tel quel.

Scores de référence d'un modèle non mature (critères de maturité non atteints, 7 itérations). Un score ordonne; il n'affirme jamais une catégorie.

Tête enseignante Opus0,055
Tête enseignante GPT0,364
Écart entre enseignants0,309 · la distance entre les deux têtes enseignantes sur ce seul travail
Statut de validationscore_only:v0-immature-baseline · tel quel depuis la passe de notation : score_only signifie que le nombre peut ordonner les travaux, et qu'aucune étiquette de catégorie n'en découle

Classification

machine, non validée

Prédiction automatique; un appel candidat d’une seule tête enseignante, pas un consensus.

Les modèles n’ont appliqué aucune catégorie : rien dans la taxonomie ne correspondait à ce travail.
Devis d'étudeObservationnel
Domainenon disponible
GenreEmpirique

Le détail, modèle par modèle et score par score, se trouve en fin de page sous « Comment cette classification a été obtenue ».

En bref

Citations0
Publié2023
Routes d'admission1
Résumé présentoui

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