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Enregistrement W4386467177 · doi:10.1007/s00431-023-05179-7

COVID-19 and MIS-C treatment in children—results from an international survey

2023· article· en· W4386467177 sur OpenAlexfundno aff
Daniele Donà, Chiara Minotti, Tiziana Masini, Martina Penazzato, Marieke M. van der Zalm, Ali Judd, Carlo Giaquinto, Marc Lallemant, Antonia H. Bouts, Eric D. McCollum, Alasdair Bamford, Pablo Rojo, Alfredo Tagarro, Nanny Nan P., Eduardo López, Sonia Bianchini, Giangiacomo Nicolini, Алла Волоха, Luca Pierantoni, Stefania Bernardi, Vania Giacomet, Tinsae Alemayehu, Kanokkron Swasdichai, Elio Castagnola, Charl Verwey, Petar Velikov, Paolo Palma, Fatima Mir, Rhian Isaac, Timo Jahnukainen, Cristina Calvo, Nicolaus Schwerk, Omotakin Omolokun, Agnese Tamborino, Marinella Della Negra, Shubhada Hooli, Gary Reubenson, A. Mazimpaka, Devika Dixit, Qalab Abbas, Taryn Gray, Marta González‐Vicent, Kate Webb, Grace Damasy, Andrew Riordan, Maria Francelina Lopes, Suparat Kanjanavanit, Steven Welch, Andrea Lo Vecchio, Silvia Garazzino, Helen Payne, Suchada Ruenglerdpong, Katja Masjosthusmann, Malte Kohns Vasconcelos, David Burgner, Davide Meneghesso, Alessandra Meneghel, Elizabeth Whittaker, J A Aluoch, Vannee Thirapattarapong, Magdalena Maria Marczyńska, Winnie August, Helena Rabie, Andreas H. Groll, Guido Castelli Gattinara, A. Madrid, M. González Hierro, Dominique Debray, S Jamal, Elisabetta Calore, Mara Cananzi, Marica De Pieri, Martín Brizuela, Chawanzi Kachikoti, George Patrick Akabwai, Selam Seged, Tom F.W. Wolfs, Christos Karatzios, Marco Tovar, A. Polynary, Edward Kabeja

Notice bibliographique

RevueEuropean Journal of Pediatrics · 2023
Typearticle
Langueen
DomaineMedicine
ThématiqueKawasaki Disease and Coronary Complications
Établissements canadiensnon disponible
Organismes subventionnairesInstitute of Infection and ImmunityUniversity of Cape TownAmsterdam University Medical CentersHelsingin YliopistoUniversità degli Studi di PadovaMedizinischen Hochschule HannoverMedical University SofiaAlder Hey Children's NHS Foundation TrustMedical Research CouncilOspedale Pediatrico Bambino GesùUniversità degli Studi di Napoli Federico IIEuropean CommissionWorld Health OrganizationTexas Children's HospitalJohns Hopkins University
Mots-clésMedicineCoronavirus disease 2019 (COVID-19)Clinical trialMedical prescriptionOff-label useFamily medicineSevere acute respiratory syndrome coronavirus 2 (SARS-CoV-2)2019-20 coronavirus outbreakPandemicMEDLINEPediatric Infectious DiseasePediatricsIntensive care medicineOutbreakPharmacologyInternal medicinePathologyInfectious disease (medical specialty)Disease

Résumé

récupéré en direct d'OpenAlex

Children have been mostly excluded from COVID-19 clinical trials, and, as a result, most medicines approved for COVID-19 have no pediatric indication. In addition, access to COVID-19 therapeutics remains limited. Collecting physicians' experiences with off-label use of therapeutics is important to inform global prioritization processes and better target pediatric research and development. A standardized questionnaire was designed to explore the use of therapeutics used to treat COVID-19 and multisystem inflammatory syndrome in children (MIS-C) in pediatric patients globally. Seventy-three physicians from 29 countries participated. For COVID-19, steroids were used by 75.6% of respondents; remdesivir and monoclonal antibodies were prescribed by 48.6% and 27.1% of respondents, respectively. For MIS-C, steroids were prescribed by 79.1% of respondents and intravenous immunoglobulins by 69.6%. The use of these products depended on their pediatric approval and the limited availability of antivirals and most monoclonal antibodies in Africa, South America, Southeast Asia, and Eastern Europe. Off-label prescription resulted widespread due to the paucity of clinical trials in young children at the time of the survey; though, based on our survey results, it was generally safe and led to clinical benefits. Conclusion: This survey provides a snapshot of current practice for treating pediatric COVID-19 worldwide, informing global prioritization efforts to better target pediatric research and development for COVID-19 therapeutics. Off-label use of such medicines is widespread for the paucity of clinical trials under 12 years and 40 kg, though appears to be safe and generally results in clinical benefits, even in young children. However, access to care, including medicine availability, differs widely globally. Clinical development of COVID-19 antivirals and monoclonal antibodies requires acceleration to ensure pediatric indication and allow worldwide availability of therapeutics that will enable more equitable access to COVID-19 treatment. What is Known: • Children have been mostly excluded from COVID-19 clinical trials, and, as a result, most medicines approved for COVID-19 have no pediatric indication. • Access to care differs widely globally, so because of the diversity of national healthcare systems; the unequal availability of medicines for COVID-19 treatment represents an obstacle to the pediatric population's universal right to health care. What is New: • Off-label COVID-19 drug prescription is widespread due to the lack of clinical trials in children younger than 12 years and weighing less than 40 kg, but relatively safe and generally leading to clinical benefit. • The application of the GAP-f framework to COVID-19 medicines is crucial, ensuring widespread access to all safe and effective drugs, enabling the rapid development of age-appropriate formulations, and developing specific access plans (including stability, storage, packaging, and labeling) for distribution in low- and middle-income countries (LMICs). Antivirals and monoclonal antibodies may benefit from the acceleration to reach widespread and equal diffusion.

Récupéré en direct depuis OpenAlex et désinversé. Les résumés ne sont pas conservés dans cette base de données : les index inversés représentent 8,6 Go des 9,3 Go de texte de la base, et le serveur dispose de 13 Go libres.

Comment cette classification a été obtenuedéplier

Prédiction distillée sur la base complète

Imitation des enseignants

Ni prévalence calibrée, ni vérité terrain. Validation humaine à venir. Apprise à partir de 10 348 étiquettes directes de Codex et de 10 348 étiquettes directes de Gemma. Le mode candidate est l'union des têtes enseignantes seuillées; le consensus est leur intersection. Ces sorties portent le statut machine_predicted_unvalidated et ne sont ni des étiquettes humaines ni des étiquettes directes de modèles de pointe.

score de la tête « metaresearch » (Codex)0,001
score de la tête « metaresearch » (Gemma)0,001
Version: codex-gemma-dda1882f352aStatut de validation: machine_predicted_unvalidated
Catégories candidatesaucune
Catégories consensuellesaucune
DomaineSignal candidat: aucune · Signal consensuel: aucune
Devis d'étudeSignal candidat: Observationnel · Signal consensuel: Observationnel
GenreSignal candidat: Empirique · Signal consensuel: Empirique
Score de désaccord entre enseignants0,006
Score d'incertitude au seuil0,292

Scores Codex et Gemma par catégorie

CatégorieCodexGemma
Métarecherche0,0010,001
Méta-épidémiologie (sens strict)0,0000,000
Méta-épidémiologie (sens large)0,0000,000
Bibliométrie0,0000,000
Études des sciences et des technologies0,0000,000
Communication savante0,0000,000
Science ouverte0,0000,000
Intégrité de la recherche0,0000,000
Charge utile insuffisante (le modèle a refusé de juger)0,0000,000

Scores machine (provisoires)

Les deux têtes enseignantes du modèle étudiant, lues sur ce travail. Un score ordonne la base pour la relecture; il n'affirme jamais une catégorie, et le statut de validation accompagne chaque rangée tel quel.

Scores de référence d'un modèle non mature (critères de maturité non atteints, 7 itérations). Un score ordonne; il n'affirme jamais une catégorie.

Tête enseignante Opus0,055
Tête enseignante GPT0,333
Écart entre enseignants0,278 · la distance entre les deux têtes enseignantes sur ce seul travail
Statut de validationscore_only:v0-immature-baseline · tel quel depuis la passe de notation : score_only signifie que le nombre peut ordonner les travaux, et qu'aucune étiquette de catégorie n'en découle

Classification

machine, non validée

Prédiction automatique; un appel candidat d’une seule tête enseignante, pas un consensus.

Les modèles n’ont appliqué aucune catégorie : rien dans la taxonomie ne correspondait à ce travail.
Devis d'étudeObservationnel
Domainenon disponible
GenreEmpirique

Le détail, modèle par modèle et score par score, se trouve en fin de page sous « Comment cette classification a été obtenue ».

En bref

Citations0
Publié2023
Routes d'admission1
Résumé présentoui

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