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Enregistrement W4414572355 · doi:10.1016/j.ebiom.2025.105929

Once-daily dolutegravir/lamivudine fixed-dose formulations in children living with HIV: a pharmacokinetic and safety sub-study nested in the open-label, multicentre, randomised, non-inferiority D3/PENTA 21 trial

2025· article· en· W4414572355 sur OpenAlexaff
Lisanne A. H. Bevers, Gabriela Toledo, Muzamil Kisekka, Elizabeth Kaudha, Grace Miriam Ahimbisibwe, Isabelle Déprez, Tiyara Arumugan, Ebrahim Variava, Iona White, Dickson Bbuye, Annet Nanduudu, Enoch Mulwanyi, Pauline Amuge, Diana Rutebarika, Adeodata Kekitiinwa, Cissy Kityo, Philippa Musoke, Moherndran Archary, Justine Boles, Margaret J. Thomason, Saskia N. de Wildt, Carlo Giaquinto, Angela Colbers, David M. Burger, Ann M. Buchanan, Man K. Chan, Tom Jacobs, Anna Turkova, Alessandra Nardone, Gabija Morkunaite, Debbie Ford, Elizabeth C James, Nazia Parkar, Anna Parker, A Omar, Zainab Alkurwi, Moira Spyer, Katja Doerholt, Stephen Townsend, Hannah Sweeney, Alvin Daramola-Rose, Lu Gao, Matteo Quartagno, Diana M. Gibb, Tim R. Cressey, Suwalai Chalermpantmetagul, Rukchanok Peongjakta, Ketwarin Pongkawong, Worathip Sripaoraya, Warunee Khamjakkaew, Namthip Kruenual, Pra-ornsuda Sukrakanchana, Ampika Kaewbundit, Christine Namugwanya, Lameck Kiyimba, Resty Babirye Okello, Florence Namuli, Ronald Nabimba, Angella Baita, Susan Tukamuhebwa, Rachael Namuddu Kikabi, Rose Jacqueline Kadhuba, Henry Balwa, Sarah Nabukalu, Muzamil Nsibuka Kisekka, Anthony Kirabira, L Lawrence, Judith Tikabibamu, M. Aino, Gerald Agaba Muzorah, Collins Mujyanama, Annet Nalugo, Priscilla Namubiru, Victor Musiime, Henry Mugerwa, Caroline Otike, Emmanuel Mujyambere, Dridah Nakiboneka, Barbara Mukanza, Julius Tumusiime, Ritah Mbabazi, Abigail Atwine, Priscilla Kyobutungi, Juliet Ategeka, Alex Musiime, Sharif Musumba, Rashidah Nazzinda, Nicholas Wangwe, Phyllis Mwesigwa, Jameena Elsauko, Mangadalen Nansaigi, Mercy Tukamushaba, Alice Mulindwa, Aidah Nakalyango, Christine Nambi, Milly Ndigendawani, Mariam Naabalamba, Ezra Lutalo, Eddie Rubanga, Josephine Namusanje, Josephine Kobusingye, Disan Mulima, Maria Nannungi, F Balmoi, C Draleku, Faith Mbasani, Crispus Katemba, Juliet Ankunda, Julian Tusiime, Hajira Kataike, Winnie Nansamba, David Balamusani, Rosemary Namwanje, Enoch Mulwanyi, Gerald Businge, Maxensia Owor, Aziida Nabukeera, Ruth Sentongo Nakku, Zainab Nakivumbi Nassoma, Immaculate Nayiga Serunjogi, Barbara Musoke Nakirya, Sarah Nakabuye, Erinah Kyomukama, Rebecca Wampamba, Stella Nalusiba, Emmanuel Mayanja, Donald Wagaana, Zaam Zinda Nakawungu, Sarah Babirye Ssebabi, Olivia Higiro Kaboggoza, Edith Nabawubye, Mildred Kabasonga, Harriet Namusisi, Judith Nampewo, Agnes Mary Mugagga, Richard Isabirye, Francis Sserugo, Annet Kawuma, Agnes Namuddu, Joanita Nankya Baddokwaya, Juliet Nanyonjo, Winifred Kaahwa, Maria Musisi, Paula Mubiru Namayanja, Doreen Twenatwine, Robert Byuma, Winifred Luwedde, M Mugenyi, Joseph Mutebo, Francis Katongole, Fabian Okello, Max Kiwewa, Ronald Okwera, Derick Balungi, Obed Tumwizere, Teopista Nakyanzi, Ann Kankindi, Maria Janine Nambusi, Ivan Rukundo, Henry Odyek, Barnabas Weere, Bosco Kafufu, David Ssebunya, Africano Kamugisha, Emmanual Hakizimana, Charles Nyende, Eva Akurut, Johnson Tumwesigye, Brenda Catherine Kakayi, Rebecca Sakwa, Mark Ssenyonga, Joseph Semakula, Joyce Mwebaza, Judith Kainza, Rosie Mngqibisa, Sada Pillay, Raziya Bobat, Nombuso Nkosi, Nozibusiso Rejoice Mosia, Sheleika Singh, Shingirai Chimene, Jabu Mkhulise, Innocentia Thandokuhle Mncube, Zethu Mnyandu, Popi Shabalala, Simangele Bengu, Ida Elizabeth Mundhree, Tumelo Moloantoa, Nadia Sabet, Ryan Sabet, Modiehi Helen Mosala, Itumeleng Holele, Eva Mogotsi, Angelinah Montwedi, Serame Mokoena, Keabetswe Kotsokoane, Dineo Rampai, Lerato Maretlwa, Palesa Tshipunyane, Iris Matotong, Abraham Mammwn Pattamukkil, Ofhani Harmious Makhari, Zukisa Mpeluza, Abdul Hamid Kaka, R P Stokes, Nadia Bellingan, L. Grange, Leoni Stytler, Zakkiyya Igbal Jeeva, Avy Violari, Afaaf Liberty, Mandisa Nyati, Haseena Cassim, Sisinyana Ruth Mathiba, Lindiwe Maseko, Jackie Brown, Emily Lebotsa, Deirdre Josipovic, Mantwa Kunene, Nasreen Abrahams, Zaakirah Essack, Z Mtshali, Dipuo Dhlomoza, Thabile Degracia Hlomuka, Valerie Khemese, Pradthana Ounchanum, Suchada Ruenglerdpong, Areerat Kongponoi, Kanyanee Kaewmamueng, Warunee Srisuk, Yupawan Thaweesombat, Sukanda Denjanta, Jutarat Thewsoongnoen, Naowarat Kunyanone, Sakulrat Srirojana, Doungjai Donngern, P. Phunkhum, A. Kamkoonmongkol, Thananya Naksomboon, N. Na Kalasin, Ussanee Srirompotong, Athiporn Rungsapphaiboon, Wallapa Daechasatain, Wanchalerm Boonsub, Patamawadee Sudsaard, Thunyasiri Dechboran, Manthana Mitchai, Thanawat Samranphit, Orapin Wannasri, K. Kongsuk, Suparat Kanjanavanit, Rujirek Kamolrattana, Thannapat Chankun, Jiraporn Punyayen, Chayakorn Saewtrakool, Pacharaporn Yingyong, Raungwit Junkaew, Benjawan Thomyota, Kanokkorn Sawasdichai, Chaiwat Ngampiyaskul, Nantika Paiboon, Benjama I-nala, Wanna Chamjamrat, Pisut Greetanukroh, Chanthaporn Imbumroong, Sasipass Khannak, Rattana Chahmeanprabnakorn, Steven Welch, Ezgi Seager, Yvonne Beuvink, Melanie Rooney, Laura Thrasyvoulou, Katie Price, Molly Williams, Alasdair Bamford, Delane Shingadia, Jade Sugars, Olamide Alimi, C.S.K. Chan, Kelly Cripps, Sara S. El Zahed, J. B. Koroma, Clàudia Fortuny, Antoni Noguera‐Julián, A Marchan, K Sanchez, B Ruiz, Pablo Rojo, Cristina Epalza, Luis Prieto, José Tomás Ramos, Ianire Gallego, Verónica Martín, Lilit Manukyan, Manuel Gijón, Daniel F. Carr, Andrew Owen, Rebecca L. Jensen, Eleni Nastouli, Matt Byott, I Botha, Paul Revill, Simon Walker, Magda Conway, Lungile Jafta, Mercy Shibemba, Hermione Lyall, Elizabeth Obimbo, Theodore Ruel, Alexandra Compagnucci, Imelda Mahaka, Fanele Bulose, Gugulethu Bomela, Anton Pozniak, Jane Crawley, Rodolphe Thiébaut, Helen McIlleron

Notice bibliographique

RevueEBioMedicine · 2025
Typearticle
Langueen
DomaineMedicine
ThématiqueHIV/AIDS drug development and treatment
Établissements canadiensGlaxoSmithKline (Canada)
Organismes subventionnairesNIHR Clinical Research Network North West LondonRadboud Universitair Medisch CentrumViiV Healthcare
Mots-clésPharmacokineticsClinical trialMEDLINERandomized controlled trial

Résumé

récupéré en direct d'OpenAlex

Background Two-drug regimen dolutegravir/lamivudine (DTG/3TC) is recommended as an alternative to standard three-drug regimens in adult treatment guidelines. This nested pharmacokinetic sub-study within the D3/Penta 21 randomised trial (#NCT04337450) assessed DTG and 3TC concentrations and safety in virologically-suppressed children, switching to once-daily DTG/3TC fixed-dose formulations. Methods Children aged 2–<15 years received either 5/30 mg DTG/3TC dispersible tablets (DT) or 50/300 mg film-coated tablets (FCT), using WHO weight band (WB)-aligned dosing: 10–<14 kg 4 DTs; 14–<20 kg 5 DTs; 20–<25 kg 6 DTs or 1 FCT; 25–<40 kg 1 FCT. A minimum of 8-evaluable pharmacokinetic curves per WB/formulation were targeted for 24 h pharmacokinetic profiling (t = 0, 1, 2, 3, 4, 6, and 24 h post-dosing) at steady state. The number of children with DTG C trough <0.32 mg/L (EC90) and <0.064 mg/L (PA-IC90) were summarised. Safety was evaluated through 48 weeks in eligible children consented to the pharmacokinetic sub-study. Findings Between 11th May 2022 and 31st May 2023, 82 children consented for the sub-study. Seventy-two were included in the pharmacokinetic analysis; median (IQR) age was 7.1 (4.9–10.0) years and weight 21.6 (17.7–24.8) kg. DTG geometric mean (GM) (%CV) C trough and AUC 0–24 h were 0.82 (54) mg/L and 66.2 (35) h∗mg/L. 3TC GM-AUC 0–24 h was 16.2 (45) h∗mg/L. Three children had DTG C trough <0.32 mg/L, all had DTG C trough ≥0.064 mg/L. In children weighing 20–<25 kg WB and taking 1 FCT (50/300 mg) 3TC GM AUC 0–24 h was 19% higher than in children ≥25 kg (1 FCT). Of 82 children, 3 had 4 serious adverse events (SAEs) and 5 had 6 grade ≥3 adverse events (AEs). No AEs were related to DTG/3TC or resulted in treatment discontinuation. No 3TC-related AEs or laboratory abnormalities were observed in children taking FCT in the 20–<25 kg WB. PK parameters were comparable to historical paediatric data from ODYSSEY (DTG) and IMPAACT2019 (3TC) trials. Interpretation The study demonstrated adequate DTG and 3TC exposures with reassuring safety profiles using WB-based dosing, supporting licencing applications for dispersible and film-coated DTG/3TC formulations for paediatric use. Funding The D3/Penta 21 trial is sponsored by Fondazione Penta Onlus ETS (Penta) and funded by ViiV Healthcare.

Récupéré en direct depuis OpenAlex et désinversé. Les résumés ne sont pas conservés dans cette base de données : les index inversés représentent 8,6 Go des 9,3 Go de texte de la base, et le serveur dispose de 13 Go libres.

Comment cette classification a été obtenuedéplier

Prédiction distillée sur la base complète

Imitation des enseignants

Ni prévalence calibrée, ni vérité terrain. Validation humaine à venir. Apprise à partir de 10 348 étiquettes directes de Codex et de 10 348 étiquettes directes de Gemma. Le mode candidate est l'union des têtes enseignantes seuillées; le consensus est leur intersection. Ces sorties portent le statut machine_predicted_unvalidated et ne sont ni des étiquettes humaines ni des étiquettes directes de modèles de pointe.

score de la tête « metaresearch » (Codex)0,001
score de la tête « metaresearch » (Gemma)0,000
Version: codex-gemma-dda1882f352aStatut de validation: machine_predicted_unvalidated
Catégories candidatesMéta-épidémiologie (sens strict)
Catégories consensuellesaucune
DomaineSignal candidat: aucune · Signal consensuel: aucune
Devis d'étudeSignal candidat: Observationnel · Signal consensuel: Observationnel
GenreSignal candidat: Empirique · Signal consensuel: Empirique
Score de désaccord entre enseignants0,365
Score d'incertitude au seuil1,000

Scores Codex et Gemma par catégorie

CatégorieCodexGemma
Métarecherche0,0010,000
Méta-épidémiologie (sens strict)0,0000,000
Méta-épidémiologie (sens large)0,0010,000
Bibliométrie0,0010,002
Études des sciences et des technologies0,0000,000
Communication savante0,0000,000
Science ouverte0,0000,000
Intégrité de la recherche0,0000,000
Charge utile insuffisante (le modèle a refusé de juger)0,0000,000

Scores machine (provisoires)

Les deux têtes enseignantes du modèle étudiant, lues sur ce travail. Un score ordonne la base pour la relecture; il n'affirme jamais une catégorie, et le statut de validation accompagne chaque rangée tel quel.

Scores de référence d'un modèle non mature (critères de maturité non atteints, 7 itérations). Un score ordonne; il n'affirme jamais une catégorie.

Tête enseignante Opus0,015
Tête enseignante GPT0,315
Écart entre enseignants0,299 · la distance entre les deux têtes enseignantes sur ce seul travail
Statut de validationscore_only:v0-immature-baseline · tel quel depuis la passe de notation : score_only signifie que le nombre peut ordonner les travaux, et qu'aucune étiquette de catégorie n'en découle

Classification

machine, non validée

Prédiction automatique; un appel candidat d’une seule tête enseignante, pas un consensus.

Devis d'étudeObservationnel
Domainenon disponible
GenreEmpirique

Le détail, modèle par modèle et score par score, se trouve en fin de page sous « Comment cette classification a été obtenue ».

En bref

Citations2
Publié2025
Routes d'admission1
Résumé présentoui

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