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Enregistrement W4417012721 · doi:10.1182/blood-2025-6220

Transfer and integration into a young adult clinic for sickle cell disease: Stay with me

2025· article· en· W4417012721 sur OpenAlexaboutno aff
Elizabeth Prince, Eboni I. Lance, M. Bifano, Lydia H. Pecker

Notice bibliographique

RevueBlood · 2025
Typearticle
Langueen
DomaineHealth Professions
ThématiqueAdolescent and Pediatric Healthcare
Établissements canadiensnon disponible
Organismes subventionnairesnon disponible
Mots-clésYoung adultHematologistAdult careCohortSickle cell anemiaDiseaseMEDLINE

Résumé

récupéré en direct d'OpenAlex

Abstract Introduction: Near universal survival of children with sickle cell disease (SCD) into adulthood makes transition from pediatric to adult care a necessary step. Got Transition guidelines define core elements of healthcare transition but offer little on supporting young people after arrival in adult care. In 2025, the National Alliance of Sickle Cell Centers (NASCC) published consensus definitions of successful transfer and integration into adult SCD care. The purpose of this study was to apply these definitions to our previously described cohort of young adults with SCD at a single Center and identify factors associated with transfer and integration into adult care. Methods – This retrospective cohort study was approved by the Johns Hopkins Institutional Review Board. In May 2025, we collected young adult clinic visits for patients aged 18-24 years who transitioned to our adult Center. All patients attended an initial hematologist visit between March 2019 and May 2024. Patient demographics, disease characteristics, and Montreal Cognitive Assessment (MoCA) screening were collected by chart review. At their first visit, a subset of patients completed the American Society of Hematology's Sickle Cell Disease Transition Readiness Assessment, Transition Intervention Program - Readiness for Transition, and the Adult Sickle Cell Quality of Life Measurement (ASCQ-Me). A NASCC consensus statement defines successful transfer of care as attending two visits with a comprehensive sickle cell program in the first year in adult care. We operationalized this definition as routine visits with the hematologist or advanced practice providers in our Center. The NASCC definition of successful integration into care is completion of at least 50% of annual comprehensive visits in the first 5 years of adult care. We considered one hematologist appointment per calendar year an annual comprehensive visit. Applying these definitions to our cohort, we categorized patients to determine rates of successful transfer and integration. Subsequent analyses determined patient characteristics and survey results associated with these outcomes. Patient characteristics were compared using chi-square tests for independence. Differences in mean ages, scores on cognitive screening assessments, and surveys were compared using t-tests. Results: One hundred and forty-five patients met inclusion criteria, mean age of 22.7 (SD 1.4) years, 57% female, 97% Black, 74% HbSS/HbSβ0 genotypes, and 54% publicly insured. Following the initial young adult clinic hematologist visit, 83% attended a second Center visit within a year, meeting successful transfer of care standards. Failure to transfer was associated with lower cognitive screening scores (mean MoCA score 25.2 vs 23.2, p=0.01). Successful transfer was associated with completion of the ASCQ-Me (51% vs 28% completion, p=0.04). No other associations between characteristics or surveys were identified. Fifty-one patients had 5 years of data from their initial visit until May 2025. Thirty-four (67%) attended at least half of their annual hematologist visits over that period and met criteria for successful integration into adult care. Among the remaining patients, 5 (10%) left the Center, with all but one transferring SCD care elsewhere. Four (8%) remained in the Center, seeing advanced practice providers. Three (6%) moved out of state for work or family, 2 (4%) died, 2 (4%) had successful bone marrow transplant, and 1 (2%) was seen only in consultation. Better cognitive screening scores were also associated with successful integration (mean score 25.7 vs 23.8, p<0.05). There were no patient characteristics or survey results associated with integration. Discussion: Most patients successfully transferred and integrated into a dedicated young adult clinic embedded in a comprehensive adult SCD Center. To our knowledge, this is the first application of NASCC consensus definitions of transfer and integration. Better cognitive screening scores were associated with successful transfer and integration. Participation in specific survey assessments was associated with successful transfer. Of the patients falling below the threshold for integration, nearly half moved or changed care centers, and only one patient became unaffiliated with SCD care entirely. Our findings highlight the challenge of collecting and interpreting appointment attendance data during the dynamic period of young adulthood.

Récupéré en direct depuis OpenAlex et désinversé. Les résumés ne sont pas conservés dans cette base de données : les index inversés représentent 8,6 Go des 9,3 Go de texte de la base, et le serveur dispose de 13 Go libres.

Comment cette classification a été obtenuedéplier

Prédiction machine sur la base complète

Imitation des enseignants

Ni prévalence calibrée, ni vérité terrain. Validation humaine à venir. Le volet Gemma est une étiquette directe du modèle pour chaque travail de la base, lue sur la notice réduite au titre. Le volet Codex est un classifieur appris des 10 348 étiquettes directes de Codex et calibré sur les taux pondérés de l'échantillon; les champs sans appui suffisant ne portent aucun appel Codex. Le mode candidate est l'union des deux volets; le consensus est leur intersection. Ces sorties portent le statut machine_predicted_unvalidated et ne sont pas des étiquettes humaines.

score de la tête « metaresearch » (Codex)0,001
score de la tête « metaresearch » (Gemma)0,002
Version: metacan-v3-hybrid-931329e0061cStatut de validation: machine_predicted_unvalidated
Catégories candidatesaucune
Catégories consensuellesaucune
DomaineSignal candidat: aucune · Signal consensuel: aucune
Devis d'étudeSignal candidat: Qualitatif · Signal consensuel: aucune
GenreSignal candidat: Empirique · Signal consensuel: Empirique
Score de désaccord entre enseignants0,010
Score d'incertitude au seuil0,021

Scores du classifieur distillé par catégorie (deux têtes)

CatégorieCodexGemma
Métarecherche0,0010,002
Méta-épidémiologie (sens strict)0,0000,000
Méta-épidémiologie (sens large)0,0000,000
Bibliométrie0,0010,001
Études des sciences et des technologies0,0010,000
Communication savante0,0010,001
Science ouverte0,0000,001
Intégrité de la recherche0,0000,001
Charge utile insuffisante (le modèle a refusé de juger)0,0030,000

Scores machine (provisoires)

Les deux têtes enseignantes du modèle étudiant, lues sur ce travail. Un score ordonne la base pour la relecture; il n'affirme jamais une catégorie, et le statut de validation accompagne chaque rangée tel quel.

Scores de référence d'un modèle non mature (critères de maturité non atteints, 7 itérations). Un score ordonne; il n'affirme jamais une catégorie.

Tête enseignante Opus0,025
Tête enseignante GPT0,379
Écart entre enseignants0,354 · la distance entre les deux têtes enseignantes sur ce seul travail
Statut de validationscore_only:v0-immature-baseline · tel quel depuis la passe de notation : score_only signifie que le nombre peut ordonner les travaux, et qu'aucune étiquette de catégorie n'en découle

Classification

machine, non validée

Prédiction automatique; un appel candidat d’une seule source (Gemma direct ou Codex distillé), pas un consensus.

Les modèles n’ont appliqué aucune catégorie : rien dans la taxonomie ne correspondait à ce travail.
Devis d'étudeQualitatif
Domainenon disponible
GenreEmpirique

Le détail, modèle par modèle et score par score, se trouve en fin de page sous « Comment cette classification a été obtenue ».

En bref

Citations1
Publié2025
Routes d'admission1
Résumé présentoui

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