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Record W2533344724 · doi:10.15252/emmm.201505719

TECRL, a new life‐threatening inherited arrhythmia gene associated with overlapping clinical features of both LQTS and CPVT

2016· article· en· W2533344724 on OpenAlexafffundabout
Harsha D. Devalla, Roselle Gélinas, Elhadi H. Aburawi, Abdelaziz Beqqali, Philippe Goyette, Christian Freund, Marie Chaix, Rafik Tadros, Hui Jiang, Antony Le Béchec, Jantine Monshouwer‐Kloots, Tom Zwetsloot, Georgios Kosmidis, Frédéric Latour, Azadeh Alikashani, Maaike Hoekstra, Jürg Schlaepfer, Christine L. Mummery, Brian J. Stevenson, Zoltán Kutalik, Antoine AF de Vries, Léna Rivard, Mario Talajic, Arie O. Verkerk, Lihadh Al‐Gazali, John D. Rioux, Zahurul A. Bhuiyan, Robert Passier

Bibliographic record

VenueEMBO Molecular Medicine · 2016
Typearticle
Languageen
FieldMedicine
TopicCardiac electrophysiology and arrhythmias
Canadian institutionsUniversité de MontréalMontreal Heart Institute
FundersSwiss Institute of BioinformaticsInstitut de Cardiologie de MontréalNederlandse Federatie van Universitair Medische CentraUniversitätsspital ZürichUniversität ZürichCentre Hospitalier Universitaire VaudoisHospital for Sick ChildrenUniversité de MontréalLeids Universitair Medisch CentrumSchweizerische HerzstiftungUniversity of TorontoSchweizerischer Nationalfonds zur Förderung der Wissenschaftlichen ForschungKoninklijke Nederlandse Akademie van WetenschappenEuropean Research CouncilMcMaster UniversityNational Institute of Advanced Industrial Science and TechnologyHelsingin ja Uudenmaan SairaanhoitopiiriFondation LeenaardsHelsingin YliopistoHartstichtingUniversidad de ChileUniversitätsspital BaselAmerican University of BeirutZonMwAlbert-Ludwigs-Universität FreiburgKaiser PermanenteNational Science Foundation
KeywordsCatecholaminergic polymorphic ventricular tachycardiaRyanodine receptor 2SERCASudden deathInternal medicineMedicineSudden cardiac deathLong QT syndromeAfterdepolarizationTachycardiaExome sequencingRepolarizationProbandEndocrinologyRyanodine receptorMutationCalciumChemistryBiologyGeneQT intervalGeneticsElectrophysiologyBiochemistry

Abstract

fetched live from OpenAlex

Abstract Genetic causes of many familial arrhythmia syndromes remain elusive. In this study, whole‐exome sequencing ( WES ) was carried out on patients from three different families that presented with life‐threatening arrhythmias and high risk of sudden cardiac death ( SCD ). Two French Canadian probands carried identical homozygous rare variant in TECRL gene (p.Arg196Gln), which encodes the trans ‐2,3‐enoyl‐CoA reductase‐like protein. Both patients had cardiac arrest, stress‐induced atrial and ventricular tachycardia, and QT prolongation on adrenergic stimulation. A third patient from a consanguineous Sudanese family diagnosed with catecholaminergic polymorphic ventricular tachycardia ( CPVT ) had a homozygous splice site mutation (c.331+1G>A) in TECRL . Analysis of intracellular calcium ([Ca 2+ ] i ) dynamics in human induced pluripotent stem cell‐derived cardiomyocytes (hi PSC ‐ CM s) generated from this individual ( TECRL H om ‐hi PSC s), his heterozygous but clinically asymptomatic father ( TECRL H et ‐hi PSC s), and a healthy individual ( CTRL ‐hi PSC s) from the same Sudanese family, revealed smaller [Ca 2+ ] i transient amplitudes as well as elevated diastolic [Ca 2+ ] i in TECRL H om ‐hi PSC ‐ CM s compared with CTRL ‐hi PSC ‐ CM s. The [Ca 2+ ] i transient also rose markedly slower and contained lower sarcoplasmic reticulum ( SR ) calcium stores, evidenced by the decreased magnitude of caffeine‐induced [Ca 2+ ] i transients. In addition, the decay phase of the [Ca 2+ ] i transient was slower in TECRL H om ‐hi PSC ‐ CM s due to decreased SERCA and NCX activities. Furthermore, TECRL H om ‐hi PSC ‐ CM s showed prolonged action potentials ( AP s) compared with CTRL ‐hi PSC ‐ CM s. TECRL knockdown in control human embryonic stem cell‐derived CM s ( hESC ‐ CM s) also resulted in significantly longer AP s. Moreover, stimulation by noradrenaline ( NA ) significantly increased the propensity for triggered activity based on delayed afterdepolarizations ( DAD s) in TECRL H om ‐hi PSC ‐ CM s and treatment with flecainide, a class Ic antiarrhythmic drug, significantly reduced the triggered activity in these cells. In summary, we report that mutations in TECRL are associated with inherited arrhythmias characterized by clinical features of both LQTS and CPVT . Patient‐specific hi PSC ‐ CM s recapitulated salient features of the clinical phenotype and provide a platform for drug screening evidenced by initial identification of flecainide as a potential therapeutic. These findings have implications for diagnosis and treatment of inherited cardiac arrhythmias.

Fetched live from OpenAlex and de-inverted. Abstracts are not stored in this database: the inverted indexes are 8.6 GB of the frame’s 9.3 GB of text, and the host has 13 GB free.

How this classification was reachedexpand

Full frame distilled prediction

Teacher imitation

Not calibrated prevalence, not ground truth. Human validation pending. Learned from the 10,348 direct Codex labels and 10,348 direct Gemma labels. Candidate is the union of thresholded teacher heads; consensus is their intersection. These outputs are machine_predicted_unvalidated and are not human labels or direct frontier model labels.

metaresearch head score (Codex)0.000
metaresearch head score (Gemma)0.002
Version: codex-gemma-dda1882f352aValidation status: machine_predicted_unvalidated
Candidate categoriesnone
Consensus categoriesnone
DomainCandidate signal: none · Consensus signal: none
Study designCandidate signal: Bench or experimental · Consensus signal: none
GenreCandidate signal: Empirical · Consensus signal: Empirical
Teacher disagreement score0.923
Threshold uncertainty score0.696

Codex and Gemma teacher scores by category

CategoryCodexGemma
Metaresearch0.0000.002
Meta-epidemiology (narrow)0.0000.000
Meta-epidemiology (broad)0.0010.000
Bibliometrics0.0000.000
Science and technology studies0.0000.001
Scholarly communication0.0000.000
Open science0.0000.000
Research integrity0.0000.000
Insufficient payload (model declined to judge)0.0000.000

Machine scores (provisional)

The two teacher heads of the student model, read on this work. A score orders the frame for review; it never asserts a category, and the validation status ships verbatim with every row.

Baseline scores from an immature model (maturity gate not passed, 7 training rounds). Scores rank; they never assert a category.

Opus teacher head0.016
GPT teacher head0.284
Teacher spread0.268 · how far apart the two teachers sit on this one work
Validation statusscore_only:v0-immature-baseline · verbatim from the scoring run: score_only means the number may rank works, and no category label ships from it

Classification

machine, unvalidated

Machine predicted; a candidate call from one teacher head, not a consensus.

The models applied no category: nothing in the taxonomy fit this work.
Study designBench or experimental
Domainnot available
GenreEmpirical

How this classification was reached, model by model and score by score, is at the end of the page under "How this classification was reached".

Quick stats

Citations133
Published2016
Admission routes3
Has abstractyes

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