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Record W2589148380 · doi:10.1002/mgg3.266

Structural modeling of a novel <i><scp>SLC</scp>38A8</i> mutation that causes foveal hypoplasia

2017· article· en· W2589148380 on OpenAlexaff
Marcus A. Toral, Gabriel Velez, Katherine Boudreault, Kellie A. Schaefer, Yu Xu, Norman Saffra, Alexander G. Bassuk, Stephen H. Tsang, Vinit B. Mahajan

Bibliographic record

VenueMolecular Genetics & Genomic Medicine · 2017
Typearticle
Languageen
FieldBiochemistry, Genetics and Molecular Biology
TopicRetinal Development and Disorders
Canadian institutionsUniversité de Montréal
FundersNational Institute of General Medical SciencesNational Cancer InstituteNational Institutes of HealthCongressionally Directed Medical Research ProgramsFoundation Fighting BlindnessCrowley Family FoundationNational Institute on AgingResearch to Prevent BlindnessNational Eye InstituteDoris Duke Charitable Foundation
KeywordsMutationGeneticsPoint mutationAchromatopsiaHypoplasiaFovealBiologyMedicineRetinalPathologyBioinformaticsOphthalmologyAnatomyGene

Abstract

fetched live from OpenAlex

Abstract Background Foveal hypoplasia ( FH ) in the absence of albinism, aniridia, microphthalmia, or achromatopsia is exceedingly rare, and the molecular basis for the disorder remains unknown. FH is characterized by the absence of both the retinal foveal pit and avascular zone, but with preserved retinal architecture. SLC 38A8 encodes a sodium‐coupled neutral amino acid transporter with a preference for glutamate as a substrate. SLC 38A8 has been linked to FH . Here, we describe a novel mutation to SLC 38A8 which causes FH , and report the novel use of OCT ‐angiography to improve the precision of FH diagnosis. More so, we used computational modeling to explore possible functional effects of known SLC 38A8 mutations. Methods Fundus autofluorescence, SD ‐ OCT , and OCT ‐angiography were used to make the clinical diagnosis. Whole‐exome sequencing led to the identification of a novel disease‐causing variant in SLC 38A8 . Computational modeling approaches were used to visualize known SLC 38A8 mutations, as well as to predict mutation effects on transporter structure and function. Results We identified a novel point mutation in SLC 38A8 that causes FH . A conclusive diagnosis was made using OCT ‐angiography, which more clearly revealed retinal vasculature penetrating into the foveal region. Structural modeling of the channel showed the mutation was near previously published mutations, clustered on an extracellular loop. Our modeling also predicted that the mutation destabilizes the protein by altering the electrostatic potential within the channel pore. Conclusion Our results demonstrate a novel use for OCT ‐angiography in confirming FH , and also uncover genotype–phenotype correlations of FH ‐linked SLC 38A8 mutations.

Fetched live from OpenAlex and de-inverted. Abstracts are not stored in this database: the inverted indexes are 8.6 GB of the frame’s 9.3 GB of text, and the host has 13 GB free.

How this classification was reachedexpand

Full frame distilled prediction

Teacher imitation

Not calibrated prevalence, not ground truth. Human validation pending. Learned from the 10,348 direct Codex labels and 10,348 direct Gemma labels. Candidate is the union of thresholded teacher heads; consensus is their intersection. These outputs are machine_predicted_unvalidated and are not human labels or direct frontier model labels.

metaresearch head score (Codex)0.000
metaresearch head score (Gemma)0.000
Version: codex-gemma-dda1882f352aValidation status: machine_predicted_unvalidated
Candidate categoriesMeta-epidemiology (narrow)
Consensus categoriesnone
DomainCandidate signal: none · Consensus signal: none
Study designCandidate signal: Bench or experimental · Consensus signal: Bench or experimental
GenreCandidate signal: Empirical · Consensus signal: Empirical
Teacher disagreement score0.121
Threshold uncertainty score1.000

Codex and Gemma teacher scores by category

CategoryCodexGemma
Metaresearch0.0000.000
Meta-epidemiology (narrow)0.0000.000
Meta-epidemiology (broad)0.0000.000
Bibliometrics0.0000.000
Science and technology studies0.0000.000
Scholarly communication0.0000.000
Open science0.0010.000
Research integrity0.0000.000
Insufficient payload (model declined to judge)0.0000.000

Machine scores (provisional)

The two teacher heads of the student model, read on this work. A score orders the frame for review; it never asserts a category, and the validation status ships verbatim with every row.

Baseline scores from an immature model (maturity gate not passed, 7 training rounds). Scores rank; they never assert a category.

Opus teacher head0.026
GPT teacher head0.269
Teacher spread0.243 · how far apart the two teachers sit on this one work
Validation statusscore_only:v0-immature-baseline · verbatim from the scoring run: score_only means the number may rank works, and no category label ships from it

Classification

machine, unvalidated

Machine predicted; a candidate call from one teacher head, not a consensus.

Study designBench or experimental
Domainnot available
GenreEmpirical

How this classification was reached, model by model and score by score, is at the end of the page under "How this classification was reached".

Quick stats

Citations26
Published2017
Admission routes1
Has abstractyes

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