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PF408 DASFREE 2‐YEAR UPDATE: DASATINIB DISCONTINUATION IN PATIENTS (PTS) WITH CHRONIC MYELOID LEUKEMIA IN CHRONIC PHASE (CML‐CP) AND DEEP MOLECULAR RESPONSE (DMR)

2019· article· en· W2951051106 on OpenAlexaff
Nirav Shah, Valentín García‐Gutiérrez, Antonio Jiménez‐Velasco, Sarah Larson, Susanne Saußele, Delphine Réa, François‐Xavier Mahon, Moshe Levy, María Teresa Gómez‐Casares, Luigiana Luciano, F.‐E. Nicolini, Michael J. Mauro, Oumar Sy, Patricia Martin‐Regueira, J. H. Lipton

Bibliographic record

VenueHemaSphere · 2019
Typearticle
Languageen
FieldMedicine
TopicChronic Myeloid Leukemia Treatments
Canadian institutionsPrincess Margaret Cancer CentreUniversity of Toronto
Fundersnot available
KeywordsDasatinibDiscontinuationMedicineInternal medicineClinical endpointOncologyMyeloid leukemiaImatinibGastroenterologyClinical trial

Abstract

fetched live from OpenAlex

Background: Treatment‐free remission (TFR) is a potential treatment goal for pts with CML‐CP. Sustained TFR has previously been reported for pts enrolled in the DASFREE trial (CA180406/NCT01850004), in which a 48% rate of relapse‐free survival was observed at 18 mo after dasatinib discontinuation (Shah Blood 2018). Here we report results for pts in DASFREE with a minimum of 2 y of follow‐up. Aims: To assess the durability of TFR at 2 y after discontinuing dasatinib treatment in pts with CML‐CP and dasatinib‐induced DMR. Methods: DASFREE is an open‐label, single‐arm phase 2 study in adult pts with CML‐CP on first‐line (1L) or subsequent‐line (≥2L) dasatinib for ≥2 y and with DMR (MR 4.5 ; BCR‐ABL1 ≤0.0032% on the International Scale [IS]). MR 4.5 was confirmed at a local lab for ≥1 y prior to enrollment and confirmed at a central lab twice within 3 mo prior to dasatinib discontinuation. BCR‐ABL1 was monitored centrally every mo after discontinuation in the 1st y and every 3 mo thereafter. If major molecular response (MMR; BCR‐ABL1 ≤0.1% IS) was lost, pts resumed dasatinib at their previous dose. The primary endpoint was the rate of MMR at 12 mo after discontinuation without restarting dasatinib. Key secondary endpoints include event‐free survival (EFS; survival with no loss of MMR), rate of transformation to accelerated phase/blast crisis (AP/BC), progression‐free survival (PFS; survival without progression to AP/BC), and overall survival. Key exploratory analyses include the frequency of adverse events (AEs) on and off treatment. Results: Pt characteristics were previously reported; briefly, 37 pts (44%) discontinued 1L dasatinib and 47 pts (56%) discontinued ≥2L dasatinib (Shah Blood 2018). To date, 11 pts (13%) have discontinued the study (2 off‐treatment; 9 after restarting dasatinib). In total, 46 pts lost MMR (1 pt lost MMR at mo 39 and had not restarted therapy at the time of this analysis) after a median of 4 mo (range 1–39) after discontinuation. Of the 46 pts who lost MMR, 45 (98%) restarted on dasatinib; 44 of 45 (98%) regained MMR after a median of 2 mo (range 1–4) and 43 (96%) regained MR 4.5 after a median of 3 mo (range 2–18) ( Figure ). At 2 y, EFS was 46% (95% confidence interval [CI] 36, 57) in all pts, 51% (95% CI 35, 67) in 1L pts, and 42% (95% CI 28, 57) in ≥2L pts. PFS at 2 y was 99% (95% CI 96, 100) in all pts (there was 1 death unrelated to CML). No pts transformed to AP/BC. Time on prior treatment (regardless of line of dasatinib) was 65 mo for pts who lost MMR (n = 19) and 73 mo for pts who maintained MMR (n = 18). A univariate analysis revealed statistically significant associations between EFS and older age (hazard ratio [HR] 2.722; 95% CI 1.126, 6.578; P = 0.0261) and prior 1L therapy (HR 0.381; 95% CI 0.162, 0.893; P = 0.0265). All AEs observed thus far in DASFREE have been consistent with the known safety profile of dasatinib. There were 2 additional withdrawal events (in the same pts) at this follow‐up. Summary/Conclusion: Extended follow‐up results from DASFREE continue to support the feasibility of TFR in pts with CML‐CP who achieve stable DMR with dasatinib. The observed durability of TFR at 2 y (with 46% of all pts maintaining EFS) provides clinically relevant information for many pts considering TFR with dasatinib in the 1L and beyond. Lastly, no new pts experienced withdrawal events. image

Fetched live from OpenAlex and de-inverted. Abstracts are not stored in this database: the inverted indexes are 8.6 GB of the frame’s 9.3 GB of text, and the host has 13 GB free.

How this classification was reachedexpand

Full frame distilled prediction

Teacher imitation

Not calibrated prevalence, not ground truth. Human validation pending. Learned from the 10,348 direct Codex labels and 10,348 direct Gemma labels. Candidate is the union of thresholded teacher heads; consensus is their intersection. These outputs are machine_predicted_unvalidated and are not human labels or direct frontier model labels.

metaresearch head score (Codex)0.000
metaresearch head score (Gemma)0.000
Version: codex-gemma-dda1882f352aValidation status: machine_predicted_unvalidated
Candidate categoriesMeta-epidemiology (narrow), Insufficient payload (model declined to judge)
Consensus categoriesnone
DomainCandidate signal: none · Consensus signal: none
Study designCandidate signal: Observational · Consensus signal: Observational
GenreCandidate signal: Empirical · Consensus signal: Empirical
Teacher disagreement score0.209
Threshold uncertainty score1.000

Codex and Gemma teacher scores by category

CategoryCodexGemma
Metaresearch0.0000.000
Meta-epidemiology (narrow)0.0000.000
Meta-epidemiology (broad)0.0010.000
Bibliometrics0.0000.001
Science and technology studies0.0000.000
Scholarly communication0.0000.000
Open science0.0000.000
Research integrity0.0000.001
Insufficient payload (model declined to judge)0.0010.000

Machine scores (provisional)

The two teacher heads of the student model, read on this work. A score orders the frame for review; it never asserts a category, and the validation status ships verbatim with every row.

Baseline scores from an immature model (maturity gate not passed, 7 training rounds). Scores rank; they never assert a category.

Opus teacher head0.006
GPT teacher head0.249
Teacher spread0.243 · how far apart the two teachers sit on this one work
Validation statusscore_only:v0-immature-baseline · verbatim from the scoring run: score_only means the number may rank works, and no category label ships from it

Classification

machine, unvalidated

Machine predicted; a candidate call from one teacher head, not a consensus.

Study designObservational
Domainnot available
GenreEmpirical

How this classification was reached, model by model and score by score, is at the end of the page under "How this classification was reached".

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Citations2
Published2019
Admission routes1
Has abstractyes

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