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Record W2955606726 · doi:10.1016/j.conctc.2019.100402

An alternative trial-level measure for evaluating failure-time surrogate endpoints based on prediction error

2019· article· en· W2955606726 on OpenAlex
Shaima Belhechmi, Stefan Michiels, Xavier Paolettí, Federico Rotolo

Why this work is in the frame

A frame that forgets how it found something cannot be audited. These are the routes that admitted this work.

fundA Canadian funder is recorded on the work.
no affNo Canadian affiliation: this work is invisible to an affiliation-only frame.
No Canadian affiliation. An affiliation-only frame, the usual design, would never have seen this work. It is one of the works that make the case for inverting the frame.

Bibliographic record

VenueContemporary Clinical Trials Communications · 2019
Typearticle
Languageen
FieldMathematics
TopicStatistical Methods in Clinical Trials
Canadian institutionsnot available
FundersInstitute of Cancer ResearchInstitut National Du CancerLigue Contre le Cancer
KeywordsStatisticsCorrelationSurrogate endpointStandard errorClinical trialMeasure (data warehouse)MathematicsMedicineComputer scienceData miningInternal medicine

Abstract

fetched live from OpenAlex

To validate a failure-time surrogate for an established failure-time clinical endpoint such as overall survival, the meta-analytic approach is commonly used. The standard correlation approach considers two levels: the individual level, with Kendall's τ measuring the rank correlation between the endpoints, and the trial level, with the coefficient of determination R2 measuring the correlation between the treatment effects on the surrogate and on the final endpoint. However, the estimation of R2 is not robust with respect to the estimation error of the trial-specific treatment effects. The alternative proposed in this article uses a prediction error based on a measure of the weighted difference between the observed treatment effect on the final endpoint and a model-based predicted effect. The measures can be estimated by cross-validation within the meta-analytic setting or external validation on a set of trials. Several distances are presented, with varying weights, based on the standard error of the observed treatment effect and of its predicted value. A simulation study was conducted under different scenarios, varying the number and the size of the trials, Kendall's τ and R2. These measures have been applied to individual patient data from a meta-analysis of trials in advanced/recurrent gastric cancer (20 randomized trials of chemotherapy, 4069 patients). The distance-based measures appeared to be robust with respect to different values of simulation parameters in several scenarios (such as Kendall's τ, size and number of clinical trials). The absolute prediction error can be an alternative to the trial-level R2 for evaluation of candidate time-to-event surrogates.

Fetched live from OpenAlex and de-inverted. Abstracts are not stored in this database: the inverted indexes are 8.6 GB of the frame’s 9.3 GB of text, and the host has 13 GB free.

Full frame distilled prediction

Teacher imitation

Not calibrated prevalence, not ground truth. Human validation pending. Learned from the 10,348 direct Codex labels and 10,348 direct Gemma labels. Candidate is the union of thresholded teacher heads; consensus is their intersection. These outputs are machine_predicted_unvalidated and are not human labels or direct frontier model labels.

metaresearch head score (Codex)0.148
metaresearch head score (Gemma)0.606
Version: codex-gemma-dda1882f352aValidation status: machine_predicted_unvalidated
Candidate categoriesMetaresearch, Meta-epidemiology (narrow)
Consensus categoriesMetaresearch
DomainCandidate signal: none · Consensus signal: none
Study designCandidate signal: Theoretical or conceptual · Consensus signal: none
GenreCandidate signal: Methods · Consensus signal: Methods
Teacher disagreement score0.458
Threshold uncertainty score1.000

Codex and Gemma teacher scores by category

CategoryCodexGemma
Metaresearch0.1480.606
Meta-epidemiology (narrow)0.0010.001
Meta-epidemiology (broad)0.0040.002
Bibliometrics0.0000.000
Science and technology studies0.0000.001
Scholarly communication0.0000.000
Open science0.0030.000
Research integrity0.0010.001
Insufficient payload (model declined to judge)0.0010.000

Machine scores (provisional)

The two teacher heads of the student model, read on this work. A score orders the frame for review; it never asserts a category, and the validation status ships verbatim with every row.

Baseline scores from an immature model (maturity gate not passed, 7 training rounds). Scores rank; they never assert a category.

Opus teacher head0.935
GPT teacher head0.690
Teacher spread0.245 · how far apart the two teachers sit on this one work
Validation statusscore_only:v0-immature-baseline · verbatim from the scoring run: score_only means the number may rank works, and no category label ships from it