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Fraction of exhaled nitric oxide increases in children treated with elexacaftor-tezacaftor-ivacaftor

2023· article· en· W4387979629 on OpenAlexaff
Isaac Martín de Diego, Félix Ratjen, Hartmut Grasemann

Bibliographic record

Venuenot available
Typearticle
Languageen
FieldHealth Professions
TopicPediatric health and respiratory diseases
Canadian institutionsHospital for Sick Children
Fundersnot available
KeywordsIvacaftorMedicineCystic fibrosisExhaled nitric oxideObservational studyInternal medicineAirwayCombination therapyAsthmaAnesthesiaCystic fibrosis transmembrane conductance regulatorSpirometry

Abstract

fetched live from OpenAlex

Introduction: Airway nitric oxide (FENO) in people with cystic fibrosis (CF) is lower than normal and ivacaftor results in an early and sustained increase in FENO in treated individuals (Grasemann H et al. Eur Respir J. 2020). The effect of elexacaftor-tezacaftor-ivacaftor (ETI) on airway NO is not known. We aimed to study the effect of ETI on FENO in children with CF. Methods: This is a prospective observational study in children with CF 6-18 years old and started on ETI therapy. The study was approved by the local REB. FENO was measured before and 1-3 months after ETI initiation at regular clinic visits using a Niox Vero device. Comparisons between pre and post were made with t-test or Wilcoxon test, where appropriate. Results: Thirty-eight patients (median 14.8 yrs, IQR 11.5-16.9) were included, 21 were male, 24 F508del homozygous, 28 were naïve to CFTR modulator therapy, and 10 switched from lumacaftor-ivacaftor to ETI. Baseline and follow-up FENO (median, IQ range) values are shown in the table. There was no correlation between FENO or changes in FENO with sweat chloride levels or pulmonary function (FEV1). Conclusions: ETI results in an increase in FENO in treated children with CF 1-3 months after initiation of therapy. The increase in FENO seems more robust in F508del/F508del patients naïve to CFTR modulator therapy compared to those switched from lumacaftor-ivacaftor or those with a single F508del allele.

Fetched live from OpenAlex and de-inverted. Abstracts are not stored in this database: the inverted indexes are 8.6 GB of the frame’s 9.3 GB of text, and the host has 13 GB free.

How this classification was reachedexpand

Direct model labels (unvalidated)

Per-model category and study-design labels from the labeling rounds. They are machine output, unvalidated, and the disagreement between models ships as data. No study design here is MEDLINE-validated yet.

Model armCategoriesStudy designConfidence
gemmano category
Domain: not available · Genre: Empirical
About the Canadian research system: no · About a Canadian topic: no
Observationallow
gptno category
Domain: not available · Genre: Empirical
About the Canadian research system: no · About a Canadian topic: no
Observationalhigh
models agreeAgreement compares identical category sets and study designs across arms.

Full frame machine prediction

Teacher imitation

Not calibrated prevalence, not ground truth. Human validation pending. The Gemma side is a direct model label for every work in the frame, read from the title-only record. The Codex side is a classifier learned from the 10,348 direct Codex labels and calibrated to design-weighted sample rates; fields without enough sample support carry no Codex call. Candidate is the union of the two sides; consensus is their intersection. These outputs are machine_predicted_unvalidated and are not human labels.

metaresearch head score (Codex)0.000
metaresearch head score (Gemma)0.002
Version: metacan-v3-hybrid-931329e0061cValidation status: machine_predicted_unvalidated
Candidate categoriesnone
Consensus categoriesnone
DomainCandidate signal: none · Consensus signal: none
Study designCandidate signal: Observational · Consensus signal: Observational
GenreCandidate signal: Empirical · Consensus signal: Empirical
Teacher disagreement score0.003
Threshold uncertainty score0.007

Distilled classifier scores by category (both heads)

CategoryCodexGemma
Metaresearch0.0000.002
Meta-epidemiology (narrow)0.0000.000
Meta-epidemiology (broad)0.0010.001
Bibliometrics0.0010.001
Science and technology studies0.0000.000
Scholarly communication0.0010.000
Open science0.0000.000
Research integrity0.0010.001
Insufficient payload (model declined to judge)0.0020.000

Machine scores (provisional)

The two teacher heads of the student model, read on this work. A score orders the frame for review; it never asserts a category, and the validation status ships verbatim with every row.

Baseline scores from an immature model (maturity gate not passed, 7 training rounds). Scores rank; they never assert a category.

Opus teacher head0.028
GPT teacher head0.366
Teacher spread0.338 · how far apart the two teachers sit on this one work
Validation statusscore_only:v0-immature-baseline · verbatim from the scoring run: score_only means the number may rank works, and no category label ships from it

Classification

machine, unvalidated

Labeled directly by 2 models reading the full record.

The models applied no category: nothing in the taxonomy fit this work.
Study designObservational
Domainnot available
GenreEmpirical

How this classification was reached, model by model and score by score, is at the end of the page under "How this classification was reached".

Quick stats

Citations1
Published2023
Admission routes1
Has abstractyes

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