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Record W4389243521 · doi:10.1182/blood-2023-185210

Prevalence and Risk Factors of Diagnostic Delays in Acquired Hemophilia A

2023· article· en· W4389243521 on OpenAlexaffabout
Bradley Rutherford, Ellen Cusano, M. Dawn Goodyear, Haowei Sun

Bibliographic record

VenueBlood · 2023
Typearticle
Languageen
FieldMedicine
TopicHemophilia Treatment and Research
Canadian institutionsUniversity of CalgaryUniversity of Alberta
Fundersnot available
KeywordsMedicinePediatricsLogistic regressionCohortProportional hazards modelRetrospective cohort studyComorbidityInternal medicine

Abstract

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Introduction: Acquired hemophilia A (AHA) is a rare bleeding disorder characterized by autoantibodies against factor VIII (FVIII). Delayed diagnosis is frequent, resulting in morbidity and health resource utilization. Predictors of diagnostic delays and their impact on outcomes are unclear. Aims: 1) Evaluate the time from presentation to AHA diagnosis, in a large Canadian province, 2) examine predictors of diagnostic delays, and 3) assess the impact of delays on outcomes and resource utilization. Methods: This multicentre retrospective cohort study included adults (≥18 years) diagnosed with AHA (January 2000-December 2021) in Alberta, Canada. Alberta's 661,848 km 2 geographic area encompasses two adult hemophilia treatment centres (HTCs). We assessed the prevalence of delayed diagnosis (from bleeding or first prolonged aPTT) and examined the impact of sociodemographic variables (age, sex, rural residence, living arrangement, initial presentation to HTC) and disease variables (AHA etiology, major bleed at presentation, comorbidities, FVIII activity and inhibitor titre) on the diagnostic delays. Case-based analysis and logistic regression were used to identify contributory factors and predictors of diagnostic delays, respectively. Kaplan-Meier curves were used to estimate overall survival (OS), and Cox proportional hazards regression analysis was used to assess the impact of diagnostic delays on OS. Ethics board approval was obtained. Results: Of the 38 patients diagnosed with AHA, 25 (66%) were female, 8 (21%) resided in rural areas, and 10 (26%) resided >100 km from HTC. Median age was 74 years (IQR 61-81), with marked comorbidities (median Charlson comorbidity index [CCI] 5, IQR 3-7). Most patients (27; 71%) initially presented to non-HTCs while 32 (84%) were eventually admitted to HTCs. At presentation, 27 (71%) had ISTH major bleeding and 13 (34%) were on anticoagulants or antiplatelets/NSAIDs. The median time from bleeding symptom and prolonged aPTT to diagnosis was 3.5 days (IQR 0-11.0) and 3.5 days (IQR 1.3-9.5), respectively. From first bleeding symptom, diagnosis was delayed ≥7 days in 15 (39%) patients and >30 days in 2 (5%). Case-based analysis identified the top reasons for delays ≥7 days: delayed ordering of aPTT from 7-62 days after bleeding (6/15; 40%), delayed ordering of mixing study following first abnormal aPTT from 7 days to >1 year (9/15; 60%) and attribution of bleeding to antiplatelets/anticoagulants (5/15; 33%). Neither demographic nor disease characteristics were identified as significant predictors of delayed diagnosis by logistic regression (Table 1). Initial presentation to HTCs had no impact on time to diagnosis. While non-statistically significant, there appears to be a clinically significant temporal gradient suggesting higher odds of diagnostic delays in 2010-2015 (OR 1.4) and 2016-2021 (OR 2.1) compared to pre-2010. Delayed diagnosis was not significantly associated with hospitalization rates, LOS, bypassing agent consumption, or units of packed red cells or plasma transfused. At a median follow-up of 3 years, 18 patients (47%) died at a median of 7 months (IQR 3-30). The most common causes of death included: infection (4), malignancy (3), bleeding (2), and thrombosis (2). Delayed diagnosis ≥7 days was associated with a non-significant trend towards worse 3-month OS (80% vs 91%) and 1-year OS (67% vs 87%, log-rank P=0.40; Figure 1). On Cox proportional hazards analysis, male sex (HR 4.0, 95% CI 1.5-10.5) and CCI 4-5 vs 0-3 (HR 7.0, 95% CI 1.5-32.3), but not delayed diagnosis (HR 1.5, 95% CI 0.6-3.9) were associated with increased hazard of death. Conclusion: In our large geographic catchment area, in the absence of an AHA reference centre, the median time to diagnosis (3.5 days) was markedly shorter than that reported in other single-centre studies (14-19 days), although delayed diagnosis ≥7 days was common. We did not identify statistically significant predictors of diagnostic delays, likely limited by small numbers. However, case-based analysis highlighted knowledge gaps as contributory factors, such as delayed ordering of aPTT in bleeding patients and delayed mixing study if aPTT is prolonged. Interestingly, time to diagnosis did not improve in recent years or with initial presentation to HTCs. Given the potential impact of delays on morbidity/mortality, further education is needed to expedite diagnosis in both HTCs and community settings.

Fetched live from OpenAlex and de-inverted. Abstracts are not stored in this database: the inverted indexes are 8.6 GB of the frame’s 9.3 GB of text, and the host has 13 GB free.

How this classification was reachedexpand

Full frame machine prediction

Teacher imitation

Not calibrated prevalence, not ground truth. Human validation pending. The Gemma side is a direct model label for every work in the frame, read from the title-only record. The Codex side is a classifier learned from the 10,348 direct Codex labels and calibrated to design-weighted sample rates; fields without enough sample support carry no Codex call. Candidate is the union of the two sides; consensus is their intersection. These outputs are machine_predicted_unvalidated and are not human labels.

metaresearch head score (Codex)0.000
metaresearch head score (Gemma)0.003
Version: metacan-v3-hybrid-931329e0061cValidation status: machine_predicted_unvalidated
Candidate categoriesnone
Consensus categoriesnone
DomainCandidate signal: none · Consensus signal: none
Study designCandidate signal: Observational · Consensus signal: Observational
GenreCandidate signal: Empirical · Consensus signal: Empirical
Teacher disagreement score0.261
Threshold uncertainty score0.518

Distilled classifier scores by category (both heads)

CategoryCodexGemma
Metaresearch0.0000.003
Meta-epidemiology (narrow)0.0000.000
Meta-epidemiology (broad)0.0000.000
Bibliometrics0.0010.001
Science and technology studies0.0000.000
Scholarly communication0.0010.000
Open science0.0000.000
Research integrity0.0000.000
Insufficient payload (model declined to judge)0.0020.000

Machine scores (provisional)

The two teacher heads of the student model, read on this work. A score orders the frame for review; it never asserts a category, and the validation status ships verbatim with every row.

Baseline scores from an immature model (maturity gate not passed, 7 training rounds). Scores rank; they never assert a category.

Opus teacher head0.026
GPT teacher head0.294
Teacher spread0.268 · how far apart the two teachers sit on this one work
Validation statusscore_only:v0-immature-baseline · verbatim from the scoring run: score_only means the number may rank works, and no category label ships from it

Classification

machine, unvalidated

Machine predicted; a candidate call from one source (direct Gemma or distilled Codex), not a consensus.

The models applied no category: nothing in the taxonomy fit this work.
Study designObservational
Domainnot available
GenreEmpirical

How this classification was reached, model by model and score by score, is at the end of the page under "How this classification was reached".

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Citations3
Published2023
Admission routes2
Has abstractyes

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