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Record W4391925503 · doi:10.1038/s41586-024-07019-6

Genetic drivers of heterogeneity in type 2 diabetes pathophysiology

2024· article· en· W4391925503 on OpenAlexafffund
Ken Suzuki, Konstantinos Hatzikotoulas, Lorraine Southam, Henry J. Taylor, Xianyong Yin, Kimberly Lorenz, Ravi Mandla, Alicia Huerta‐Chagoya, Giorgio Melloni, Stavroula Kanoni, Nigel W. Rayner, Ozvan Bocher, Ana Luiza Arruda, Kyuto Sonehara, Shinichi Namba, Simon Lee, Michael Preuß, Lauren E. Petty, Philip Schroeder, Brett Vanderwerff, Mart Kals, Fiona Bragg, Kuang Lin, Xiuqing Guo, Weihua Zhang, Jie Yao, Young Jin Kim, Mariaelisa Graff, Fumihiko Takeuchi, Jana Nano, Amel Lamri, Masahiro Nakatochi, Sanghoon Moon, Robert A. Scott, James P. Cook, Jung‐Jin Lee, Ian Pan, Daniel Taliun, Esteban J. Parra, Jin Fang Chai, Lawrence F. Bielak, Yasuharu Tabara, Yang Hai, Guðmar Þorleifsson, Niels Grarup, Tamar Sofer, Matthias Wuttke, Chloé Sarnowski, Christian Gieger, Darryl Nousome, Stella Trompet, Soo‐Heon Kwak, Jirong Long, Meng Sun, Tong Lin, Wei‐Min Chen, Suraj S. Nongmaithem, Raymond Noordam, Victor Lim, Claudia H.T. Tam, Yoonjung Yoonie Joo, Chien-Hsiun Chen, Laura M. Raffield, Bram P. Prins, Aude Nicolas, Lisa R. Yanek, Guanjie Chen, Jennifer A. Brody, Edmond K. Kabagambe, Ping An, Anny H. Xiang, Hyeok Sun Choi, Brian E. Cade, Jingyi Tan, K. Alaine Broadaway, Alice Williamson, Zoha Kamali, Jinrui Cui, Manonanthini Thangam, Linda S. Adair, Adebowale Adeyemo, Carlos A. Aguilar‐Salinas, Tarunveer S. Ahluwalia, Sonia S. Anand, Alain G. Bertoni, Jette Bork‐Jensen, Ivan Brandslund, Thomas A. Buchanan, Charles Burant, Adam S. Butterworth, Mickaël Canouil, Juliana C.N. Chan, Li-Ching Chang, Miao-Li Chee, Chen Ji, Shyh‐Huei Chen, Yuan‐Tsong Chen, Zhengming Chen, Lee‐Ming Chuang, Mary Cushman, John Danesh, Swapan K. Das, H. Janaka de Silva, George Dedoussis, Latchezar Dimitrov, Ayo P. Doumatey, Shufa Du, Qing Duan, Kai‐Uwe Eckardt, Leslie S. Emery, Daniel S. Evans, Michele K. Evans, Krista Fischer, James S. Floyd, Ian Ford, Oscar H. Franco, Timothy M. Frayling, Barry I. Freedman, Pauline Genter, Hertzel C. Gerstein, Vilmantas Giedraitis, Clicerio González‐Villalpando, María Elena González-Villalpando, Penny Gordon‐Larsen, Myron D. Gross, Lindsay Guare, Sophie Hackinger, Liisa Hakaste, Sohee Han, Andrew T. Hattersley, Christian Herder, Momoko Horikoshi, Annie-Green Howard, Willa A. Hsueh, Mengna Huang, Wei Huang, Yi‐Jen Hung, Mi Yeong Hwang, Chii‐Min Hwu, Sahoko Ichihara, M. Arfan Ikram, Martin Ingelsson, Md. Tariqul Islam, Masato Isono, Hye-Mi Jang, Farzana Jasmine, Guozhi Jiang, Jost B. Jonas, Torben Jørgensen, Frederick Kamanu, Fouad Kandeel, Anuradhani Kasturiratne, Tomohiro Katsuya, Varinderpal Kaur, Takahisa Kawaguchi, Jacob M. Keaton, Abel Kho, Chiea Chuen Khor, Muhammad G. Kibriya, Duk-Hwan Kim, Florian Kronenberg, Johanna Kuusisto, Kristi Läll, Leslie A. Lange, Kyung Min Lee, Myung‐Shik Lee, Nanette R. Lee, Aaron Leong, Liming Li, Yun Li, Ruifang Li‐Gao, Symen Ligthart, Cecilia M. Lindgren, Allan Linneberg, Ching‐Ti Liu, Jianjun Liu, Adam E. Locke, Tin Louie, Jian’an Luan, Andrea O. Y. Luk, Xi Luo, Jun Lv, Julie A. Lynch, Valeriya Lyssenko, Shiro Maeda, Vasiliki Mamakou, Sohail Rafik Mansuri, Koichi Matsuda, Thomas Meitinger, Olle Melander, Andres Metspalu, Huan Mo, Andrew D. Morris, Filipe A. Moura, Jerry L. Nadler, Uma Nayak, Ιωάννα Ντάλλα, Yukinori Okada, Lorena Orozco, Sanjay R. Patel, Snehal Patil, Pei Pei, Mark A. Pereira, Annette Peters, Fraser Pirie, Hannah G. Polikowsky, Bianca Porneala, Gauri Prasad, Laura J. Rasmussen‐Torvik, Alexander P. Reiner, Michael Roden, Rebecca Rohde, Katheryn Roll, Charumathi Sabanayagam, Kevin Sandow, Alagu Sankareswaran, Naveed Sattar, Sebastian Schönherr, Hasan Shahriar, Botong Shen, Jinxiu Shi, Dong Mun Shin, Nobuhiro Shojima, Jennifer A. Smith, Wing Yee So, Alena Stančáková, Valgerður Steinthórsdóttir, Adrienne M. Stilp, Konstantin Strauch, Kent D. Taylor, Barbara Thorand, Unnur Þorsteinsdóttir, Brian Tomlinson, Tam C. Tran, Fuu‐Jen Tsai, Jaakko Tuomilehto, Teresa Tusié‐Luna, Miriam S. Udler, Adán Valladares‐Salgado, Rob M. van Dam, Jan B. van Klinken, Rohit Varma, Niels Wacher-Rodarte, Eleanor Wheeler, Ananda R. Wickremasinghe, Ko Willems van Dijk, Daniel R. Witte, Chittaranjan S. Yajnik, Ken Yamamoto, Kenichi Yamamoto, Kyungheon Yoon, Canqing Yu, Jian‐Min Yuan, Salim Yusuf, Matthew Zawistowski, Liang Zhang, Wei Zheng, Stavroula Kanona, David A. van Heel, Leslie J. Raffel, Michiya Igase, Eli Ipp, Susan Redline, Yoon Shin Cho, Lars Lind, Michael A. Province, Myriam Fornage, Craig L. Hanis, Erik Ingelsson, Alan B. Zonderman, Bruce M. Psaty, Ya Xing Wang, Charles N. Rotimi, Diane M. Becker, Fumihiko Matsuda, Mitsuhiro Yokota, Sharon L.R. Kardia, Patricia A. Peyser, James S. Pankow, James C. Engert, Amélie Bonnefond, Philippe Froguel, James G. Wilson, Wayne Huey‐Herng Sheu, Jer‐Yuarn Wu, M. Geoffrey Hayes, C. W. Ronald, Tien Yin Wong, Dennis O. Mook‐Kanamori, Giriraj R. Chandak, Francis S. Collins, Dwaipayan Bharadwaj, Guillaume Paré, Michèle M. Sale, Habibul Ahsan, Ayesha A. Motala, Xiao‐Ou Shu, Kyong Soo Park, J. Wouter Jukema, Miguel Cruz, Yii‐Der Ida Chen, Stephen S. Rich, Roberta McKean‐Cowdin, Harald Grallert, Ching‐Yu Cheng, Mohsen Ghanbari, E Shyong Tai, Josée Dupuis, Norihiro Kato, Markku Laakso, Anna Köttgen, Woon‐Puay Koh, Donald W. Bowden, Jaspal S. Kooner, Charles Kooperberg, Simin Liu, Kari E. North, Danish Saleheen, Torben Hansen, Oluf Pedersen, Nicholas J. Wareham, Juyoung Lee, Bong-Jo Kim, Iona Y. Millwood, Robin Walters, Kāri Stefánsson, Emma Ahlqvist, Mark O. Goodarzi, Karen L. Mohlke, Claudia Langenberg, Christopher A. Haiman, Ruth J. F. Loos, José C. Florez, Daniel J. Rader, Marylyn D. Ritchie, Sebastian Zöllner, Reedik Mägi, Nicholas Marston, Christian T. Ruff, Sarah Finer, Joshua C. Denny, Toshimasa Yamauchi, Takashi Kadowaki, John C. Chambers, Maggie Ng, Xueling Sim, Jennifer E. Below, Philip S. Tsao, Kyong‐Mi Chang, Mark I. McCarthy, James B. Meigs, Anubha Mahajan, Cassandra N. Spracklen, Josep M. Mercader, Michael Boehnke, Jerome I. Rotter, Marijana Vujković, Benjamin F. Voight, Andrew P. Morris, Eleftheria Zeggini

Bibliographic record

VenueNature · 2024
Typearticle
Languageen
FieldBiochemistry, Genetics and Molecular Biology
TopicGenetic Associations and Epidemiology
Canadian institutionsMcGill UniversityImpactHamilton Health SciencesUniversity of TorontoMcMaster UniversityPopulation Health Research Institute
FundersJanssen Research and DevelopmentNational Institute of Environmental Health SciencesNational Institute of Diabetes and Digestive and Kidney DiseasesNational Human Genome Research InstituteNational Heart, Lung, and Blood InstituteNational Institute on AgingHelmholtz Zentrum MünchenRIKENRespicardiaManchester Biomedical Research CentrePerelman School of Medicine, University of PennsylvaniaSteno Diabetes Center AarhusNational Institutes of HealthRegeneron PharmaceuticalsVersus ArthritisMedical Research CouncilTartu ÜlikoolServierAmerican Heart AssociationNovo Nordisk FondenTechnische Universität MünchenGenentechQuest DiagnosticsAstraZenecaEuropean CommissionMcMaster UniversityUniversity of OxfordDepartment of Health and Social CareGuangdong Provincial People's HospitalBritish Heart FoundationZora BiosciencesIonis PharmaceuticalsCancer Research UKWellcome TrustARCA BiopharmaMedicines CompanyVanderbilt University Medical CenterHamilton Health SciencesUniversity of North Carolina at Chapel HillQueen Mary University of LondonHarvard UniversityNovo NordiskU.S. Department of Veterans AffairsUniversity of PennsylvaniaDaiichi-SankyoNanjing Medical UniversityVanderbilt UniversityYale UniversityMassachusetts General HospitalBrigham and Women's HospitalImperial College LondonEunice Kennedy Shriver National Institute of Child Health and Human DevelopmentU.S. Department of Health and Human ServicesAbiomedGlaxoSmithKlineEli Lilly and CompanyPfizerAmgenBroad InstituteSanofiNational Center for Global Health and MedicineNational Institute for Health and Care ResearchAmerican Diabetes AssociationKowa Company
KeywordsGenome-wide association studyType 2 diabetesBiologyGenetic associationGeneticsEpigenomicsDiseaseGenetic architectureGenetic genealogyGenetic heterogeneityCell typeEvolutionary biologyBioinformaticsQuantitative trait locusDiabetes mellitusMedicinePhenotypeInternal medicineSingle-nucleotide polymorphismGeneGenotypeEndocrinologyCellDNA methylationPopulation

Abstract

fetched live from OpenAlex

Abstract Type 2 diabetes (T2D) is a heterogeneous disease that develops through diverse pathophysiological processes 1,2 and molecular mechanisms that are often specific to cell type 3,4 . Here, to characterize the genetic contribution to these processes across ancestry groups, we aggregate genome-wide association study data from 2,535,601 individuals (39.7% not of European ancestry), including 428,452 cases of T2D. We identify 1,289 independent association signals at genome-wide significance ( P < 5 × 10 −8 ) that map to 611 loci, of which 145 loci are, to our knowledge, previously unreported. We define eight non-overlapping clusters of T2D signals that are characterized by distinct profiles of cardiometabolic trait associations. These clusters are differentially enriched for cell-type-specific regions of open chromatin, including pancreatic islets, adipocytes, endothelial cells and enteroendocrine cells. We build cluster-specific partitioned polygenic scores 5 in a further 279,552 individuals of diverse ancestry, including 30,288 cases of T2D, and test their association with T2D-related vascular outcomes. Cluster-specific partitioned polygenic scores are associated with coronary artery disease, peripheral artery disease and end-stage diabetic nephropathy across ancestry groups, highlighting the importance of obesity-related processes in the development of vascular outcomes. Our findings show the value of integrating multi-ancestry genome-wide association study data with single-cell epigenomics to disentangle the aetiological heterogeneity that drives the development and progression of T2D. This might offer a route to optimize global access to genetically informed diabetes care.

Fetched live from OpenAlex and de-inverted. Abstracts are not stored in this database: the inverted indexes are 8.6 GB of the frame’s 9.3 GB of text, and the host has 13 GB free.

How this classification was reachedexpand

Full frame distilled prediction

Teacher imitation

Not calibrated prevalence, not ground truth. Human validation pending. Learned from the 10,348 direct Codex labels and 10,348 direct Gemma labels. Candidate is the union of thresholded teacher heads; consensus is their intersection. These outputs are machine_predicted_unvalidated and are not human labels or direct frontier model labels.

metaresearch head score (Codex)0.000
metaresearch head score (Gemma)0.000
Version: codex-gemma-dda1882f352aValidation status: machine_predicted_unvalidated
Candidate categoriesnone
Consensus categoriesnone
DomainCandidate signal: none · Consensus signal: none
Study designCandidate signal: Observational · Consensus signal: none
GenreCandidate signal: Empirical · Consensus signal: Empirical
Teacher disagreement score0.724
Threshold uncertainty score0.679

Codex and Gemma teacher scores by category

CategoryCodexGemma
Metaresearch0.0000.000
Meta-epidemiology (narrow)0.0000.000
Meta-epidemiology (broad)0.0000.000
Bibliometrics0.0000.000
Science and technology studies0.0000.000
Scholarly communication0.0000.000
Open science0.0000.000
Research integrity0.0010.000
Insufficient payload (model declined to judge)0.0000.000

Machine scores (provisional)

The two teacher heads of the student model, read on this work. A score orders the frame for review; it never asserts a category, and the validation status ships verbatim with every row.

Baseline scores from an immature model (maturity gate not passed, 7 training rounds). Scores rank; they never assert a category.

Opus teacher head0.005
GPT teacher head0.258
Teacher spread0.253 · how far apart the two teachers sit on this one work
Validation statusscore_only:v0-immature-baseline · verbatim from the scoring run: score_only means the number may rank works, and no category label ships from it

Classification

machine, unvalidated

Machine predicted; a candidate call from one teacher head, not a consensus.

The models applied no category: nothing in the taxonomy fit this work.
Study designObservational
Domainnot available
GenreEmpirical

How this classification was reached, model by model and score by score, is at the end of the page under "How this classification was reached".

Quick stats

Citations513
Published2024
Admission routes2
Has abstractyes

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