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Uso de glucocorticoides en pacientes con distrofia muscular de Duchenne

2025· article· es· W4409659370 on OpenAlexaff
Edna Julieth Bobadilla-Quesada, Juan David Lasprilla Tovar, Norma Carolina Barajas Viracachá, Paulo César Becerra Ortiz, Carlos Ernesto Bolaños Almeida, José Manuel Cañón Zambrano, Sandra Milena Castellar-Leones, Manuel Huertas Quiñones, Isabel Londoño Ossa, Blair Ortiz, Fernando Ortiz‐Corredor, Sandra Yaneth Ospina Lagos, Juan Carlos Prieto, Carolina Rivera‐Nieto, Edicson Ruiz Ospina, Felipe Ruiz-Botero, Maria Salcedo-Maldonado, Diana Pilar Soto Peña, Fernando Suárez‐Obando, Lina Marcela Tavera-Saldaña, María Julia Torres-Nieto, Diana Carolina Sánchez-Peñarete

Bibliographic record

VenueRevista Ciencias de la Salud · 2025
Typearticle
Languagees
FieldBiochemistry, Genetics and Molecular Biology
TopicMuscle Physiology and Disorders
Canadian institutionsMisericordia Community Hospital
Fundersnot available
KeywordsMedicine

Abstract

fetched live from OpenAlex

La distrofia muscular de Duchenne es una condición severa y debilitante que lleva a dificultades en la marcha, el movimiento y eventualmente a la necesidad de ventilación mecánica y a la muerte prematura. Sin embargo, su historia natural ha evolucionado de la mano con la aparición de nuevas intervenciones que han demostrado tener un efecto positivo en la enfermedad. La terapia farmacológica con glucocorticoides es uno de los estándares de cuidado en pacientes con distrofia muscular de Duchenne, cuyos efectos están relacionados con la prolongación del tiempo de pérdida de marcha, una menor disminución en el puntaje de las pruebas funcionales y la preservación de la función mano-boca y de la función de la mano para el agarre de objetos. El beneficio del uso de glucocorticoides está establecido en pacientes con deambulación y sin la misma, al tener un impacto en la función pulmonar. Sin embargo, es importante tener claros los efectos secundarios derivados del tratamiento. El presente documento busca proveer una síntesis sobre el uso adecuado de los glucocorticoides y el seguimiento de la terapia en pacientes con distrofia muscular de Duchenne.

Fetched live from OpenAlex and de-inverted. Abstracts are not stored in this database: the inverted indexes are 8.6 GB of the frame’s 9.3 GB of text, and the host has 13 GB free.

How this classification was reachedexpand

Full frame machine prediction

Teacher imitation

Not calibrated prevalence, not ground truth. Human validation pending. The Gemma side is a direct model label for every work in the frame, read from the title-only record. The Codex side is a classifier learned from the 10,348 direct Codex labels and calibrated to design-weighted sample rates; fields without enough sample support carry no Codex call. Candidate is the union of the two sides; consensus is their intersection. These outputs are machine_predicted_unvalidated and are not human labels.

metaresearch head score (Codex)0.000
metaresearch head score (Gemma)0.002
Version: metacan-v3-hybrid-931329e0061cValidation status: machine_predicted_unvalidated
Candidate categoriesnone
Consensus categoriesnone
DomainCandidate signal: none · Consensus signal: none
Study designCandidate signal: Observational · Consensus signal: Observational
GenreCandidate signal: Empirical · Consensus signal: Empirical
Teacher disagreement score0.005
Threshold uncertainty score0.011

Distilled classifier scores by category (both heads)

CategoryCodexGemma
Metaresearch0.0000.002
Meta-epidemiology (narrow)0.0000.000
Meta-epidemiology (broad)0.0010.000
Bibliometrics0.0000.001
Science and technology studies0.0000.000
Scholarly communication0.0010.000
Open science0.0000.000
Research integrity0.0000.001
Insufficient payload (model declined to judge)0.0010.000

Machine scores (provisional)

The two teacher heads of the student model, read on this work. A score orders the frame for review; it never asserts a category, and the validation status ships verbatim with every row.

Baseline scores from an immature model (maturity gate not passed, 7 training rounds). Scores rank; they never assert a category.

Opus teacher head0.003
GPT teacher head0.272
Teacher spread0.269 · how far apart the two teachers sit on this one work
Validation statusscore_only:v0-immature-baseline · verbatim from the scoring run: score_only means the number may rank works, and no category label ships from it

Classification

machine, unvalidated

Machine predicted; a candidate call from one source (direct Gemma or distilled Codex), not a consensus.

The models applied no category: nothing in the taxonomy fit this work.
Study designObservational
Domainnot available
GenreEmpirical

How this classification was reached, model by model and score by score, is at the end of the page under "How this classification was reached".

Quick stats

Citations0
Published2025
Admission routes1
Has abstractyes

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