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Record W4414978444 · doi:10.1038/s41591-025-03986-z

Feasibility, acceptability and clinical outcomes of the BabyScreen+ genomic newborn screening study

2025· article· en· W4414978444 on OpenAlexaff
Sebastian Lunke, Lilian Downie, Jade Caruana, Nathasha Kugenthiran, Paul De Fazio, Sebastian Hollizeck, Sophie E. Bouffler, David J. Amor, Alison D. Archibald, Yvonne Bombard, John Christodoulou, Marc Clausen, Wendy Fagan, Clara Gaff, Ronda F. Greaves, Christopher Gyngell, Anaita Kanga‐Parabia, Nitzan Lang, Crystle Lee, Fiona Lynch, Anthony Marty, Melanie A. Marty, Candice McGregor, Jessica R. Riseley, Simon Sadedin, Katrina L. Scarff, Erin Tutty, Ching Vang, Meaghan Wall, Ee Ming Wong, Alison Yeung, Ilias Goranitis, Stephanie Best, Danya F. Vears, Zornitza Stark

Bibliographic record

VenueNature Medicine · 2025
Typearticle
Languageen
FieldBiochemistry, Genetics and Molecular Biology
TopicGenomics and Rare Diseases
Canadian institutionsOntario GenomicsUniversity of Toronto
FundersNational Health and Medical Research CouncilMedical Research CouncilState Government of VictoriaAustralian GovernmentChildren's Hospital Foundation
KeywordsNewborn screeningGenomic medicineGenomic sequencingRegretInterquartile rangeCohortProspective cohort studyPersonalized medicine

Abstract

fetched live from OpenAlex

Incorporating genomic sequencing into newborn screening will dramatically increase the number of detectable conditions but evidence is needed to guide policy. The prospective BabyScreen+ cohort study screened 1,000 newborns from the state of Victoria, Australia for variants in 605 genes associated with early-onset, severe, treatable conditions using whole-genome sequencing performed on dried blood spot cards. Sixteen infants (1.6%) were identified as having high-chance results. Of these, only one was detected by standard newborn screening. Average time to genomic newborn result was 13 days. Clinical impact ranged from instituting preventative measures or surveillance to active management, including transplantation. Twenty relatives received a diagnosis following cascade testing. Median parental decisional regret was low (median 0, interquartile range 0-10); >99% of participants thought genomic newborn screening should be available to all parents. Our study demonstrates the feasibility of clinically accredited genomic newborn screening, using a scalable model that is highly acceptable to parents. Future research is needed to address issues of scalability and equity.

Fetched live from OpenAlex and de-inverted. Abstracts are not stored in this database: the inverted indexes are 8.6 GB of the frame’s 9.3 GB of text, and the host has 13 GB free.

How this classification was reachedexpand

Full frame machine prediction

Teacher imitation

Not calibrated prevalence, not ground truth. Human validation pending. The Gemma side is a direct model label for every work in the frame, read from the title-only record. The Codex side is a classifier learned from the 10,348 direct Codex labels and calibrated to design-weighted sample rates; fields without enough sample support carry no Codex call. Candidate is the union of the two sides; consensus is their intersection. These outputs are machine_predicted_unvalidated and are not human labels.

metaresearch head score (Codex)0.070
metaresearch head score (Gemma)0.113
Version: metacan-v3-hybrid-931329e0061cValidation status: machine_predicted_unvalidated
Candidate categoriesnone
Consensus categoriesnone
DomainCandidate signal: none · Consensus signal: none
Study designCandidate signal: Observational · Consensus signal: Observational
GenreCandidate signal: Empirical · Consensus signal: Empirical
Teacher disagreement score0.070
Threshold uncertainty score0.373

Distilled classifier scores by category (both heads)

CategoryCodexGemma
Metaresearch0.0700.113
Meta-epidemiology (narrow)0.0000.000
Meta-epidemiology (broad)0.0000.001
Bibliometrics0.0010.001
Science and technology studies0.0010.001
Scholarly communication0.0020.001
Open science0.0010.003
Research integrity0.0010.001
Insufficient payload (model declined to judge)0.0030.001

Machine scores (provisional)

The two teacher heads of the student model, read on this work. A score orders the frame for review; it never asserts a category, and the validation status ships verbatim with every row.

Baseline scores from an immature model (maturity gate not passed, 7 training rounds). Scores rank; they never assert a category.

Opus teacher head0.016
GPT teacher head0.364
Teacher spread0.348 · how far apart the two teachers sit on this one work
Validation statusscore_only:v0-immature-baseline · verbatim from the scoring run: score_only means the number may rank works, and no category label ships from it

Classification

machine, unvalidated

Machine predicted; a candidate call from one source (direct Gemma or distilled Codex), not a consensus.

The models applied no category: nothing in the taxonomy fit this work.
Study designObservational
Domainnot available
GenreEmpirical

How this classification was reached, model by model and score by score, is at the end of the page under "How this classification was reached".

Quick stats

Citations16
Published2025
Admission routes1
Has abstractyes

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