MétaCan
Menu
Back to cohort
Record W3081055933 · doi:10.1002/ajmg.a.61799

Missense variants in the spectrin repeat domain of <scp><i>DSP</i></scp> are associated with arrhythmogenic cardiomyopathy: A family report and systematic review

2020· review· en· W3081055933 on OpenAlexafffund
Steffany Grondin, Avedis‐Christ Wazirian, Paloma Jordà, Donato Terrone, Johannie Gagnon, Laura Robb, Julie Amyot, Léna Rivard, Sylvain Pagé, Mario Talajic, Julia Cadrin‐Tourigny, Rafik Tadros

Bibliographic record

VenueAmerican Journal of Medical Genetics Part A · 2020
Typereview
Languageen
FieldMedicine
TopicCardiovascular Effects of Exercise
Canadian institutionsInstitut universitaire de cardiologie et de pneumologie de QuébecUniversité de MontréalMontreal Heart Institute
FundersFonds de Recherche du Québec - SantéCanadian Institutes of Health ResearchSociedad Española de Cardiología
KeywordsMissense mutationDesmoplakinCardiomyopathyDilated cardiomyopathyMedicineInternal medicinePhenotypeCardiologyGeneticsHeart failureBiologyGene

Abstract

fetched live from OpenAlex

Rare loss of function variants in DSP, which codes for the desmosomal protein desmoplakin, have been implicated in dilated and arrhythmogenic right ventricular cardiomyopathies. We present a family with arrhythmogenic cardiomyopathy associated with a novel missense variant in DSP (NM_004415.4): c.877G>A, p.(Glu293Lys). The phenotype is characterized by predominant involvement of the left ventricle with systolic dysfunction, fibrosis, and life-threatening arrhythmias. We performed a systematic review of literature collecting all cardiomyopathy cases with rare missense variants in DSP. We demonstrate that the distribution of missense variants across the protein domains in cardiomyopathy cases differs from that in gnomAD (p = .04), with a case enrichment of rare missense variants in the spectrin repeat domain (36/78 [46%] in cases vs. 449/1495 [30%] in gnomAD; p = .004). Our findings highlight the predominance of cardiac arrhythmia and left ventricular involvement in desmoplakin cardiomyopathy and pinpoint to a potential mutation hotspot in DSP thereby facilitating missense variant interpretation in the diagnostic setting.

Fetched live from OpenAlex and de-inverted. Abstracts are not stored in this database: the inverted indexes are 8.6 GB of the frame’s 9.3 GB of text, and the host has 13 GB free.

How this classification was reachedexpand

Full frame distilled prediction

Teacher imitation

Not calibrated prevalence, not ground truth. Human validation pending. Learned from the 10,348 direct Codex labels and 10,348 direct Gemma labels. Candidate is the union of thresholded teacher heads; consensus is their intersection. These outputs are machine_predicted_unvalidated and are not human labels or direct frontier model labels.

metaresearch head score (Codex)0.011
metaresearch head score (Gemma)0.016
Version: codex-gemma-dda1882f352aValidation status: machine_predicted_unvalidated
Candidate categoriesMetaresearch, Meta-epidemiology (narrow)
Consensus categoriesnone
DomainCandidate signal: none · Consensus signal: none
Study designCandidate signal: Systematic review · Consensus signal: Systematic review
GenreCandidate signal: Review · Consensus signal: Review
Teacher disagreement score0.128
Threshold uncertainty score1.000

Codex and Gemma teacher scores by category

CategoryCodexGemma
Metaresearch0.0110.016
Meta-epidemiology (narrow)0.0010.000
Meta-epidemiology (broad)0.0110.002
Bibliometrics0.0000.002
Science and technology studies0.0000.001
Scholarly communication0.0000.000
Open science0.0010.000
Research integrity0.0000.002
Insufficient payload (model declined to judge)0.0000.000

Machine scores (provisional)

The two teacher heads of the student model, read on this work. A score orders the frame for review; it never asserts a category, and the validation status ships verbatim with every row.

Baseline scores from an immature model (maturity gate not passed, 7 training rounds). Scores rank; they never assert a category.

Opus teacher head0.017
GPT teacher head0.289
Teacher spread0.272 · how far apart the two teachers sit on this one work
Validation statusscore_only:v0-immature-baseline · verbatim from the scoring run: score_only means the number may rank works, and no category label ships from it

Classification

machine, unvalidated

Machine predicted; a candidate call from one teacher head, not a consensus.

Study designSystematic review
Domainnot available
GenreReview

How this classification was reached, model by model and score by score, is at the end of the page under "How this classification was reached".

Quick stats

Citations7
Published2020
Admission routes2
Has abstractyes

Explore more

Same venueAmerican Journal of Medical Genetics Part ASame topicCardiovascular Effects of ExerciseFrench-language works237,207