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Record W4403909425 · doi:10.1002/bimj.70002

Estimating the Sampling Distribution of Posterior Decision Summaries in Bayesian Clinical Trials

2024· article· en· W4403909425 on OpenAlex
Shirin Golchi, James J. Willard

Why this work is in the frame

A frame that forgets how it found something cannot be audited. These are the routes that admitted this work.

affAt least one author lists a Canadian institution in the pinned OpenAlex snapshot.
fundA Canadian funder is recorded on the work.

Bibliographic record

VenueBiometrical Journal · 2024
Typearticle
Languageen
FieldMathematics
TopicStatistical Methods in Clinical Trials
Canadian institutionsMcGill University
FundersFonds de recherche du Québec – Nature et technologiesFonds de Recherche du Québec - SantéNatural Sciences and Engineering Research Council of Canada
KeywordsFrequentist inferencePosterior probabilitySample size determinationComputer scienceBayesian probabilityPosterior predictive distributionPrior probabilitySampling (signal processing)Bayesian linear regressionStatisticsBayes factorEconometricsBayesian hierarchical modelingParametric statisticsBayesian inferenceCategorical distributionMachine learningArtificial intelligenceMathematics

Abstract

fetched live from OpenAlex

Bayesian inference and the use of posterior or posterior predictive probabilities for decision making have become increasingly popular in clinical trials. The current practice in Bayesian clinical trials relies on a hybrid Bayesian-frequentist approach where the design and decision criteria are assessed with respect to frequentist operating characteristics such as power and type I error rate conditioning on a given set of parameters. These operating characteristics are commonly obtained via simulation studies. The utility of Bayesian measures, such as "assurance," that incorporate uncertainty about model parameters in estimating the probabilities of various decisions in trials has been demonstrated. However, the computational burden remains an obstacle toward wider use of such criteria. In this article, we propose methodology which utilizes large sample theory of the posterior distribution to define parametric models for the sampling distribution of the posterior summaries used for decision making. The parameters of these models are estimated using a small number of simulation scenarios, thereby refining these models to capture the sampling distribution for small to moderate sample size. The proposed approach toward the assessment of conditional and marginal operating characteristics and sample size determination can be considered as simulation-assisted rather than simulation-based. It enables formal incorporation of uncertainty about the trial assumptions via a design prior and significantly reduces the computational burden for the design of Bayesian trials in general.

Fetched live from OpenAlex and de-inverted. Abstracts are not stored in this database: the inverted indexes are 8.6 GB of the frame’s 9.3 GB of text, and the host has 13 GB free.

Full frame distilled prediction

Teacher imitation

Not calibrated prevalence, not ground truth. Human validation pending. Learned from the 10,348 direct Codex labels and 10,348 direct Gemma labels. Candidate is the union of thresholded teacher heads; consensus is their intersection. These outputs are machine_predicted_unvalidated and are not human labels or direct frontier model labels.

metaresearch head score (Codex)0.078
metaresearch head score (Gemma)0.737
Version: codex-gemma-dda1882f352aValidation status: machine_predicted_unvalidated
Candidate categoriesMetaresearch
Consensus categoriesMetaresearch
DomainCandidate signal: none · Consensus signal: none
Study designCandidate signal: Theoretical or conceptual · Consensus signal: none
GenreCandidate signal: Methods · Consensus signal: Methods
Teacher disagreement score0.981
Threshold uncertainty score0.949

Codex and Gemma teacher scores by category

CategoryCodexGemma
Metaresearch0.0780.737
Meta-epidemiology (narrow)0.0000.000
Meta-epidemiology (broad)0.0010.001
Bibliometrics0.0010.003
Science and technology studies0.0000.000
Scholarly communication0.0000.000
Open science0.0000.000
Research integrity0.0000.001
Insufficient payload (model declined to judge)0.0000.000

Machine scores (provisional)

The two teacher heads of the student model, read on this work. A score orders the frame for review; it never asserts a category, and the validation status ships verbatim with every row.

Baseline scores from an immature model (maturity gate not passed, 7 training rounds). Scores rank; they never assert a category.

Opus teacher head0.764
GPT teacher head0.669
Teacher spread0.095 · how far apart the two teachers sit on this one work
Validation statusscore_only:v0-immature-baseline · verbatim from the scoring run: score_only means the number may rank works, and no category label ships from it