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Record W4411779851 · doi:10.1038/s41375-025-02667-7

Disease-specific U1 spliceosomal RNA mutations in mature B-cell neoplasms

2025· article· en· W4411779851 on OpenAlexaff
Ferran Nadeu, Shimin Shuai, Guillem Clot, Laura K. Hilton, Ander Díaz‐Navarro, Silvia Martín, Romina Royo, Tycho Baumann, Marta Kulis, Irene López‐Oreja, Manuel Cossio, Junyan Lu, Viktor Ljungström, Emma Young, Karla Plevová, Binyamin A. Knisbacher, Ziao Lin, Cynthia K. Hahn, Pablo Bousquets‐Muñoz, Miguel Alcoceba, Marcos González, Enrique Colado, Ángel Ramírez Páyer, Marta Aymerich, María José Terol, Alfredo Rivas‐Delgado, Anna Enjuanes, Sílvia Ruiz-Gaspà, Thomas Chatzikonstantinou, Daniel Hägerstrand, Cecilia Jylhä, Aron Skaftason, Larry Mansouri, Kamila Stránská, Michael Doubek, Ellen J. van Gastel-Mol, Zadie Davis, Renata Walewska, Lydia Scarfò, Livio Trentin, Andrea Visentin, Sameer A. Parikh, Kari G. Rabe, Riccardo Moia, Marine Armand, Davide Rossi, Frédéric Davi, Gianluca Gaïdano, Neil E. Kay, Tait D. Shanafelt, Paolo Ghia, David Oscier, Anton W. Langerak, Sı́lvia Beà, Armando López‐Guillermo, Donna Neuberg, Catherine J. Wu, Gad Getz, Šárka Pospı́šilová, Κώστας Σταματόπουλος, Richard Rosenquist, Wolfgang Huber, Thorsten Zenz, Dolors Colomer, José I. Martín‐Subero, Julio Delgado, Ryan D. Morin, Lincoln Stein, Xosé S. Puente, Elı́as Campo

Bibliographic record

VenueLeukemia · 2025
Typearticle
Languageen
FieldMedicine
TopicChronic Lymphocytic Leukemia Research
Canadian institutionsUniversity of TorontoOntario Institute for Cancer ResearchCanada's Michael Smith Genome Sciences CentreSimon Fraser University
FundersAgencia Estatal de InvestigaciónEuropean Regional Development FundAstraZenecaAgència de Gestió d'Ajuts Universitaris i de RecercaFundación Bancaria Caixa d'Estalvis i Pensions de BarcelonaEusko JaurlaritzaAssociazione Italiana per la Ricerca sul CancroNational Cancer InstituteKnut och Alice Wallenbergs StiftelseSouthern University of Science and TechnologyScience for Life LaboratoryNational Natural Science Foundation of ChinaVetenskapsrådetKarolinska InstitutetInstitució Catalana de Recerca i Estudis AvançatsEuropean CommissionMinisterio de Ciencia e InnovaciónMinisterstvo Zdravotnictví Ceské RepublikyFundación Española de Hematología y HemoterapiaGeneralitat de CatalunyaRadiumhemmets ForskningsfonderCancerfondenEuropean Hematology AssociationAmgenAmerican Association for Cancer ResearchCentres de Recerca de Catalunya
KeywordsBiologyRNADiseaseGeneticsMutationGeneMedicinePathology

Abstract

fetched live from OpenAlex

Recurrent mutations in the third base of U1 spliceosomal RNA responsible for marked splicing and expression abnormalities have been described in chronic lymphocytic leukemia (CLL) and some solid tumors. However, the clinical significance of these mutations in large and independent CLL cohorts as well as their presence in other B-cell neoplasms is unknown. Here we characterized U1 mutations in 1670 CLL and 363 mature B-cell lymphomas. We confirmed that the g.3A>C U1 mutation is found in 3.5% of CLL, which conferred rapid disease progression independently of the main biological and clinical prognostic markers of the disease. Additionally, a recurrent g.9C>T mutation was found in 1.5% of CLL causing downstream splicing alterations and associated with adverse prognosis. We also identified a g.4C>T mutation in 10% of diffuse large B-cell lymphomas of the germinal center subtype and a g.7A>G mutation in 30% of EBV-negative Burkitt lymphomas, both of which altered the splicing pattern of multiple genes. This study reveals novel, recurrent, and tumor-specific U1 mutations in mature B-cell neoplasms with biological and prognostic implications, thus establishing U1 as a novel pan-B-cell malignancy driver gene.

Fetched live from OpenAlex and de-inverted. Abstracts are not stored in this database: the inverted indexes are 8.6 GB of the frame’s 9.3 GB of text, and the host has 13 GB free.

How this classification was reachedexpand

Full frame machine prediction

Teacher imitation

Not calibrated prevalence, not ground truth. Human validation pending. The Gemma side is a direct model label for every work in the frame, read from the title-only record. The Codex side is a classifier learned from the 10,348 direct Codex labels and calibrated to design-weighted sample rates; fields without enough sample support carry no Codex call. Candidate is the union of the two sides; consensus is their intersection. These outputs are machine_predicted_unvalidated and are not human labels.

metaresearch head score (Codex)0.000
metaresearch head score (Gemma)0.000
Version: metacan-v3-hybrid-931329e0061cValidation status: machine_predicted_unvalidated
Candidate categoriesnone
Consensus categoriesnone
DomainCandidate signal: none · Consensus signal: none
Study designCandidate signal: Observational · Consensus signal: none
GenreCandidate signal: Empirical · Consensus signal: Empirical
Teacher disagreement score0.001
Threshold uncertainty score0.002

Distilled classifier scores by category (both heads)

CategoryCodexGemma
Metaresearch0.0000.000
Meta-epidemiology (narrow)0.0000.000
Meta-epidemiology (broad)0.0000.000
Bibliometrics0.0010.000
Science and technology studies0.0000.000
Scholarly communication0.0000.000
Open science0.0000.000
Research integrity0.0000.000
Insufficient payload (model declined to judge)0.0010.000

Machine scores (provisional)

The two teacher heads of the student model, read on this work. A score orders the frame for review; it never asserts a category, and the validation status ships verbatim with every row.

Baseline scores from an immature model (maturity gate not passed, 7 training rounds). Scores rank; they never assert a category.

Opus teacher head0.015
GPT teacher head0.282
Teacher spread0.267 · how far apart the two teachers sit on this one work
Validation statusscore_only:v0-immature-baseline · verbatim from the scoring run: score_only means the number may rank works, and no category label ships from it

Classification

machine, unvalidated

Machine predicted; a candidate call from one source (direct Gemma or distilled Codex), not a consensus.

The models applied no category: nothing in the taxonomy fit this work.
Study designObservational
Domainnot available
GenreEmpirical

How this classification was reached, model by model and score by score, is at the end of the page under "How this classification was reached".

Quick stats

Citations2
Published2025
Admission routes1
Has abstractyes

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