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Record W7117318193 · doi:10.1080/23995270.2025.2607961

The plight of rare diseases in Southern Africa: health and social services policy recommendations

2025· article· en· W7117318193 on OpenAlexaff
Aneth David, Mohamed Zahir Alimohamed, Grantina Modern, Sharifa Mbarak, Husna Mad-hy, B. Ozcan, Nomsa Mtshali, Hlumela Tshijila, Kelly du Plessis, Eda Selebatso, Matshediso Letsholo, Nthabeleng Ramoeli, Trudy Nyakambangwe, Reon Van Der Merwe, Vivian Joseph, Farhan Yusuf, Maximilian Godwin Kilipamwambu, Kilaza Samson Mwaikono, Siana Nkya

Bibliographic record

VenueFuture Rare Diseases · 2025
Typearticle
Languageen
FieldBiochemistry, Genetics and Molecular Biology
TopicGenomics and Rare Diseases
Canadian institutionsAga Khan Foundation
Fundersnot available
KeywordsSocial WelfareHealth servicesSocial policyGovernment (linguistics)Health policyPublic health

Abstract

fetched live from OpenAlex

Rare diseases impact approximately 300 million people globally, yet they receive minimal attention compared to infectious and non-communicable diseases. There are over 10,000 known rare diseases, most of which being hereditary and primarily affecting children. In sub-Saharan Africa (SSA), weak public health infrastructure exacerbates the challenges of diagnosis, management, and treatment of rare diseases. Further, the absence of a definition of rare diseases in the region and the lack of and/or unclear policy frameworks to manage the conditions further slow down the progress toward realization of universal healthcare and the Sustainable Development Goals. We propose harmonized policy recommendations for tackling rare diseases across the Southern African Development Community (SADC). These include establishing a common definition, centralizing healthcare services, promoting preventive measures, enhancing collaborative research and building healthcare workers’ capacity. We also recommend the adoption of shared cost models and specialized health insurance to ensure access to necessary services for those living with rare diseases. This is a starting point to discuss policy issues on healthcare and social services necessary for improving the quality of life of people living with rare diseases (PLRDs) in SSA. Harmonization will also promote effective utilization of resources for both research and care of rare diseases.

Fetched live from OpenAlex and de-inverted. Abstracts are not stored in this database: the inverted indexes are 8.6 GB of the frame’s 9.3 GB of text, and the host has 13 GB free.

How this classification was reachedexpand

Full frame machine prediction

Teacher imitation

Not calibrated prevalence, not ground truth. Human validation pending. The Gemma side is a direct model label for every work in the frame, read from the title-only record. The Codex side is a classifier learned from the 10,348 direct Codex labels and calibrated to design-weighted sample rates; fields without enough sample support carry no Codex call. Candidate is the union of the two sides; consensus is their intersection. These outputs are machine_predicted_unvalidated and are not human labels.

metaresearch head score (Codex)0.017
metaresearch head score (Gemma)0.038
Version: metacan-v3-hybrid-931329e0061cValidation status: machine_predicted_unvalidated
Candidate categoriesnone
Consensus categoriesnone
DomainCandidate signal: none · Consensus signal: none
Study designCandidate signal: Theoretical or conceptual · Consensus signal: none
GenreCandidate signal: Review · Consensus signal: none
Teacher disagreement score0.077
Threshold uncertainty score0.153

Distilled classifier scores by category (both heads)

CategoryCodexGemma
Metaresearch0.0170.038
Meta-epidemiology (narrow)0.0020.001
Meta-epidemiology (broad)0.0010.003
Bibliometrics0.0030.002
Science and technology studies0.0040.003
Scholarly communication0.0080.008
Open science0.0030.009
Research integrity0.0240.013
Insufficient payload (model declined to judge)0.0340.004

Machine scores (provisional)

The two teacher heads of the student model, read on this work. A score orders the frame for review; it never asserts a category, and the validation status ships verbatim with every row.

Baseline scores from an immature model (maturity gate not passed, 7 training rounds). Scores rank; they never assert a category.

Opus teacher head0.005
GPT teacher head0.256
Teacher spread0.251 · how far apart the two teachers sit on this one work
Validation statusscore_only:v0-immature-baseline · verbatim from the scoring run: score_only means the number may rank works, and no category label ships from it

Classification

machine, unvalidated

Machine predicted; a candidate call from one source (direct Gemma or distilled Codex), not a consensus.

The models applied no category: nothing in the taxonomy fit this work.
Study designTheoretical or conceptual
Domainnot available
GenreReview

How this classification was reached, model by model and score by score, is at the end of the page under "How this classification was reached".

Quick stats

Citations0
Published2025
Admission routes1
Has abstractyes

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