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Interim data from a long-term safety, tolerability, and efficacy study of liposomal amikacin for inhalation in cystic fibrosis patients with chronic <i>pseudomonas aeruginosa</i> infection

2014· article· en· W7140030509 on OpenAlexaboutno aff
Diana Bilton, Tacjana Pressler, Isabelle Fajac, John Clancy, Dorota Sands, Predrag Minić, Marco Cipolli, Mario La Rosa, Ivanka Galeva, Amparó Solé, Nicole Mayer-Hamblett, Scott Constantine, Michael W. Konstan

Bibliographic record

VenueEuropean Respiratory Journal · 2014
Typearticle
Languageen
FieldMedicine
TopicInhalation and Respiratory Drug Delivery
Canadian institutionsnot available
Fundersnot available
KeywordsInhalationCystic fibrosisAdverse effectInterim analysisPopulationInterim

Abstract

fetched live from OpenAlex

Rationale: Liposomal amikacin for inhalation (LAI) is a novel lipid formulation being developed to treat chronic Pseudomonas aeruginosa (Pa) infection in cystic fibrosis (CF) patients (pts). CLEAR-110 is an extension study of a completed LAI versus tobramycin inhalation solution comparator study (CLEAR-108) to evaluate long-term safety, tolerability, and efficacy of once-daily (QD) LAI. Methods : The study was conducted in 54 centers in 16 countries in Europe and Canada. Eligible pts from CLEAR-108 received LAI 590 mg QD via a PARI Investigational eFlow ® Nebulizer System (28 days on/off treatment) for 6 cycles (12 months) and could re-consent for additional 6 cycles (12 total [∼2 yrs]). Patients were evaluated every 28 days. Results: A total of 266 pts completed CLEAR-108; 206 (77%) enrolled in CLEAR-110 and received ≥1 dose of LAI. At the time of the interim data, 98 pts had completed 6 cycles of treatment. Overall, data show that LAI was well tolerated, and no unexpected adverse events (AEs) were observed. At the end of treatment of cycle 6, mean % increase from baseline in forced expiratory volume in 1 second (FEV1 [L]) was 3.65 % and 0.78% at the end of off-treatment period of the 6th cycle. Conclusion: These interim data demonstrate that LAI was well tolerated during 6 cycles, with AEs being consistent with those expected in a population of CF patients receiving inhaled medicines. Additionally, pts receiving 6 cycles of LAI showed mean increase in relative change in FEV1 that was sustained during both on- and off-treatment months, showing longer-term durability of treatment effect.

Fetched live from OpenAlex and de-inverted. Abstracts are not stored in this database: the inverted indexes are 8.6 GB of the frame’s 9.3 GB of text, and the host has 13 GB free.

How this classification was reachedexpand

Full frame machine prediction

Teacher imitation

Not calibrated prevalence, not ground truth. Human validation pending. The Gemma side is a direct model label for every work in the frame, read from the title-only record. The Codex side is a classifier learned from the 10,348 direct Codex labels and calibrated to design-weighted sample rates; fields without enough sample support carry no Codex call. Candidate is the union of the two sides; consensus is their intersection. These outputs are machine_predicted_unvalidated and are not human labels.

metaresearch head score (Codex)0.004
metaresearch head score (Gemma)0.003
Version: metacan-v3-hybrid-931329e0061cValidation status: machine_predicted_unvalidated
Candidate categoriesnone
Consensus categoriesnone
DomainCandidate signal: none · Consensus signal: none
Study designCandidate signal: Non-randomized trial · Consensus signal: none
GenreCandidate signal: Empirical · Consensus signal: Empirical
Teacher disagreement score0.004
Threshold uncertainty score0.020

Distilled classifier scores by category (both heads)

CategoryCodexGemma
Metaresearch0.0040.003
Meta-epidemiology (narrow)0.0010.000
Meta-epidemiology (broad)0.0010.001
Bibliometrics0.0000.000
Science and technology studies0.0000.000
Scholarly communication0.0010.001
Open science0.0000.000
Research integrity0.0010.001
Insufficient payload (model declined to judge)0.0030.001

Machine scores (provisional)

The two teacher heads of the student model, read on this work. A score orders the frame for review; it never asserts a category, and the validation status ships verbatim with every row.

Baseline scores from an immature model (maturity gate not passed, 7 training rounds). Scores rank; they never assert a category.

Opus teacher head0.032
GPT teacher head0.290
Teacher spread0.257 · how far apart the two teachers sit on this one work
Validation statusscore_only:v0-immature-baseline · verbatim from the scoring run: score_only means the number may rank works, and no category label ships from it

Classification

machine, unvalidated

Machine predicted; a candidate call from one source (direct Gemma or distilled Codex), not a consensus.

The models applied no category: nothing in the taxonomy fit this work.
Study designNon-randomized trial
Domainnot available
GenreEmpirical

How this classification was reached, model by model and score by score, is at the end of the page under "How this classification was reached".

Quick stats

Citations0
Published2014
Admission routes1
Has abstractyes

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