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S131 CP101, an Investigational Orally Administered Microbiome Therapeutic, Increases Intestinal Microbiome Diversity and Prevents Recurrent C. difficile Infection: Results From a Randomized, Placebo-Controlled Trial

2021· article· en· W3209596191 on OpenAlexaff
Sahil Khanna, Colleen Kelly, Thomas Louie, Monika Fisher, Susy Hota, Bharat Misra, Nicholas W. Van Hise, Eugene F. Yen, John Pullman, Richard Nathan, Michael Silverman, Ian Davis, Sarah McGill, Ylaine Gerardin, Josh Silva, Darrell S. Pardi, Robert Orenstein, Ari Grinspan, Najwa El‐Nachef, Colleen S. Kraft, Shrish Budree, Thomas J. Borody, Zain Kassam, Jessica R. Allegretti

Bibliographic record

VenueThe American Journal of Gastroenterology · 2021
Typearticle
Languageen
FieldMedicine
TopicClostridium difficile and Clostridium perfringens research
Canadian institutionsDalhousie UniversityUniversity Health NetworkUniversity of TorontoSt Joseph's Health CareWestern UniversityUniversity of Calgary
Fundersnot available
KeywordsMedicineMicrobiomePlaceboRandomized controlled trialInternal medicineClinical endpointAntibioticsDosingClinical trialSurrogate endpointBioinformaticsPathologyMicrobiologyBiology

Abstract

fetched live from OpenAlex

Introduction: Microbiome diversity is a surrogate marker for microbiome health with decreased diversity observed in many diseases. Key to disease pathogenesis in recurrent Clostridioides difficile infection (CDI) is decreased microbiome diversity and impaired colonization resistance. CP101 is an investigational orally administered microbiome therapeutic designed to restore microbiome diversity and enable early intervention in the management of recurrent CDI. Microbiome diversity is a key pharmacodynamic marker in recurrent CDI; however, data on the impact of increasing diversity on efficacy is scarce. Methods: We conducted a double-blind, randomized, placebo-controlled trial (PRISM3) enrolling adults who received standard-of-care antibiotics for recurrent CDI. Patients with first CDI recurrence at high-risk for further recurrence (≥65 years), or those with two or more recurrences were eligible. The qualifying CDI episode was diagnosed prior to study entry by guideline recommended testing (PCR-based or toxin EIA-based). Following CDI antibiotics, participants completed a minimum 2-day washout period. Eligible participants were randomized 1:1 to receive one-time oral administration of CP101 or placebo without bowel preparation. The primary efficacy endpoint was sustained clinical cure, defined as an absence of CDI recurrence through Week 8 following dosing. Diversity of the intestinal microbiome was measured at baseline, Week 1, and Week 8 using 16S rRNA gene amplicon sequencing. Results: Among the 198 enrolled participants analyzed, the CP101 arm demonstrated a statistically significant and clinically meaningful improvement in sustained clinical cure compared to placebo through Week 8 (74.5% [76/102] vs 61.5% [59/96], P=0.0488). Alpha diversity was low in the CP101 and placebo arms at baseline, and similar between both groups. Participants treated with CP101 achieved significantly higher alpha diversity compared to placebo, and the increase in diversity was rapid and sustained over time (p< 0.001 at Week 1, p< 0.0001 at Week 8) (Fig. 1a). Participants who received CP101 also had a significantly greater change in their microbial community composition from baseline compared to placebo at Week 1 (p< 0.001). Clinically, an increase in microbiome diversity at Week 1 was associated with sustained clinical cure through Week 8 (p< 0.001) (Fig. 1b). Conclusion: These data suggest that CP101 restores microbiome diversity, leading to colonization resistance and driving sustained clinical cure in recurrent CDI.Figure 1.: a. CP101 drives restoration of microbiome diversity. B. An increase in microbiome diversity at Week 1 is associated with sustained clinical cure through Week 8.

Fetched live from OpenAlex and de-inverted. Abstracts are not stored in this database: the inverted indexes are 8.6 GB of the frame’s 9.3 GB of text, and the host has 13 GB free.

How this classification was reachedexpand

Full frame machine prediction

Teacher imitation

Not calibrated prevalence, not ground truth. Human validation pending. The Gemma side is a direct model label for every work in the frame, read from the title-only record. The Codex side is a classifier learned from the 10,348 direct Codex labels and calibrated to design-weighted sample rates; fields without enough sample support carry no Codex call. Candidate is the union of the two sides; consensus is their intersection. These outputs are machine_predicted_unvalidated and are not human labels.

metaresearch head score (Codex)0.003
metaresearch head score (Gemma)0.004
Version: metacan-v3-hybrid-931329e0061cValidation status: machine_predicted_unvalidated
Candidate categoriesnone
Consensus categoriesnone
DomainCandidate signal: none · Consensus signal: none
Study designCandidate signal: Randomized trial · Consensus signal: Randomized trial
GenreCandidate signal: Empirical · Consensus signal: Empirical
Teacher disagreement score0.010
Threshold uncertainty score0.034

Distilled classifier scores by category (both heads)

CategoryCodexGemma
Metaresearch0.0030.004
Meta-epidemiology (narrow)0.0010.001
Meta-epidemiology (broad)0.0030.003
Bibliometrics0.0000.001
Science and technology studies0.0000.002
Scholarly communication0.0010.001
Open science0.0010.000
Research integrity0.0030.002
Insufficient payload (model declined to judge)0.0100.001

Machine scores (provisional)

The two teacher heads of the student model, read on this work. A score orders the frame for review; it never asserts a category, and the validation status ships verbatim with every row.

Baseline scores from an immature model (maturity gate not passed, 7 training rounds). Scores rank; they never assert a category.

Opus teacher head0.032
GPT teacher head0.296
Teacher spread0.264 · how far apart the two teachers sit on this one work
Validation statusscore_only:v0-immature-baseline · verbatim from the scoring run: score_only means the number may rank works, and no category label ships from it

Classification

machine, unvalidated

Machine predicted; a candidate call from one source (direct Gemma or distilled Codex), not a consensus.

The models applied no category: nothing in the taxonomy fit this work.
Study designRandomized trial
Domainnot available
GenreEmpirical

How this classification was reached, model by model and score by score, is at the end of the page under "How this classification was reached".

Quick stats

Citations18
Published2021
Admission routes1
Has abstractyes

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